Cancer Clinical Trial Eligibility Criteria: Patients With Organ Dysfunction or Prior or Concurrent Malignancies; Guidance for Industry; Availability, 41993-41995 [2020-14996]
Download as PDF
Federal Register / Vol. 85, No. 134 / Monday, July 13, 2020 / Notices
Hampshire Ave., Hillandale Building,
4th Floor, Silver Spring, MD 20993–
0002; or to the Office of
Communication, Outreach and
Development, Center for Biologics
Evaluation and Research, Food and
Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 3128,
Silver Spring, MD 20993–0002. Send
one self-addressed adhesive label to
assist that office in processing your
requests. See the SUPPLEMENTARY
INFORMATION section for electronic
access to the guidance document.
FOR FURTHER INFORMATION CONTACT: Julia
Beaver, Center for Drug Evaluation and
Research, Food and Drug
Administration, 10903 New Hampshire
Ave., Bldg. 22, Rm. 2100, Silver Spring,
MD 20993–0002, 240–402–0489; or
Stephen Ripley, Center for Biologics
Evaluation and Research, Food and
Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 7301,
Silver Spring, MD 20993–0002, 240–
402–7911.
SUPPLEMENTARY INFORMATION:
jbell on DSKJLSW7X2PROD with NOTICES
I. Background
FDA is announcing the availability of
a guidance for industry entitled ‘‘Cancer
Clinical Trial Eligibility Criteria: Brain
Metastases.’’ This guidance provides
recommendations on the inclusion of
patients with brain metastases in
clinical trials of drugs or biological
products regulated by CDER and CBER
for the treatment of cancer.
A clinical trial’s eligibility criteria (for
inclusion and exclusion) are essential
components of the trial, defining the
characteristics of the study population.
Because there is variability in
investigational drugs and trial
objectives, eligibility criteria should be
developed taking into consideration the
mechanism of action of the drug, the
targeted disease or patient population,
the anticipated safety of the
investigational drug, the availability of
adequate safety data, and the ability to
recruit trial participants from the patient
population to meet the objectives of the
clinical trial. However, some eligibility
criteria have become commonly
accepted over time or used as a template
across trials without clear scientific or
clinical rationale. Unnecessarily
restrictive eligibility criteria may slow
patient accrual, limit patients’ access to
clinical trials, and lead to trial results
that do not fully represent treatment
effects in the patient population that
will ultimately use the drug. Broadening
cancer trial eligibility criteria can
maximize the generalizability of trial
results and the ability to understand the
therapy’s benefit-risk profile across the
VerDate Sep<11>2014
20:25 Jul 10, 2020
Jkt 250001
patient population likely to use the drug
in clinical practice and should be
considered to avoid jeopardizing patient
safety.
Patients with brain metastases have
historically been excluded from clinical
trials due to concerns of poor functional
status, shortened life expectancy, or
increased risk of toxicity. Given the
prevalence of brain metastases in
patients with cancer, their systematic
exclusion from clinical trials may result
in the assessment of an investigational
drug’s efficacy or safety in a trial
population that is not fully
representative of the patient population
that will be prescribed the drug in
clinical practice. The guidance includes
recommendations regarding eligibility
criteria for patients with brain
metastases, as well as recommendations
specific to patients with treated/stable
metastases, active metastases, and
leptomeningeal metastases.
The recommendations in this
guidance do not apply to trials designed
specifically to assess the safety and
efficacy of investigational drugs for the
treatment of primary brain cancers (e.g.,
glioblastoma) or brain metastases.
In the Federal Register of March 13,
2019 (84 FR 9127), FDA announced the
availability of the draft guidance of the
same title. FDA received comments and
considered those comments as the
guidance was finalized. The final
guidance includes general
considerations and general approaches
for including patients with the different
types of brain metastases described in
the guidance. The final guidance
includes clarifications, for example
regarding the description of the types of
metastases and the recommendations for
inclusion of patients with the different
types of metastases and the
recommendation for exclusion of
patients with brain metastases and a
history of seizures in trials for drugs
with the potential to lower seizure
threshold.
This guidance is being issued
consistent with FDA’s good guidance
practices regulation (21 CFR 10.115).
The guidance represents the current
thinking of FDA on ‘‘Cancer Clinical
Trial Eligibility Criteria: Brain
Metastases.’’ It does not establish any
rights for any person and is not binding
on FDA or the public. You can use an
alternative approach if it satisfies the
requirements of the applicable statutes
and regulations.
II. Paperwork Reduction Act of 1995
This guidance refers to previously
approved FDA collections of
information. These collections of
information are subject to review by the
PO 00000
Frm 00056
Fmt 4703
Sfmt 4703
41993
Office of Management and Budget
(OMB) under the Paperwork Reduction
Act of 1995 (44 U.S.C. 3501–3521). The
collections of information in 21 CFR
part 312 have been approved under
OMB control number 0910–0014; the
collections of information in 21 CFR
201.56 and 201.57 have been approved
under OMB control number 0910–0572.
III. Electronic Access
Persons with access to the internet
may obtain the guidance at either
https://www.fda.gov/drugs/guidancecompliance-regulatory-information/
guidances-drugs, https://www.fda.gov/
vaccines-blood-biologics/guidancecompliance-regulatory-informationbiologics/biologics-guidances, or https://
www.regulations.gov.
Dated: July 7, 2020.
Lowell J. Schiller,
Principal Associate Commissioner for Policy.
[FR Doc. 2020–14997 Filed 7–10–20; 8:45 am]
BILLING CODE 4164–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA–2019–D–0359]
Cancer Clinical Trial Eligibility Criteria:
Patients With Organ Dysfunction or
Prior or Concurrent Malignancies;
Guidance for Industry; Availability
AGENCY:
Food and Drug Administration,
HHS.
ACTION:
Notice of availability.
The Food and Drug
Administration (FDA or Agency) is
announcing the availability of a final
guidance for industry entitled ‘‘Cancer
Clinical Trial Eligibility Criteria:
Patients with Organ Dysfunction or
Prior or Concurrent Malignancies.’’ This
guidance is one in a series of guidances
that provide recommendations
regarding eligibility criteria for clinical
trials of drugs or biological products
regulated by the Center for Drug
Evaluation and Research (CDER) and the
Center for Biologics Evaluation and
Research (CBER) for the treatment of
cancer. Specifically, this guidance
includes recommendations on the
inclusion of patients with organ
dysfunction or with prior or concurrent
malignancies. This guidance finalizes
the draft guidance of the same title that
published on March 13, 2019.
DATES: The announcement of the
guidance is published in the Federal
Register on July 13, 2020.
SUMMARY:
E:\FR\FM\13JYN1.SGM
13JYN1
41994
Federal Register / Vol. 85, No. 134 / Monday, July 13, 2020 / Notices
You may submit either
electronic or written comments on
Agency guidances at any time as
follows:
ADDRESSES:
jbell on DSKJLSW7X2PROD with NOTICES
Electronic Submissions
Submit electronic comments in the
following way:
• Federal eRulemaking Portal:
https://www.regulations.gov. Follow the
instructions for submitting comments.
Comments submitted electronically,
including attachments, to https://
www.regulations.gov will be posted to
the docket unchanged. Because your
comment will be made public, you are
solely responsible for ensuring that your
comment does not include any
confidential information that you or a
third party may not wish to be posted,
such as medical information, your or
anyone else’s Social Security number, or
confidential business information, such
as a manufacturing process. Please note
that if you include your name, contact
information, or other information that
identifies you in the body of your
comments, that information will be
posted on https://www.regulations.gov.
• If you want to submit a comment
with confidential information that you
do not wish to be made available to the
public, submit the comment as a
written/paper submission and in the
manner detailed (see ‘‘Written/Paper
Submissions’’ and ‘‘Instructions’’).
Written/Paper Submissions
Submit written/paper submissions as
follows:
• Mail/Hand Delivery/Courier (for
written/paper submissions): Dockets
Management Staff (HFA–305), Food and
Drug Administration, 5630 Fishers
Lane, Rm. 1061, Rockville, MD 20852.
• For written/paper comments
submitted to the Dockets Management
Staff, FDA will post your comment, as
well as any attachments, except for
information submitted, marked and
identified, as confidential, if submitted
as detailed in ‘‘Instructions.’’
Instructions: All submissions received
must include the Docket No. FDA–
2019–D–0359 for ‘‘Cancer Clinical Trial
Eligibility Criteria: Patients with Organ
Dysfunction or Prior or Concurrent
Malignancies.’’ Received comments will
be placed in the docket and, except for
those submitted as ‘‘Confidential
Submissions,’’ publicly viewable at
https://www.regulations.gov or at the
Dockets Management Staff between 9
a.m. and 4 p.m., Monday through
Friday, 240–402–7500.
• Confidential Submissions—To
submit a comment with confidential
information that you do not wish to be
made publicly available, submit your
VerDate Sep<11>2014
20:25 Jul 10, 2020
Jkt 250001
comments only as a written/paper
submission. You should submit two
copies total. One copy will include the
information you claim to be confidential
with a heading or cover note that states
‘‘THIS DOCUMENT CONTAINS
CONFIDENTIAL INFORMATION.’’ The
Agency will review this copy, including
the claimed confidential information, in
its consideration of comments. The
second copy, which will have the
claimed confidential information
redacted/blacked out, will be available
for public viewing and posted on
https://www.regulations.gov. Submit
both copies to the Dockets Management
Staff. If you do not wish your name and
contact information to be made publicly
available, you can provide this
information on the cover sheet and not
in the body of your comments and you
must identify this information as
‘‘confidential.’’ Any information marked
as ‘‘confidential’’ will not be disclosed
except in accordance with 21 CFR 10.20
and other applicable disclosure law. For
more information about FDA’s posting
of comments to public dockets, see 80
FR 56469, September 18, 2015, or access
the information at: https://
www.govinfo.gov/content/pkg/FR-201509-18/pdf/2015-23389.pdf.
Docket: For access to the docket to
read background documents or the
electronic and written/paper comments
received, go to https://
www.regulations.gov and insert the
docket number, found in brackets in the
heading of this document, into the
‘‘Search’’ box and follow the prompts
and/or go to the Dockets Management
Staff, 5630 Fishers Lane, Rm. 1061,
Rockville, MD 20852, 240–402–7500.
You may submit comments on any
guidance at any time (see 21 CFR
10.115(g)(5)).
Submit written requests for single
copies of this guidance to the Division
of Drug Information, Center for Drug
Evaluation and Research, Food and
Drug Administration, 10001 New
Hampshire Ave., Hillandale Building,
4th Floor, Silver Spring, MD 20993–
0002; or to the Office of
Communication, Outreach and
Development, Center for Biologics
Evaluation and Research, Food and
Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 3128,
Silver Spring, MD 20993–0002. Send
one self-addressed adhesive label to
assist that office in processing your
requests. See the SUPPLEMENTARY
INFORMATION section for electronic
access to the guidance document.
FOR FURTHER INFORMATION CONTACT: Julia
Beaver, Center for Drug Evaluation and
Research, Food and Drug
PO 00000
Frm 00057
Fmt 4703
Sfmt 4703
Administration, 10903 New Hampshire
Ave., Bldg. 22, Rm. 2100, Silver Spring,
MD 20993–0002, 240–402–0489; or
Stephen Ripley, Center for Biologics
Evaluation and Research, Food and
Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 7301,
Silver Spring, MD 20993–0002, 240–
402–7911.
SUPPLEMENTARY INFORMATION:
I. Background
FDA is announcing the availability of
a guidance for industry entitled ‘‘Cancer
Clinical Trial Eligibility Criteria:
Patients with Organ Dysfunction or
Prior or Concurrent Malignancies.’’ This
guidance provides recommendations on
the inclusion of patients with organ
dysfunction or prior or concurrent
malignancies in clinical trials of drugs
or biological products regulated by
CDER and CBER for the treatment of
cancer.
A clinical trial’s eligibility criteria (for
inclusion and exclusion) are essential
components of the trial, defining the
characteristics of the study population.
Because there is variability in
investigational drugs and trial
objectives, eligibility criteria should be
developed taking into consideration the
mechanism of action of the drug, the
targeted disease or patient population,
the anticipated safety of the
investigational drug, the availability of
adequate safety data, and the ability to
recruit trial participants from the patient
population to meet the objectives of the
clinical trial. However, some eligibility
criteria have become commonly
accepted over time or used as a template
across trials without clear scientific or
clinical rationale. Unnecessarily
restrictive eligibility criteria may slow
patient accrual, limit patients’ access to
clinical trials, and lead to trial results
that do not fully represent treatment
effects in the patient population that
will ultimately use the drug. Broadening
cancer trial eligibility criteria can
maximize the generalizability of trial
results and the ability to understand the
therapy’s benefit-risk profile across the
patient population likely to use the drug
in clinical practice and should be
considered to avoid jeopardizing patient
safety.
The recommendations in this
guidance for clinical trial eligibility
criteria for patients with organ
dysfunction focus on renal function,
cardiac function, and hepatic function.
This guidance also includes
recommendations for eligibility criteria
for patients with cancer who have prior
or concurrent malignancies.
In the Federal Register of March 13,
2019 (84 FR 9129), FDA announced the
E:\FR\FM\13JYN1.SGM
13JYN1
Federal Register / Vol. 85, No. 134 / Monday, July 13, 2020 / Notices
availability of the draft guidance of the
same title. FDA received comments and
considered those comments as the
guidance was finalized. The final
guidance clarifies the recommendations
regarding eligibility criteria related to
renal function, cardiac function, and
hepatic function. For example,
recommendations regarding the
equation used to assess renal function
for eligibility were clarified and
recommendations regarding population
pharmacokinetic analyses of patients
with renal impairment were added. In
addition, recommendations regarding
QTc prolongation were clarified and the
recommendation on patients with
asymptomatic elevations in
unconjugated bilirubin was removed
because it is out of the scope of organ
dysfunction.
This guidance is being issued
consistent with FDA’s good guidance
practices regulation (21 CFR 10.115).
The guidance represents the current
thinking of FDA on ‘‘Cancer Clinical
Trial Eligibility Criteria: Patients with
Organ Dysfunction or Prior or
Concurrent Malignancies.’’ It does not
establish any rights for any person and
is not binding on FDA or the public.
You can use an alternative approach if
it satisfies the requirements of the
applicable statutes and regulations.
II. Paperwork Reduction Act of 1995
This guidance refers to previously
approved FDA collections of
information. These collections of
information are subject to review by the
Office of Management and Budget
(OMB) under the Paperwork Reduction
Act of 1995 (44 U.S.C. 3501–3521). The
collections of information in 21 CFR
part 312 have been approved under
OMB control number 0910–0014; the
collections of information in 21 CFR
201.56 and 201.57 have been approved
under OMB control number 0910–0572.
jbell on DSKJLSW7X2PROD with NOTICES
III. Electronic Access
Persons with access to the internet
may obtain the guidance at either
https://www.fda.gov/drugs/guidancecompliance-regulatory-information/
guidances-drugs, https://www.fda.gov/
vaccines-blood-biologics/guidancecompliance-regulatory-informationbiologics/biologics-guidances, or https://
www.regulations.gov.
Dated: July 7, 2020.
Lowell J. Schiller,
Principal Associate Commissioner for Policy.
[FR Doc. 2020–14996 Filed 7–10–20; 8:45 am]
BILLING CODE 4164–01–P
VerDate Sep<11>2014
20:25 Jul 10, 2020
Jkt 250001
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
[Docket No.FDA–2020–N–1500]
Food and Drug Administration Hiring
and Retention Interim Assessment;
Public Meeting; Request for Comments
AGENCY:
Food and Drug Administration,
HHS.
Notice of public meeting;
request for comments.
ACTION:
The Food and Drug
Administration (FDA, the Agency, or
we) is holding a virtual meeting entitled
‘‘FDA Hiring and Retention Interim
Assessment’’ and an opportunity for
public comment. The topic to be
discussed is FDA’s hiring and retention
interim assessment which was an
independent assessment performed by
Booz Allen Hamilton, published on June
5, 2020. This public meeting will take
place virtually due to extenuating
circumstances and will be held by
webcast only.
DATES: The public meeting will be held
on July 30, 2020, from 9 a.m. to noon.
Submit either electronic or written
comments on this public meeting by
September 30, 2020. See the
SUPPLEMENTARY INFORMATION section for
registration date and information.
ADDRESSES: You may submit comments
as follows. Please note that late,
untimely filed comments will not be
considered. Electronic comments must
be submitted on or by September 30,
2020. The https://www.regulations.gov
electronic filing system will accept
comments until 11:59 p.m. Eastern Time
at the end of September 30, 2020.
Comments received by mail/hand
delivery/courier (for written/paper
submissions) will be considered timely
if they are postmarked or the delivery
service acceptance receipt is on or
before that date.
SUMMARY:
Electronic Submissions
Submit electronic comments in the
following way:
• Federal eRulemaking Portal:
https://www.regulations.gov. Follow the
instructions for submitting comments.
Comments submitted electronically,
including attachments, to https://
www.regulations.gov will be posted to
the docket unchanged. Because your
comment will be made public, you are
solely responsible for ensuring that your
comment does not include any
confidential information that you or a
third party may not wish to be posted,
such as medical information, your or
anyone else’s Social Security number, or
PO 00000
Frm 00058
Fmt 4703
Sfmt 4703
41995
confidential business information, such
as a manufacturing process. Please note
that if you include your name, contact
information, or other information that
identifies you in the body of your
comments, that information will be
posted on https://www.regulations.gov.
• If you want to submit a comment
with confidential information that you
do not wish to be made available to the
public, submit the comment as a
written/paper submission and in the
manner detailed (see ‘‘Written/Paper
Submissions’’ and ‘‘Instructions’’).
Written/Paper Submissions
Submit written/paper submissions as
follows:
• Mail/Hand Delivery/Courier (for
written/paper submissions): Dockets
Management Staff (HFA–305), Food and
Drug Administration, 5630 Fishers
Lane, Rm. 1061, Rockville, MD 20852.
• For written/paper comments
submitted to the Dockets Management
Staff, FDA will post your comment, as
well as any attachments, except for
information submitted, marked and
identified, as confidential, if submitted
as detailed in ‘‘Instructions.’’
Instructions: All submissions received
must include the Docket No. FDA–
2020–N–1500 ‘‘FDA Hiring and
Retention Interim Assessment; Public
Meeting; Request for Comments.’’
Received comments, those filed in a
timely manner (see ADDRESSES), will be
placed in the docket and, except for
those submitted as ‘‘Confidential
Submissions,’’ publicly viewable at
https://www.regulations.gov or at the
Dockets Management Staff between 9
a.m. and 4 p.m., Monday through
Friday, 240–402–7500.
• Confidential Submissions—To
submit a comment with confidential
information that you do not wish to be
made publicly available, submit your
comments only as a written/paper
submission. You should submit two
copies total. One copy will include the
information you claim to be confidential
with a heading or cover note that states
‘‘THIS DOCUMENT CONTAINS
CONFIDENTIAL INFORMATION.’’ The
Agency will review this copy, including
the claimed confidential information, in
its consideration of comments. The
second copy, which will have the
claimed confidential information
redacted/blacked out, will be available
for public viewing and posted on
https://www.regulations.gov. Submit
both copies to the Dockets Management
Staff. If you do not wish your name and
contact information to be made publicly
available, you can provide this
information on the cover sheet and not
in the body of your comments and you
E:\FR\FM\13JYN1.SGM
13JYN1
Agencies
[Federal Register Volume 85, Number 134 (Monday, July 13, 2020)]
[Notices]
[Pages 41993-41995]
From the Federal Register Online via the Government Publishing Office [www.gpo.gov]
[FR Doc No: 2020-14996]
-----------------------------------------------------------------------
DEPARTMENT OF HEALTH AND HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA-2019-D-0359]
Cancer Clinical Trial Eligibility Criteria: Patients With Organ
Dysfunction or Prior or Concurrent Malignancies; Guidance for Industry;
Availability
AGENCY: Food and Drug Administration, HHS.
ACTION: Notice of availability.
-----------------------------------------------------------------------
SUMMARY: The Food and Drug Administration (FDA or Agency) is announcing
the availability of a final guidance for industry entitled ``Cancer
Clinical Trial Eligibility Criteria: Patients with Organ Dysfunction or
Prior or Concurrent Malignancies.'' This guidance is one in a series of
guidances that provide recommendations regarding eligibility criteria
for clinical trials of drugs or biological products regulated by the
Center for Drug Evaluation and Research (CDER) and the Center for
Biologics Evaluation and Research (CBER) for the treatment of cancer.
Specifically, this guidance includes recommendations on the inclusion
of patients with organ dysfunction or with prior or concurrent
malignancies. This guidance finalizes the draft guidance of the same
title that published on March 13, 2019.
DATES: The announcement of the guidance is published in the Federal
Register on July 13, 2020.
[[Page 41994]]
ADDRESSES: You may submit either electronic or written comments on
Agency guidances at any time as follows:
Electronic Submissions
Submit electronic comments in the following way:
Federal eRulemaking Portal: https://www.regulations.gov.
Follow the instructions for submitting comments. Comments submitted
electronically, including attachments, to https://www.regulations.gov
will be posted to the docket unchanged. Because your comment will be
made public, you are solely responsible for ensuring that your comment
does not include any confidential information that you or a third party
may not wish to be posted, such as medical information, your or anyone
else's Social Security number, or confidential business information,
such as a manufacturing process. Please note that if you include your
name, contact information, or other information that identifies you in
the body of your comments, that information will be posted on https://www.regulations.gov.
If you want to submit a comment with confidential
information that you do not wish to be made available to the public,
submit the comment as a written/paper submission and in the manner
detailed (see ``Written/Paper Submissions'' and ``Instructions'').
Written/Paper Submissions
Submit written/paper submissions as follows:
Mail/Hand Delivery/Courier (for written/paper
submissions): Dockets Management Staff (HFA-305), Food and Drug
Administration, 5630 Fishers Lane, Rm. 1061, Rockville, MD 20852.
For written/paper comments submitted to the Dockets
Management Staff, FDA will post your comment, as well as any
attachments, except for information submitted, marked and identified,
as confidential, if submitted as detailed in ``Instructions.''
Instructions: All submissions received must include the Docket No.
FDA-2019-D-0359 for ``Cancer Clinical Trial Eligibility Criteria:
Patients with Organ Dysfunction or Prior or Concurrent Malignancies.''
Received comments will be placed in the docket and, except for those
submitted as ``Confidential Submissions,'' publicly viewable at https://www.regulations.gov or at the Dockets Management Staff between 9 a.m.
and 4 p.m., Monday through Friday, 240-402-7500.
Confidential Submissions--To submit a comment with
confidential information that you do not wish to be made publicly
available, submit your comments only as a written/paper submission. You
should submit two copies total. One copy will include the information
you claim to be confidential with a heading or cover note that states
``THIS DOCUMENT CONTAINS CONFIDENTIAL INFORMATION.'' The Agency will
review this copy, including the claimed confidential information, in
its consideration of comments. The second copy, which will have the
claimed confidential information redacted/blacked out, will be
available for public viewing and posted on https://www.regulations.gov.
Submit both copies to the Dockets Management Staff. If you do not wish
your name and contact information to be made publicly available, you
can provide this information on the cover sheet and not in the body of
your comments and you must identify this information as
``confidential.'' Any information marked as ``confidential'' will not
be disclosed except in accordance with 21 CFR 10.20 and other
applicable disclosure law. For more information about FDA's posting of
comments to public dockets, see 80 FR 56469, September 18, 2015, or
access the information at: https://www.govinfo.gov/content/pkg/FR-2015-09-18/pdf/2015-23389.pdf.
Docket: For access to the docket to read background documents or
the electronic and written/paper comments received, go to https://www.regulations.gov and insert the docket number, found in brackets in
the heading of this document, into the ``Search'' box and follow the
prompts and/or go to the Dockets Management Staff, 5630 Fishers Lane,
Rm. 1061, Rockville, MD 20852, 240-402-7500.
You may submit comments on any guidance at any time (see 21 CFR
10.115(g)(5)).
Submit written requests for single copies of this guidance to the
Division of Drug Information, Center for Drug Evaluation and Research,
Food and Drug Administration, 10001 New Hampshire Ave., Hillandale
Building, 4th Floor, Silver Spring, MD 20993-0002; or to the Office of
Communication, Outreach and Development, Center for Biologics
Evaluation and Research, Food and Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 3128, Silver Spring, MD 20993-0002. Send
one self-addressed adhesive label to assist that office in processing
your requests. See the SUPPLEMENTARY INFORMATION section for electronic
access to the guidance document.
FOR FURTHER INFORMATION CONTACT: Julia Beaver, Center for Drug
Evaluation and Research, Food and Drug Administration, 10903 New
Hampshire Ave., Bldg. 22, Rm. 2100, Silver Spring, MD 20993-0002, 240-
402-0489; or Stephen Ripley, Center for Biologics Evaluation and
Research, Food and Drug Administration, 10903 New Hampshire Ave., Bldg.
71, Rm. 7301, Silver Spring, MD 20993-0002, 240-402-7911.
SUPPLEMENTARY INFORMATION:
I. Background
FDA is announcing the availability of a guidance for industry
entitled ``Cancer Clinical Trial Eligibility Criteria: Patients with
Organ Dysfunction or Prior or Concurrent Malignancies.'' This guidance
provides recommendations on the inclusion of patients with organ
dysfunction or prior or concurrent malignancies in clinical trials of
drugs or biological products regulated by CDER and CBER for the
treatment of cancer.
A clinical trial's eligibility criteria (for inclusion and
exclusion) are essential components of the trial, defining the
characteristics of the study population. Because there is variability
in investigational drugs and trial objectives, eligibility criteria
should be developed taking into consideration the mechanism of action
of the drug, the targeted disease or patient population, the
anticipated safety of the investigational drug, the availability of
adequate safety data, and the ability to recruit trial participants
from the patient population to meet the objectives of the clinical
trial. However, some eligibility criteria have become commonly accepted
over time or used as a template across trials without clear scientific
or clinical rationale. Unnecessarily restrictive eligibility criteria
may slow patient accrual, limit patients' access to clinical trials,
and lead to trial results that do not fully represent treatment effects
in the patient population that will ultimately use the drug. Broadening
cancer trial eligibility criteria can maximize the generalizability of
trial results and the ability to understand the therapy's benefit-risk
profile across the patient population likely to use the drug in
clinical practice and should be considered to avoid jeopardizing
patient safety.
The recommendations in this guidance for clinical trial eligibility
criteria for patients with organ dysfunction focus on renal function,
cardiac function, and hepatic function. This guidance also includes
recommendations for eligibility criteria for patients with cancer who
have prior or concurrent malignancies.
In the Federal Register of March 13, 2019 (84 FR 9129), FDA
announced the
[[Page 41995]]
availability of the draft guidance of the same title. FDA received
comments and considered those comments as the guidance was finalized.
The final guidance clarifies the recommendations regarding eligibility
criteria related to renal function, cardiac function, and hepatic
function. For example, recommendations regarding the equation used to
assess renal function for eligibility were clarified and
recommendations regarding population pharmacokinetic analyses of
patients with renal impairment were added. In addition, recommendations
regarding QTc prolongation were clarified and the recommendation on
patients with asymptomatic elevations in unconjugated bilirubin was
removed because it is out of the scope of organ dysfunction.
This guidance is being issued consistent with FDA's good guidance
practices regulation (21 CFR 10.115). The guidance represents the
current thinking of FDA on ``Cancer Clinical Trial Eligibility
Criteria: Patients with Organ Dysfunction or Prior or Concurrent
Malignancies.'' It does not establish any rights for any person and is
not binding on FDA or the public. You can use an alternative approach
if it satisfies the requirements of the applicable statutes and
regulations.
II. Paperwork Reduction Act of 1995
This guidance refers to previously approved FDA collections of
information. These collections of information are subject to review by
the Office of Management and Budget (OMB) under the Paperwork Reduction
Act of 1995 (44 U.S.C. 3501-3521). The collections of information in 21
CFR part 312 have been approved under OMB control number 0910-0014; the
collections of information in 21 CFR 201.56 and 201.57 have been
approved under OMB control number 0910-0572.
III. Electronic Access
Persons with access to the internet may obtain the guidance at
either https://www.fda.gov/drugs/guidance-compliance-regulatory-information/guidances-drugs, https://www.fda.gov/vaccines-blood-biologics/guidance-compliance-regulatory-information-biologics/biologics-guidances, or https://www.regulations.gov.
Dated: July 7, 2020.
Lowell J. Schiller,
Principal Associate Commissioner for Policy.
[FR Doc. 2020-14996 Filed 7-10-20; 8:45 am]
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