Draft Guidances Relating to the Development of Human Gene Therapy Products; Availability; Extension of Comment Period, 45249-45251 [2018-19303]
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Federal Register / Vol. 83, No. 173 / Thursday, September 6, 2018 / Notices
Evaluation, Center for Devices and
Radiological Health, Food and Drug
Administration, 10903 New Hampshire
Ave., Bldg. 66, Rm. G610, Silver Spring,
MD 20993–0002, 301–796–6875, email:
Patricio.Garcia@fda.hhs.gov.
SUPPLEMENTARY INFORMATION: FDA is
requesting nominations for voting
members on TEPRSSC that include
three general public representatives.
part 822 have been approved under
OMB control number 0910–0449.
Dated: August 30, 2018.
Leslie Kux,
Associate Commissioner for Policy.
[FR Doc. 2018–19249 Filed 9–5–18; 8:45 am]
BILLING CODE 4164–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
I. General Description of the
Committee’s Duties
Food and Drug Administration
[Docket No. FDA–2018–N–3233]
Request for Nominations for Voting
Members on a Public Advisory
Committee; Technical Electronic
Product Radiation Safety Standards
Committee
AGENCY:
Food and Drug Administration,
HHS.
ACTION:
Notice.
The Food and Drug
Administration (FDA) is requesting
nominations for members to serve on
the Technical Electronic Product
Radiation Safety Standards Committee
(TEPRSSC) in the Center for Devices
and Radiological Health. Nominations
will be accepted for current and
upcoming vacancies effective with this
notice.
FDA seeks to include the views of
women and men, members of all racial
and ethnic groups, and individuals with
and without disabilities on its advisory
committees and, therefore, encourages
nominations of appropriately qualified
candidates from these groups.
DATES: Nominations received on or
before November 5, 2018 will be given
first consideration for membership on
TEPRSSC. Nominations received after
November 5, 2018 will be considered for
nomination to the committee as later
vacancies occur.
ADDRESSES: All nominations for
membership should be sent
electronically by accessing FDA’s
Advisory Committee Membership
Nomination Portal at https://
www.accessdata.fda.gov/scripts/
FACTRSPortal/FACTRS/index.cfm or by
mail to Advisory Committee Oversight
and Management Staff, Food and Drug
Administration, 10903 New Hampshire
Ave., Bldg. 32, Rm. 5103, Silver Spring,
MD 20993–0002. Information about
becoming a member on an FDA advisory
committee can also be obtained by
visiting FDA’s website at https://
www.fda.gov/AdvisoryCommittees/
default.htm.
FOR FURTHER INFORMATION CONTACT:
Patricio G. Garcia, Office of Device
daltland on DSKBBV9HB2PROD with NOTICES
SUMMARY:
VerDate Sep<11>2014
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Jkt 244001
U.S.C. app. 2) and 21 CFR part 14,
relating to advisory committees.
Dated: August 31, 2018.
Leslie Kux,
Associate Commissioner for Policy.
[FR Doc. 2018–19355 Filed 9–5–18; 8:45 am]
BILLING CODE 4164–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
The committee provides advice and
consultation to the Commissioner of
Food and Drugs (Commissioner) on the
technical feasibility, reasonableness,
and practicability of performance
standards for electronic products to
control the emission of radiation from
such products, and may recommend
electronic product radiation safety
standards to the Commissioner for
consideration.
[Docket Nos. FDA–1999–D–0081, FDA–
2008–D–0205, FDA–2018–D–2173, FDA–
2018–D–2236, FDA–2018–D–2238, and FDA–
2018–D–2258]
Draft Guidances Relating to the
Development of Human Gene Therapy
Products; Availability; Extension of
Comment Period
AGENCY:
II. Criteria for Voting Members
HHS.
The committee consists of a core of 15
voting members including the Chair.
Members and the Chair are selected by
the Commissioner or designee from
among authorities knowledgeable in the
fields of science or engineering,
applicable to electronic product
radiation safety. Members will be
invited to serve for overlapping terms of
up to 4 years. Terms of more than 2
years are contingent upon the renewal
of the committee by appropriate action
prior to its expiration.
ACTION:
III. Nomination Procedures
Any interested person may nominate
one or more qualified individuals for
membership on the committee. Selfnominations are also accepted.
Nominations must include a current,
complete re´sume´ or curriculum vitae for
each nominee, including current
business address and/or home address,
telephone number, and email address if
available, and a signed copy of the
Acknowledgement and Consent form
available at the FDA Advisory
Nomination Portal (see ADDRESSES).
Nominations must also specify the
advisory committee for which the
nominee is recommended. Nominations
must also acknowledge that the
nominee is aware of the nomination
unless self-nominated. FDA will ask
potential candidates to provide detailed
information concerning such matters
related to financial holdings,
employment, and research grants and/or
contracts to permit evaluation of
possible sources of conflicts of interest.
This notice is issued under the
Federal Advisory Committee Act (5
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45249
Food and Drug Administration,
Notification; extension of
comment period.
The Food and Drug
Administration (FDA or the Agency) is
extending the comment period for the
notices of availability for six draft
guidance documents relating to the
development of human gene therapy
products that appeared in the Federal
Register of July 12, 2018. The Agency is
taking this action in response to
requests for an extension to allow
interested persons additional time to
submit comments and any new
information.
SUMMARY:
FDA is extending the comment
period on the six documents that
published on July 12, 2018 (see
SUPPLEMENTARY INFORMATION). Submit
either electronic or written comments
by December 10, 2018, to ensure that the
Agency considers your comment on
these draft guidances before it begins
work on the final version of the
guidances.
DATES:
You may submit comments
as follows. Please note that late,
untimely filed comments will not be
considered. Electronic comments must
be submitted on or before December 10,
2018. The https://www.regulations.gov
electronic filing system will accept
comments until midnight Eastern Time
at the end of December 10, 2018.
Comments received by mail/hand
delivery/courier (for written/paper
submissions) will be considered timely
if they are postmarked or the delivery
service acceptance receipt is on or
before that date.
ADDRESSES:
E:\FR\FM\06SEN1.SGM
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45250
Federal Register / Vol. 83, No. 173 / Thursday, September 6, 2018 / Notices
Electronic Submissions
Submit electronic comments in the
following way:
• Federal eRulemaking Portal:
https://www.regulations.gov. Follow the
instructions for submitting comments.
Comments submitted electronically,
including attachments, to https://
www.regulations.gov will be posted to
the docket unchanged. Because your
comment will be made public, you are
solely responsible for ensuring that your
comment does not include any
confidential information that you or a
third party may not wish to be posted,
such as medical information, your or
anyone else’s Social Security number, or
confidential business information, such
as a manufacturing process. Please note
that if you include your name, contact
information, or other information that
identifies you in the body of your
comments, that information will be
posted on https://www.regulations.gov.
• If you want to submit a comment
with confidential information that you
do not wish to be made available to the
public, submit the comment as a
written/paper submission and in the
manner detailed (see ‘‘Written/Paper
Submissions’’ and ‘‘Instructions’’).
Written/Paper Submissions
Submit written/paper submissions as
follows:
• Mail/Hand delivery/Courier (for
written/paper submissions): Dockets
Management Staff (HFA–305), Food and
Drug Administration, 5630 Fishers
Lane, Rm. 1061, Rockville, MD 20852.
• For written/paper comments
submitted to the Dockets Management
Staff, FDA will post your comment, as
well as any attachments, except for
information submitted, marked and
identified, as confidential, if submitted
as detailed in ‘‘Instructions.’’
Instructions: All submissions received
must include the Docket No. FDA–
1999–D–0081 for ‘‘Testing of Retroviral
Vector-Based Human Gene Therapy
Products for Replication Competent
Retrovirus During Product Manufacture
and Patient Follow-up; Draft Guidance
for Industry;’’ Docket No. FDA–2008–D–
0205 for ‘‘Chemistry, Manufacturing,
and Control Information for Human
Gene Therapy Investigational New Drug
Applications; Draft Guidance for
Industry;’’ Docket No. FDA–2018–D–
2173 for ‘‘Long Term Follow-Up After
Administration of Human Gene Therapy
Products; Draft Guidance for Industry;’’
Docket No. FDA–2018–D–2236 for
‘‘Human Gene Therapy for Retinal
Disorders; Draft Guidance for Industry;’’
Docket No. FDA–2018–D–2238 for
‘‘Human Gene Therapy for Hemophilia;
Draft Guidance for Industry;’’ or Docket
No. FDA–2018–D–2258 for ‘‘Human
Gene Therapy for Rare Diseases; Draft
Guidance for Industry.’’ Received
comments, those filed in a timely
manner (see ADDRESSES), will be placed
in the docket and, except for those
submitted as ‘‘Confidential
Submissions,’’ publicly viewable at
https://www.regulations.gov or at the
Dockets Management Staff between
9 a.m. and 4 p.m., Monday through
Friday.
• Confidential Submissions—To
submit a comment with confidential
information that you do not wish to be
made publicly available, submit your
comments only as a written/paper
submission. You should submit two
copies total. One copy will include the
information you claim to be confidential
with a heading or cover note that states
‘‘THIS DOCUMENT CONTAINS
CONFIDENTIAL INFORMATION.’’ The
Agency will review this copy, including
the claimed confidential information, in
its consideration of comments. The
second copy, which will have the
claimed confidential information
redacted/blacked out, will be available
for public viewing and posted on
https://www.regulations.gov. Submit
both copies to the Dockets Management
Staff. If you do not wish your name and
contact information to be made publicly
available, you can provide this
information on the cover sheet and not
in the body of your comments and you
must identify this information as
‘‘confidential.’’ Any information marked
as ‘‘confidential’’ will not be disclosed
except in accordance with 21 CFR 10.20
and other applicable disclosure law. For
more information about FDA’s posting
of comments to public dockets, see 80
FR 56469, September 18, 2015, or access
the information at: https://www.gpo.gov/
fdsys/pkg/FR-2015-09-18/pdf/201523389.pdf.
Docket: For access to the docket to
read background documents or the
electronic and written/paper comments
received, go to https://
www.regulations.gov and insert the
docket number, found in brackets in the
heading of this document, into the
‘‘Search’’ box and follow the prompts
and/or go to the Dockets Management
Staff, 5630 Fishers Lane, Rm. 1061,
Rockville, MD 20852.
FOR FURTHER INFORMATION CONTACT:
Jenifer Stach, Center for Biologics
Evaluation and Research, Food and
Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 7301,
Silver Spring, MD 20993–0002, 240–
402–7911.
SUPPLEMENTARY INFORMATION:
I. Background
In the Federal Register of July 12,
2018, FDA published notices of
availability with a 90-day comment
period for six draft guidance documents
listed in the following table. Three of
the six draft guidance documents
provide recommendations to
stakeholders developing gene therapies
for retinal disorders, hemophilia, and
rare diseases. The remaining three
guidance documents provide
recommendations to sponsors
manufacturing gene therapies; namely,
how to provide chemistry,
manufacturing and controls information
for gene therapy products, additional
recommendations regarding the testing
for replication competent retrovirus
during the manufacture of retroviral
vector-based gene therapy products and
during the follow-up monitoring of
patients who received retroviral vectorbased gene therapy products, and
recommendations regarding the design
of long-term follow-up observational
studies for the collection of data on
delayed adverse events following
administration of a gene therapy
product. Comments were requested on
these draft guidances by October 10,
2018.
daltland on DSKBBV9HB2PROD with NOTICES
SIX DRAFT GUIDANCES PUBLISHED JULY 12, 2018
Docket No.
Draft guidance document title
FR cite
FDA–1999–D–0081 ........
Testing of Retroviral Vector-Based Human Gene Therapy Products for Replication Competent
Retrovirus During Product Manufacture and Patient Follow-up; Draft Guidance for Industry.
Chemistry, Manufacturing, and Control Information for Human Gene Therapy Investigational New
Drug Applications; Draft Guidance for Industry.
Long Term Follow-Up After Administration of Human Gene Therapy Products; Draft Guidance for Industry.
Human Gene Therapy for Retinal Disorders; Draft Guidance for Industry .............................................
Human Gene Therapy for Hemophilia; Draft Guidance for Industry .......................................................
83 FR 32309
FDA–2008–D–0205 ........
FDA–2018–D–2173 ........
FDA–2018–D–2236 ........
FDA–2018–D–2238 ........
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83 FR 32307
83 FR 32311
83 FR 32302
83 FR 32306
Federal Register / Vol. 83, No. 173 / Thursday, September 6, 2018 / Notices
45251
SIX DRAFT GUIDANCES PUBLISHED JULY 12, 2018—Continued
Docket No.
Draft guidance document title
FR cite
FDA–2018–D–2258 ........
Human Gene Therapy for Rare Diseases; Draft Guidance for Industry .................................................
83 FR 32303
The Agency has received requests for
a 60-day extension of the comment
period for the six draft guidance
documents. These requests conveyed
concern that the current 90-day
comment period does not allow
sufficient time to develop a meaningful
or thoughtful response to the draft
guidance documents.
FDA has considered these requests
and is extending the comment period
for the six draft guidance documents for
60 days, until December 10, 2018. The
Agency believes that a 60-day extension
allows adequate time for interested
persons to submit comments.
II. References
The following references are on
display in the Dockets Management
Staff (see ADDRESSES) and are available
for viewing by interested persons
between 9 a.m. and 4 p.m., Monday
through Friday; they are also available
electronically at https://
www.regulations.gov.
1. Letter from Robert Falb, Director, U.S.
Policy and Advocacy, Alliance for
Regenerative Medicine, to Dr. Peter
Marks, Director, Center for Biologics
Evaluation and Research, FDA (July 23,
2018).
2. Letter from Sesquile Ramon, Ph.D.,
Director, Science and Regulatory Affairs,
Biotechnology Innovation Organization,
to FDA Dockets Management Staff
(August 3, 2018).
Dated: August 29, 2018.
Leslie Kux,
Associate Commissioner for Policy.
BILLING CODE 4164–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
daltland on DSKBBV9HB2PROD with NOTICES
[Docket No. FDA–2011–D–0147]
Agency Information Collection
Activities; Proposed Collection;
Comment Request; Guidance for
Industry and Food and Drug
Administration Staff; Section 905(j)
Reports: Demonstrating Substantial
Equivalence for Tobacco Products
Food and Drug Administration,
HHS.
ACTION:
Notice.
VerDate Sep<11>2014
16:56 Sep 05, 2018
Jkt 244001
Submit either electronic or
written comments on the collection of
information by November 5, 2018.
DATES:
You may submit comments
as follows. Please note that late,
untimely filed comments will not be
considered. Electronic comments must
be submitted on or before November 5,
2018. The https://www.regulations.gov
electronic filing system will accept
comments until midnight Eastern Time
at the end of November 5, 2018.
Comments received by mail/hand
delivery/courier (for written/paper
submissions) will be considered timely
if they are postmarked or the delivery
service acceptance receipt is on or
before that date.
ADDRESSES:
Electronic Submissions
[FR Doc. 2018–19303 Filed 9–5–18; 8:45 am]
AGENCY:
The Food and Drug
Administration (FDA or Agency) is
announcing an opportunity for public
comment on the proposed collection of
certain information by the Agency.
Under the Paperwork Reduction Act of
1995 (PRA), Federal Agencies are
required to publish notice in the
FEDERAL REGISTER concerning each
proposed collection of information,
including each proposed extension of an
existing collection of information, and
to allow 60 days for public comment in
response to the notice. This notice
solicits comments on ‘‘Guidance for
Industry and Food and Drug
Administration Staff; Section 905(j)
Reports: Demonstrating Substantial
Equivalence for Tobacco Products.’’
SUMMARY:
Submit electronic comments in the
following way:
• Federal eRulemaking Portal:
https://www.regulations.gov. Follow the
instructions for submitting comments.
Comments submitted electronically,
including attachments, to https://
www.regulations.gov will be posted to
the docket unchanged. Because your
comment will be made public, you are
solely responsible for ensuring that your
comment does not include any
confidential information that you or a
third party may not wish to be posted,
such as medical information, your or
anyone else’s Social Security number, or
confidential business information, such
as a manufacturing process. Please note
that if you include your name, contact
information, or other information that
identifies you in the body of your
PO 00000
Frm 00046
Fmt 4703
Sfmt 4703
comments, that information will be
posted on https://www.regulations.gov.
• If you want to submit a comment
with confidential information that you
do not wish to be made available to the
public, submit the comment as a
written/paper submission and in the
manner detailed (see ‘‘Written/Paper
Submissions’’ and ‘‘Instructions’’).
Written/Paper Submissions
Submit written/paper submissions as
follows:
• Mail/Hand Delivery/Courier (for
written/paper submissions): Dockets
Management Staff (HFA–305), Food and
Drug Administration, 5630 Fishers
Lane, Rm. 1061, Rockville, MD 20852.
• For written/paper comments
submitted to the Dockets Management
Staff, FDA will post your comment, as
well as any attachments, except for
information submitted, marked and
identified, as confidential, if submitted
as detailed in ‘‘Instructions.’’
Instructions: All submissions received
must include the Docket No. FDA–
2011–D–0147 for ‘‘Guidance for
Industry and Food and Drug
Administration Staff; Section 905(j)
Reports: Demonstrating Substantial
Equivalence for Tobacco Products.’’
Received comments, those filed in a
timely manner (see ADDRESSES), will be
placed in the docket and, except for
those submitted as ‘‘Confidential
Submissions,’’ publicly viewable at
https://www.regulations.gov or at the
Dockets Management Staff between 9
a.m. and 4 p.m., Monday through
Friday.
• Confidential Submissions—To
submit a comment with confidential
information that you do not wish to be
made publicly available, submit your
comments only as a written/paper
submission. You should submit two
copies total. One copy will include the
information you claim to be confidential
with a heading or cover note that states
‘‘THIS DOCUMENT CONTAINS
CONFIDENTIAL INFORMATION.’’ The
Agency will review this copy, including
the claimed confidential information, in
its consideration of comments. The
second copy, which will have the
claimed confidential information
redacted/blacked out, will be available
for public viewing and posted on
https://www.regulations.gov. Submit
both copies to the Dockets Management
Staff. If you do not wish your name and
E:\FR\FM\06SEN1.SGM
06SEN1
Agencies
[Federal Register Volume 83, Number 173 (Thursday, September 6, 2018)]
[Notices]
[Pages 45249-45251]
From the Federal Register Online via the Government Publishing Office [www.gpo.gov]
[FR Doc No: 2018-19303]
-----------------------------------------------------------------------
DEPARTMENT OF HEALTH AND HUMAN SERVICES
Food and Drug Administration
[Docket Nos. FDA-1999-D-0081, FDA-2008-D-0205, FDA-2018-D-2173, FDA-
2018-D-2236, FDA-2018-D-2238, and FDA-2018-D-2258]
Draft Guidances Relating to the Development of Human Gene Therapy
Products; Availability; Extension of Comment Period
AGENCY: Food and Drug Administration, HHS.
ACTION: Notification; extension of comment period.
-----------------------------------------------------------------------
SUMMARY: The Food and Drug Administration (FDA or the Agency) is
extending the comment period for the notices of availability for six
draft guidance documents relating to the development of human gene
therapy products that appeared in the Federal Register of July 12,
2018. The Agency is taking this action in response to requests for an
extension to allow interested persons additional time to submit
comments and any new information.
DATES: FDA is extending the comment period on the six documents that
published on July 12, 2018 (see SUPPLEMENTARY INFORMATION). Submit
either electronic or written comments by December 10, 2018, to ensure
that the Agency considers your comment on these draft guidances before
it begins work on the final version of the guidances.
ADDRESSES: You may submit comments as follows. Please note that late,
untimely filed comments will not be considered. Electronic comments
must be submitted on or before December 10, 2018. The https://www.regulations.gov electronic filing system will accept comments until
midnight Eastern Time at the end of December 10, 2018. Comments
received by mail/hand delivery/courier (for written/paper submissions)
will be considered timely if they are postmarked or the delivery
service acceptance receipt is on or before that date.
[[Page 45250]]
Electronic Submissions
Submit electronic comments in the following way:
Federal eRulemaking Portal: https://www.regulations.gov.
Follow the instructions for submitting comments. Comments submitted
electronically, including attachments, to https://www.regulations.gov
will be posted to the docket unchanged. Because your comment will be
made public, you are solely responsible for ensuring that your comment
does not include any confidential information that you or a third party
may not wish to be posted, such as medical information, your or anyone
else's Social Security number, or confidential business information,
such as a manufacturing process. Please note that if you include your
name, contact information, or other information that identifies you in
the body of your comments, that information will be posted on https://www.regulations.gov.
If you want to submit a comment with confidential
information that you do not wish to be made available to the public,
submit the comment as a written/paper submission and in the manner
detailed (see ``Written/Paper Submissions'' and ``Instructions'').
Written/Paper Submissions
Submit written/paper submissions as follows:
Mail/Hand delivery/Courier (for written/paper
submissions): Dockets Management Staff (HFA-305), Food and Drug
Administration, 5630 Fishers Lane, Rm. 1061, Rockville, MD 20852.
For written/paper comments submitted to the Dockets
Management Staff, FDA will post your comment, as well as any
attachments, except for information submitted, marked and identified,
as confidential, if submitted as detailed in ``Instructions.''
Instructions: All submissions received must include the Docket No.
FDA-1999-D-0081 for ``Testing of Retroviral Vector-Based Human Gene
Therapy Products for Replication Competent Retrovirus During Product
Manufacture and Patient Follow-up; Draft Guidance for Industry;''
Docket No. FDA-2008-D-0205 for ``Chemistry, Manufacturing, and Control
Information for Human Gene Therapy Investigational New Drug
Applications; Draft Guidance for Industry;'' Docket No. FDA-2018-D-2173
for ``Long Term Follow-Up After Administration of Human Gene Therapy
Products; Draft Guidance for Industry;'' Docket No. FDA-2018-D-2236 for
``Human Gene Therapy for Retinal Disorders; Draft Guidance for
Industry;'' Docket No. FDA-2018-D-2238 for ``Human Gene Therapy for
Hemophilia; Draft Guidance for Industry;'' or Docket No. FDA-2018-D-
2258 for ``Human Gene Therapy for Rare Diseases; Draft Guidance for
Industry.'' Received comments, those filed in a timely manner (see
ADDRESSES), will be placed in the docket and, except for those
submitted as ``Confidential Submissions,'' publicly viewable at https://www.regulations.gov or at the Dockets Management Staff between 9 a.m.
and 4 p.m., Monday through Friday.
Confidential Submissions--To submit a comment with
confidential information that you do not wish to be made publicly
available, submit your comments only as a written/paper submission. You
should submit two copies total. One copy will include the information
you claim to be confidential with a heading or cover note that states
``THIS DOCUMENT CONTAINS CONFIDENTIAL INFORMATION.'' The Agency will
review this copy, including the claimed confidential information, in
its consideration of comments. The second copy, which will have the
claimed confidential information redacted/blacked out, will be
available for public viewing and posted on https://www.regulations.gov.
Submit both copies to the Dockets Management Staff. If you do not wish
your name and contact information to be made publicly available, you
can provide this information on the cover sheet and not in the body of
your comments and you must identify this information as
``confidential.'' Any information marked as ``confidential'' will not
be disclosed except in accordance with 21 CFR 10.20 and other
applicable disclosure law. For more information about FDA's posting of
comments to public dockets, see 80 FR 56469, September 18, 2015, or
access the information at: https://www.gpo.gov/fdsys/pkg/FR-2015-09-18/pdf/2015-23389.pdf.
Docket: For access to the docket to read background documents or
the electronic and written/paper comments received, go to https://www.regulations.gov and insert the docket number, found in brackets in
the heading of this document, into the ``Search'' box and follow the
prompts and/or go to the Dockets Management Staff, 5630 Fishers Lane,
Rm. 1061, Rockville, MD 20852.
FOR FURTHER INFORMATION CONTACT: Jenifer Stach, Center for Biologics
Evaluation and Research, Food and Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 7301, Silver Spring, MD 20993-0002, 240-
402-7911.
SUPPLEMENTARY INFORMATION:
I. Background
In the Federal Register of July 12, 2018, FDA published notices of
availability with a 90-day comment period for six draft guidance
documents listed in the following table. Three of the six draft
guidance documents provide recommendations to stakeholders developing
gene therapies for retinal disorders, hemophilia, and rare diseases.
The remaining three guidance documents provide recommendations to
sponsors manufacturing gene therapies; namely, how to provide
chemistry, manufacturing and controls information for gene therapy
products, additional recommendations regarding the testing for
replication competent retrovirus during the manufacture of retroviral
vector-based gene therapy products and during the follow-up monitoring
of patients who received retroviral vector-based gene therapy products,
and recommendations regarding the design of long-term follow-up
observational studies for the collection of data on delayed adverse
events following administration of a gene therapy product. Comments
were requested on these draft guidances by October 10, 2018.
Six Draft Guidances Published July 12, 2018
------------------------------------------------------------------------
Draft guidance
Docket No. document title FR cite
------------------------------------------------------------------------
FDA-1999-D-0081................ Testing of Retroviral 83 FR 32309
Vector-Based Human
Gene Therapy
Products for
Replication
Competent Retrovirus
During Product
Manufacture and
Patient Follow-up;
Draft Guidance for
Industry.
FDA-2008-D-0205................ Chemistry, 83 FR 32307
Manufacturing, and
Control Information
for Human Gene
Therapy
Investigational New
Drug Applications;
Draft Guidance for
Industry.
FDA-2018-D-2173................ Long Term Follow-Up 83 FR 32311
After Administration
of Human Gene
Therapy Products;
Draft Guidance for
Industry.
FDA-2018-D-2236................ Human Gene Therapy 83 FR 32302
for Retinal
Disorders; Draft
Guidance for
Industry.
FDA-2018-D-2238................ Human Gene Therapy 83 FR 32306
for Hemophilia;
Draft Guidance for
Industry.
[[Page 45251]]
FDA-2018-D-2258................ Human Gene Therapy 83 FR 32303
for Rare Diseases;
Draft Guidance for
Industry.
------------------------------------------------------------------------
The Agency has received requests for a 60-day extension of the
comment period for the six draft guidance documents. These requests
conveyed concern that the current 90-day comment period does not allow
sufficient time to develop a meaningful or thoughtful response to the
draft guidance documents.
FDA has considered these requests and is extending the comment
period for the six draft guidance documents for 60 days, until December
10, 2018. The Agency believes that a 60-day extension allows adequate
time for interested persons to submit comments.
II. References
The following references are on display in the Dockets Management
Staff (see ADDRESSES) and are available for viewing by interested
persons between 9 a.m. and 4 p.m., Monday through Friday; they are also
available electronically at https://www.regulations.gov.
1. Letter from Robert Falb, Director, U.S. Policy and Advocacy,
Alliance for Regenerative Medicine, to Dr. Peter Marks, Director,
Center for Biologics Evaluation and Research, FDA (July 23, 2018).
2. Letter from Sesquile Ramon, Ph.D., Director, Science and
Regulatory Affairs, Biotechnology Innovation Organization, to FDA
Dockets Management Staff (August 3, 2018).
Dated: August 29, 2018.
Leslie Kux,
Associate Commissioner for Policy.
[FR Doc. 2018-19303 Filed 9-5-18; 8:45 am]
BILLING CODE 4164-01-P