Recommendations for Microbial Vectors Used for Gene Therapy; Draft Guidance for Industry; Availability, 61822-61824 [2015-26108]
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61822
Federal Register / Vol. 80, No. 198 / Wednesday, October 14, 2015 / Notices
Dated: October 7, 2015.
Leslie Kux,
Associate Commissioner for Policy.
do not wish to be made available to the
public, submit the comment as a
written/paper submission and in the
manner detailed (see ‘‘Written/Paper
Submissions’’ and ‘‘Instructions’’).
[FR Doc. 2015–26055 Filed 10–13–15; 8:45 am]
BILLING CODE 4164–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA–2010–N–0128]
Prescription Drug User Fee Act;
Reopening of Comment Period
AGENCY:
Food and Drug Administration,
HHS.
ACTION:
Notice; reopening of comment
period.
The Food and Drug
Administration (FDA) is reopening until
April 29, 2016, the comment period for
the notice of public meeting that
appeared in the Federal Register of May
13, 2015 (80 FR 27323). In the notice of
public meeting, FDA invited public
comment as the Agency begins the
process to reauthorize the Prescription
Drug User Fee Act (PDUFA) in fiscal
years (FYs) 2018 to 2022. The Agency is
taking this action to allow interested
persons additional time to submit
comments.
DATES: FDA is reopening the comment
period on the notice of public meeting
published May 13, 2015 (80 FR 27323).
Submit either electronic or written
comments by April 29, 2016.
ADDRESSES: You may submit comments
as follows:
tkelley on DSK3SPTVN1PROD with NOTICES
SUMMARY:
Electronic Submissions
Submit electronic comments in the
following way:
• Federal eRulemaking Portal: https://
www.regulations.gov. Follow the
instructions for submitting comments.
Comments submitted electronically,
including attachments, to https://
www.regulations.gov will be posted to
the docket unchanged. Because your
comment will be made public, you are
solely responsible for ensuring that your
comment does not include any
confidential information that you or a
third party may not wish to be posted,
such as medical information, your or
anyone else’s Social Security number, or
confidential business information, such
as a manufacturing process. Please note
that if you include your name, contact
information, or other information that
identifies you in the body of your
comments, that information will be
posted on https://www.regulations.gov.
• If you want to submit a comment
with confidential information that you
VerDate Sep<11>2014
16:39 Oct 13, 2015
Jkt 238001
Written/Paper Submissions
Submit written/paper submissions as
follows:
• Mail/Hand delivery/Courier (for
written/paper submissions): Division of
Dockets Management (HFA–305), Food
and Drug Administration, 5630 Fishers
Lane, Rm. 1061, Rockville, MD 20852.
• For written/paper comments
submitted to the Division of Dockets
Management, FDA will post your
comment, as well as any attachments,
except for information submitted,
marked and identified, as confidential,
if submitted as detailed in
‘‘Instructions.’’
Instructions: All submissions received
must include the Docket No. FDA–
2010–N–0128 for ‘‘Prescription Drug
User Fee Act; Reopening of Comment
Period.’’ Received comments will be
placed in the docket and, except for
those submitted as ‘‘Confidential
Submissions,’’ publicly viewable at
https://www.regulations.gov or at the
Division of Dockets Management
between 9 a.m. and 4 p.m., Monday
through Friday.
• Confidential Submissions—To
submit a comment with confidential
information that you do not wish to be
made publicly available, submit your
comments only as a written/paper
submission. You should submit two
copies total. One copy will include the
information you claim to be confidential
with a heading or cover note that states
‘‘THIS DOCUMENT CONTAINS
CONFIDENTIAL INFORMATION’’. The
Agency will review this copy, including
the claimed confidential information, in
its consideration of comments. The
second copy, which will have the
claimed confidential information
redacted/blacked out, will be available
for public viewing and posted on https://
www.regulations.gov. Submit both
copies to the Division of Dockets
Management. If you do not wish your
name and contact information to be
made publicly available, you can
provide this information on the cover
sheet and not in the body of your
comments and you must identify this
information as ‘‘confidential.’’ Any
information marked as ‘‘confidential’’
will not be disclosed except in
accordance with 21 CFR 10.20 and other
applicable disclosure law. For more
information about FDA’s posting of
comments to public dockets, see 80 FR
56469, September 18, 2015, or access
the information at: https://www.fda.gov/
PO 00000
Frm 00033
Fmt 4703
Sfmt 4703
regulatoryinformation/dockets/
default.htm.
Docket: For access to the docket to
read background documents or the
electronic and written/paper comments
received, go to https://
www.regulations.gov and insert the
docket number, found in brackets in the
heading of this document, into the
‘‘Search’’ box and follow the prompts
and/or go to the Division of Dockets
Management, 5630 Fishers Lane, Rm.
1061, Rockville, MD 20852.
FOR FURTHER INFORMATION CONTACT:
Graham Thompson, Center for Drug
Evaluation and Research, Food and
Drug Administration, 10903 New
Hampshire Ave., Bldg. 51, Rm. 1146,
Silver Spring, MD 20993–0002, 301–
796–5003.
SUPPLEMENTARY INFORMATION: In the
Federal Register of May 13, 2015, FDA
published a notice of public meeting
with a 30-day comment period
following the public meeting and
invited comments as the Agency began
the process to reauthorize PDUFA in
FYs 2018 to 2022.
FDA is reopening the comment period
until April 29, 2016. The Agency
believes that reopening the comment
period for the notice of public meeting
will allow adequate time for interested
persons to submit comments.
Dated: October 7, 2015.
Leslie Kux,
Associate Commissioner for Policy.
[FR Doc. 2015–26052 Filed 10–13–15; 8:45 am]
BILLING CODE 4164–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA–2015–D–3399]
Recommendations for Microbial
Vectors Used for Gene Therapy; Draft
Guidance for Industry; Availability
AGENCY:
Food and Drug Administration,
HHS.
ACTION:
Notice.
The Food and Drug
Administration (FDA or Agency) is
announcing the availability of a draft
document entitled ‘‘Recommendations
for Microbial Vectors Used for Gene
Therapy; Draft Guidance for Industry.’’
The draft guidance provides
investigational new drug application
(IND) sponsors, with recommendations
concerning IND submissions for
microbial vectors used for gene therapy
(MVGTs) in early-phase clinical trials.
MVGTs meet the regulatory definition of
SUMMARY:
E:\FR\FM\14OCN1.SGM
14OCN1
Federal Register / Vol. 80, No. 198 / Wednesday, October 14, 2015 / Notices
‘‘biological product’’, when such
products are applicable to the
prevention, treatment, or cure of a
disease or condition of human beings.
The draft guidance focuses on the
chemistry, manufacturing, and control
(CMC) information that sponsors should
submit in an IND for MVGTs and
provides an overview of preclinical and
clinical considerations for these
products. The draft guidance, when
finalized, will supplement the guidance
entitled, ‘‘Guidance for FDA Reviewers
and Sponsors: Content and Review of
Chemistry, Manufacturing, and Control
(CMC) Information for Human Gene
Therapy Investigational New Drug
Applications (INDs),’’ dated April 2008
(April 2008 Guidance).
DATES: Although you can comment on
any guidance at any time (see 21 CFR
10.115(g)(5)), to ensure that the Agency
considers your comment on this draft
guidance before it begins work on the
final version of the guidance, submit
either electronic or written comments
on the draft guidance by December 14,
2015.
ADDRESSES: You may submit comments
as follows:
tkelley on DSK3SPTVN1PROD with NOTICES
Electronic Submissions
Submit electronic comments in the
following way:
• Federal eRulemaking Portal: https://
www.regulations.gov. Follow the
instructions for submitting comments.
Comments submitted electronically,
including attachments, to https://
www.regulations.gov will be posted to
the docket unchanged. Because your
comment will be made public, you are
solely responsible for ensuring that your
comment does not include any
confidential information that you or a
third party may not wish to be posted,
such as medical information, your or
anyone else’s Social Security number, or
confidential business information, such
as a manufacturing process. Please note
that if you include your name, contact
information, or other information that
identifies you in the body of your
comments, that information will be
posted on https://www.regulations.gov.
• If you want to submit a comment
with confidential information that you
do not wish to be made available to the
public, submit the comment as a
written/paper submission and in the
manner detailed (see ‘‘Written/Paper
Submissions’’ and ‘‘Instructions’’).
Written/Paper Submissions
Submit written/paper submissions as
follows:
• Mail/Hand delivery/Courier (for
written/paper submissions): Division of
VerDate Sep<11>2014
16:39 Oct 13, 2015
Jkt 238001
Dockets Management (HFA–305), Food
and Drug Administration, 5630 Fishers
Lane, rm. 1061, Rockville, MD 20852.
• For written/paper comments
submitted to the Division of Dockets
Management, FDA will post your
comment, as well as any attachments,
except for information submitted,
marked and identified, as confidential,
if submitted as detailed in
‘‘Instructions.’’
Instructions: All submissions received
must include the Docket No. FDA–
2015–D–3399 for ‘‘Recommendations
for Microbial Vectors Used for Gene
Therapy; Draft Guidance for Industry.’’
Received comments will be placed in
the docket and, except for those
submitted as ‘‘Confidential
Submissions’’ publicly viewable at
https://www.regulations.gov or at the
Division of Dockets Management
between 9 a.m. and 4 p.m., Monday
through Friday.
• Confidential Submissions—To
submit a comment with confidential
information that you do not wish to be
made publicly available, submit your
comments only as a written/paper
submission. You should submit two
copies total. One copy will include the
information you claim to be confidential
with a heading or cover note that states
‘‘THIS DOCUMENT CONTAINS
CONFIDENTIAL INFORMATION’’. The
Agency will review this copy, including
the claimed confidential information, in
its consideration of comments. The
second copy, which will have the
claimed confidential information
redacted/blacked out, will be available
for public viewing and posted on https://
www.regulations.gov. Submit both
copies to the Division of Dockets
Management. If you do not wish your
name and contact information to be
made publicly available, you can
provide this information on the cover
sheet and not in the body of your
comments and you must identify this
information as ‘‘confidential.’’ Any
information marked as ‘‘confidential’’
will not be disclosed except in
accordance with 21 CFR 10.20 and other
applicable disclosure law. For more
information about FDA’s posting of
comments to public dockets, see 80 FR
56469, September 18, 2015, or access
the information at: https://www.fda.gov/
regulatoryinformation/dockets/
default.htm.
Docket: For access to the docket to
read background documents or the
electronic and written/paper comments
received, go to https://
www.regulations.gov and insert the
docket number, found in brackets in the
heading of this document, into the
‘‘Search’’ box and follow the prompts
PO 00000
Frm 00034
Fmt 4703
Sfmt 4703
61823
and/or go to the Division of Dockets
Management, 5630 Fishers Lane, Rm.
1061, Rockville, MD 20852.
Submit written requests for single
copies of the draft guidance to the Office
of Communication, Outreach and
Development, Center for Biologics
Evaluation and Research (CBER), Food
and Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, Rm. 3128,
Silver Spring, MD 20993–0002. Send
one self-addressed adhesive label to
assist the office in processing your
requests. The draft guidance may also be
obtained by mail by calling CBER at 1–
800–835–4709 or 240–402–8010. See
the SUPPLEMENTARY INFORMATION section
for electronic access to the draft
guidance document.
FOR FURTHER INFORMATION CONTACT: Paul
E. Levine, Jr., Center for Biologics
Evaluation and Research, Food and
Drug Administration, 10903 New
Hampshire Ave., Bldg. 71, rm. 7301,
Silver Spring, MD 20993–0002, 240–
402–7911.
SUPPLEMENTARY INFORMATION:
I. Background
FDA is announcing the availability of
a draft document entitled,
‘‘Recommendations for Microbial
Vectors Used for Gene Therapy; Draft
Guidance for Industry.’’ The draft
guidance provides IND sponsors, with
recommendations concerning IND
submissions for MVGTs in early-phase
clinical trials. MVGTs meet the
definition of ‘‘biological product’’ in
section 351(i) of the Public Health
Service Act (42 U.S.C. 262), when such
products are applicable to the
prevention, treatment, or cure of a
disease or condition of human beings.
MVGTs include bacterial vectors such
as Salmonella, Listeria, or E. coli
genetically modified to express human
tumor antigens, cytokines, growth
factors, enzymes, therapeutic proteins,
or nucleotides. MVGTs may also be
generated by the modification (deletion,
truncation, or point mutation) of
chromosomal or episomal genes and by
the insertion of foreign genetic material
into the chromosome, or into naturally
occurring episomes; or by the
introduction of one or more plasmids.
The MVGTs may consist of microbes
that are either live, replication restricted
(division under specific growth
conditions), capable of limited or no cell
divisions, or killed, or a combination of
these forms. The guidance focuses on
the CMC information that sponsors
should submit in an IND for MVGTs and
provides an overview of preclinical and
clinical considerations for these
products.
E:\FR\FM\14OCN1.SGM
14OCN1
61824
Federal Register / Vol. 80, No. 198 / Wednesday, October 14, 2015 / Notices
In the Federal Register of April 10,
2008 (73 FR 19511), FDA announced the
availability of the April 2008 Guidance.
In that guidance, FDA provided
sponsors of a human gene therapy IND,
including those with combination
products that contain a human gene
therapy biological product with a drug
or device as part of the final product,
with recommendations on CMC
information that is to be included in an
original IND. That guidance also
provided instruction to FDA CMC
reviewers about the information to
record and assess as part of an IND
review. The draft guidance, when
finalized, will supplement the April
2008 Guidance.
The draft guidance is being issued
consistent with FDA’s good guidance
practices regulation (21 CFR 10.115).
The draft guidance, when finalized, will
represent FDA’s current thinking on
recommendations for MVGTs. It does
not establish any rights for or on any
person and does not operate to bind
FDA or the public. An alternative
approach may be used if such approach
satisfies the requirement of the
applicable statutes and regulations.
II. Paperwork Reduction Act of 1995
The draft guidance refers to
previously approved collections of
information found in FDA regulations.
These collections of information are
subject to review by the Office of
Management and Budget (OMB) under
the Paperwork Reduction Act of 1995
(44 U.S.C. 3501–3520). The collections
of information in 21 CFR parts 211, 610,
and 312 have been approved under
OMB control numbers 0910–0139 and
0910–0114, respectively.
III. Electronic Access
Persons with access to the Internet
may obtain the draft guidance at either
https://www.fda.gov/
BiologicsBloodVaccines/
GuidanceCompliance
RegulatoryInformation/Guidances/
default.htm or https://
www.regulations.gov.
tkelley on DSK3SPTVN1PROD with NOTICES
Dated: October 7, 2015.
Leslie Kux,
Associate Commissioner for Policy.
[FR Doc. 2015–26108 Filed 10–13–15; 8:45 am]
BILLING CODE 4164–01–P
VerDate Sep<11>2014
16:39 Oct 13, 2015
Jkt 238001
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Health Resources and Service
Administration
Advisory Committee on Training in
Primary Care Medicine and Dentistry;
Notice of Meeting
In accordance with section 10(a)(2) of
the Federal Advisory Committee Act
(Public Law 92–463), notice is hereby
given of the following meeting:
Name: Council on Graduate Medical
Education (COGME).
Dates and Times: October 29, 2015
(10:30 a.m.–4:30 p.m.).
Place: Conference Call/Webinar
Format.
Status: The meeting will be open to
the public.
Purpose: The COGME provides advice
and recommendations to the Secretary
of the Department of Health and Human
Services (the Secretary) on a range of
issues including the supply and
distribution of physicians in the United
States, current and future physician
shortages or excesses, issues relating to
foreign medical school graduates, the
nature and financing of medical
education training, and the
development of performance measures
and longitudinal evaluation of medical
education programs. COGME’s reports
are submitted to the Secretary and
ranking members of the Senate
Committee on Health, Education, Labor,
and Pensions and the House of
Representatives Committee on Energy
and Commerce.
HRSA will conduct an orientation for
new members prior to the start of the
meeting. COGME will start its official
meeting at 10:30 a.m. After the
orientation, discussion will focus on
one of the recommendations from the
March 2015 meeting, namely, to identify
actions COGME can take within its
current authorities to achieve the
development of a National Strategic
Plan for Graduate Medical Education.
Agenda: The COGME agenda will be
available 2 days prior to the meeting on
the HRSA Web site at https://
www.hrsa.gov/advisorycommittees/
bhpradvisory/cogme/.
SUPPLEMENTARY INFORMATION: Requests
to make oral comments or provide
written comments to the COGME should
be sent to Dr. Joan Weiss, Designated
Federal Official, using the address and
phone number below. Individuals who
plan to participate on the conference
call and webinar should notify Dr.
Weiss at least 3 days prior to the
meeting, using the address and phone
number below. Members of the public
PO 00000
Frm 00035
Fmt 4703
Sfmt 4703
will have the opportunity to provide
comments. Interested parties should
refer to the meeting subject as the HRSA
Council on Graduate Medical
Education.
• The conference call-in number is 1–
800–619–2521. The passcode is:
9271697.
• The webinar link is https://
hrsa.connectsolutions.com/
cogme-2015/.
Contact: Anyone requesting
information regarding the COGME
should contact Dr. Joan Weiss,
Designated Federal Official within the
Bureau of Health Workforce, Health
Resources and Services Administration,
in one of three ways: (1) Send a request
to the following address: Dr. Joan Weiss,
Designated Federal Official, Bureau of
Health Workforce, Health Resources and
Services Administration, Parklawn
Building, Room 12C–05, 5600 Fishers
Lane, Rockville, Maryland 20857; (2)
call (301) 443–0430; or (3) send an email
to jweiss@hrsa.gov.
Jackie Painter,
Director, Division of the Executive Secretariat.
[FR Doc. 2015–26053 Filed 10–13–15; 8:45 am]
BILLING CODE 4165–15–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Office of the Secretary
[Document Identifier: HHS–OS–0990–New–
30D]
Agency Information Collection
Activities; Submission to OMB for
Review and Approval; Public Comment
Request
Office of the Secretary, HHS.
Notice.
AGENCY:
ACTION:
In compliance with section
3507(a)(1)(D) of the Paperwork
Reduction Act of 1995, the Office of the
Secretary (OS), Department of Health
and Human Services, has submitted an
Information Collection Request (ICR),
described below, to the Office of
Management and Budget (OMB) for
review and approval. The ICR is for a
new collection. Comments submitted
during the first public review of this ICR
will be provided to OMB. OMB will
accept further comments from the
public on this ICR during the review
and approval period.
DATES: Comments on the ICR must be
received on or before November 13,
2015.
ADDRESSES: Submit your comments to
OIRA_submission@omb.eop.gov or via
facsimile to (202) 395–5806.
SUMMARY:
E:\FR\FM\14OCN1.SGM
14OCN1
Agencies
[Federal Register Volume 80, Number 198 (Wednesday, October 14, 2015)]
[Notices]
[Pages 61822-61824]
From the Federal Register Online via the Government Publishing Office [www.gpo.gov]
[FR Doc No: 2015-26108]
-----------------------------------------------------------------------
DEPARTMENT OF HEALTH AND HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA-2015-D-3399]
Recommendations for Microbial Vectors Used for Gene Therapy;
Draft Guidance for Industry; Availability
AGENCY: Food and Drug Administration, HHS.
ACTION: Notice.
-----------------------------------------------------------------------
SUMMARY: The Food and Drug Administration (FDA or Agency) is announcing
the availability of a draft document entitled ``Recommendations for
Microbial Vectors Used for Gene Therapy; Draft Guidance for Industry.''
The draft guidance provides investigational new drug application (IND)
sponsors, with recommendations concerning IND submissions for microbial
vectors used for gene therapy (MVGTs) in early-phase clinical trials.
MVGTs meet the regulatory definition of
[[Page 61823]]
``biological product'', when such products are applicable to the
prevention, treatment, or cure of a disease or condition of human
beings. The draft guidance focuses on the chemistry, manufacturing, and
control (CMC) information that sponsors should submit in an IND for
MVGTs and provides an overview of preclinical and clinical
considerations for these products. The draft guidance, when finalized,
will supplement the guidance entitled, ``Guidance for FDA Reviewers and
Sponsors: Content and Review of Chemistry, Manufacturing, and Control
(CMC) Information for Human Gene Therapy Investigational New Drug
Applications (INDs),'' dated April 2008 (April 2008 Guidance).
DATES: Although you can comment on any guidance at any time (see 21 CFR
10.115(g)(5)), to ensure that the Agency considers your comment on this
draft guidance before it begins work on the final version of the
guidance, submit either electronic or written comments on the draft
guidance by December 14, 2015.
ADDRESSES: You may submit comments as follows:
Electronic Submissions
Submit electronic comments in the following way:
Federal eRulemaking Portal: https://www.regulations.gov.
Follow the instructions for submitting comments. Comments submitted
electronically, including attachments, to https://www.regulations.gov
will be posted to the docket unchanged. Because your comment will be
made public, you are solely responsible for ensuring that your comment
does not include any confidential information that you or a third party
may not wish to be posted, such as medical information, your or anyone
else's Social Security number, or confidential business information,
such as a manufacturing process. Please note that if you include your
name, contact information, or other information that identifies you in
the body of your comments, that information will be posted on https://www.regulations.gov.
If you want to submit a comment with confidential
information that you do not wish to be made available to the public,
submit the comment as a written/paper submission and in the manner
detailed (see ``Written/Paper Submissions'' and ``Instructions'').
Written/Paper Submissions
Submit written/paper submissions as follows:
Mail/Hand delivery/Courier (for written/paper
submissions): Division of Dockets Management (HFA-305), Food and Drug
Administration, 5630 Fishers Lane, rm. 1061, Rockville, MD 20852.
For written/paper comments submitted to the Division of
Dockets Management, FDA will post your comment, as well as any
attachments, except for information submitted, marked and identified,
as confidential, if submitted as detailed in ``Instructions.''
Instructions: All submissions received must include the Docket No.
FDA-2015-D-3399 for ``Recommendations for Microbial Vectors Used for
Gene Therapy; Draft Guidance for Industry.'' Received comments will be
placed in the docket and, except for those submitted as ``Confidential
Submissions'' publicly viewable at https://www.regulations.gov or at the
Division of Dockets Management between 9 a.m. and 4 p.m., Monday
through Friday.
Confidential Submissions--To submit a comment with
confidential information that you do not wish to be made publicly
available, submit your comments only as a written/paper submission. You
should submit two copies total. One copy will include the information
you claim to be confidential with a heading or cover note that states
``THIS DOCUMENT CONTAINS CONFIDENTIAL INFORMATION''. The Agency will
review this copy, including the claimed confidential information, in
its consideration of comments. The second copy, which will have the
claimed confidential information redacted/blacked out, will be
available for public viewing and posted on https://www.regulations.gov.
Submit both copies to the Division of Dockets Management. If you do not
wish your name and contact information to be made publicly available,
you can provide this information on the cover sheet and not in the body
of your comments and you must identify this information as
``confidential.'' Any information marked as ``confidential'' will not
be disclosed except in accordance with 21 CFR 10.20 and other
applicable disclosure law. For more information about FDA's posting of
comments to public dockets, see 80 FR 56469, September 18, 2015, or
access the information at: https://www.fda.gov/regulatoryinformation/dockets/default.htm.
Docket: For access to the docket to read background documents or
the electronic and written/paper comments received, go to https://www.regulations.gov and insert the docket number, found in brackets in
the heading of this document, into the ``Search'' box and follow the
prompts and/or go to the Division of Dockets Management, 5630 Fishers
Lane, Rm. 1061, Rockville, MD 20852.
Submit written requests for single copies of the draft guidance to
the Office of Communication, Outreach and Development, Center for
Biologics Evaluation and Research (CBER), Food and Drug Administration,
10903 New Hampshire Ave., Bldg. 71, Rm. 3128, Silver Spring, MD 20993-
0002. Send one self-addressed adhesive label to assist the office in
processing your requests. The draft guidance may also be obtained by
mail by calling CBER at 1-800-835-4709 or 240-402-8010. See the
SUPPLEMENTARY INFORMATION section for electronic access to the draft
guidance document.
FOR FURTHER INFORMATION CONTACT: Paul E. Levine, Jr., Center for
Biologics Evaluation and Research, Food and Drug Administration, 10903
New Hampshire Ave., Bldg. 71, rm. 7301, Silver Spring, MD 20993-0002,
240-402-7911.
SUPPLEMENTARY INFORMATION:
I. Background
FDA is announcing the availability of a draft document entitled,
``Recommendations for Microbial Vectors Used for Gene Therapy; Draft
Guidance for Industry.'' The draft guidance provides IND sponsors, with
recommendations concerning IND submissions for MVGTs in early-phase
clinical trials. MVGTs meet the definition of ``biological product'' in
section 351(i) of the Public Health Service Act (42 U.S.C. 262), when
such products are applicable to the prevention, treatment, or cure of a
disease or condition of human beings. MVGTs include bacterial vectors
such as Salmonella, Listeria, or E. coli genetically modified to
express human tumor antigens, cytokines, growth factors, enzymes,
therapeutic proteins, or nucleotides. MVGTs may also be generated by
the modification (deletion, truncation, or point mutation) of
chromosomal or episomal genes and by the insertion of foreign genetic
material into the chromosome, or into naturally occurring episomes; or
by the introduction of one or more plasmids. The MVGTs may consist of
microbes that are either live, replication restricted (division under
specific growth conditions), capable of limited or no cell divisions,
or killed, or a combination of these forms. The guidance focuses on the
CMC information that sponsors should submit in an IND for MVGTs and
provides an overview of preclinical and clinical considerations for
these products.
[[Page 61824]]
In the Federal Register of April 10, 2008 (73 FR 19511), FDA
announced the availability of the April 2008 Guidance. In that
guidance, FDA provided sponsors of a human gene therapy IND, including
those with combination products that contain a human gene therapy
biological product with a drug or device as part of the final product,
with recommendations on CMC information that is to be included in an
original IND. That guidance also provided instruction to FDA CMC
reviewers about the information to record and assess as part of an IND
review. The draft guidance, when finalized, will supplement the April
2008 Guidance.
The draft guidance is being issued consistent with FDA's good
guidance practices regulation (21 CFR 10.115). The draft guidance, when
finalized, will represent FDA's current thinking on recommendations for
MVGTs. It does not establish any rights for or on any person and does
not operate to bind FDA or the public. An alternative approach may be
used if such approach satisfies the requirement of the applicable
statutes and regulations.
II. Paperwork Reduction Act of 1995
The draft guidance refers to previously approved collections of
information found in FDA regulations. These collections of information
are subject to review by the Office of Management and Budget (OMB)
under the Paperwork Reduction Act of 1995 (44 U.S.C. 3501-3520). The
collections of information in 21 CFR parts 211, 610, and 312 have been
approved under OMB control numbers 0910-0139 and 0910-0114,
respectively.
III. Electronic Access
Persons with access to the Internet may obtain the draft guidance
at either https://www.fda.gov/BiologicsBloodVaccines/GuidanceComplianceRegulatoryInformation/Guidances/default.htm or https://www.regulations.gov.
Dated: October 7, 2015.
Leslie Kux,
Associate Commissioner for Policy.
[FR Doc. 2015-26108 Filed 10-13-15; 8:45 am]
BILLING CODE 4164-01-P