Linking Marketplace Heparin Product Attributes and Manufacturing Processes to Bioactivity and Immunogenicity, 36786-36787 [2013-14579]
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Federal Register / Vol. 78, No. 118 / Wednesday, June 19, 2013 / Notices
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[FR Doc. 2013–14589 Filed 6–18–13; 8:45 am]
BILLING CODE 4184–01–P
Food and Drug Administration
[Docket No. FDA–2013–N–0012]
Linking Marketplace Heparin Product
Attributes and Manufacturing
Processes to Bioactivity and
Immunogenicity
Food and Drug Administration,
HHS.
ACTION:
Notice.
The Food and Drug
Administration (FDA) is announcing the
availability of grant funds for the
support of a sole source award to the
University of North Carolina. The goal
of the award is to identify what
component(s) of the complex heparin
mixtures have the propensity to cause
heparin induced thrombocytopenia
(HIT) to improve the safety of heparin
drug products. The FDA seeks to
identify the components of the heparin
mixture that are associated with HIT so
that actions may be taken to reduce
these events and improve patient
outcomes with this widely used drug.
DATES: Important dates are as follows:
1. The application due date is July 15,
2013.
2. The anticipated start date is
August, 2013.
3. The opening date is the date this
announcement is published in the
Federal Register.
4. The expiration date is July 16,
2013.
mstockstill on DSK4VPTVN1PROD with NOTICES
SUMMARY:
Submit the paper
application to: Gladys Melendez at the
Food and Drug Administration, Grants
Management (HFA–500), 5630 Fishers
Lane, Rockville, MD 20857. For more
information, see section III of the
SUPPLEMENTARY INFORMATION section of
this notice.
ADDRESSES:
VerDate Mar<15>2010
17:13 Jun 18, 2013
Jkt 229001
David Keire, Center for Drug Evaluation
and Research, Food and Drug
Administration, 1114 Market St., rm.
1002, St Louis, MO, 63130, 314–539–
3850; or Gladys Melendez, Office of
Acquisition Support and Grant Services,
Food and Drug Administration, 5630
Fishers Lane, Rockville, MD 20857,
301–827–7175, email:
Gladys.bohler@fda.hhs.gov.
For more information on this funding
opportunity announcement (FOA) and
to obtain detailed requirements, please
contact Gladys.bohler @fda.hhs.gov.
SUPPLEMENTARY INFORMATION:
I. Funding Opportunity Description
Request for Application: FDA RFA–
13–007
[Catalog of Federal Domestic
Assistance: 93.103]
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
AGENCY:
FOR FURTHER INFORMATION CONTACT:
A. Background
The goal of this Research Project is to
identify which components of heparin
drug mixtures have the propensity to
cause heparin induced
thrombocytopenia (HIT) in order to
improve the safety profile of this widely
used anticoagulant. Heparin is a
heterogeneous mixture of
polysaccharides of varying length,
sulfation pattern, acylation and
conformation that has been in clinical
use since the 1930s. HIT is a drugdependent immune disorder caused by
antibodies to complexes formed
between platelet factor 4 (PF4) and
heparin which can occur in patients
who undergo major trauma (e.g. broken
bones and cardiovascular surgery) and
receive heparin. The condition leads to
formation of abnormal blood clots and
concomitant complications associated
with clots. PF4-heparin antibodies are
observed in all patients with HIT. In
addition, low molecular weight
heparins or the synthetic
pentasaccharide (fondaparinux) have
also been shown to cause HIT antibody
formation although these smaller chain
length heparins are much less likely to
lead to clinical HIT symptoms.
The major limitation in the available
reagents for studies aimed at identifying
the components of heparin that lead to
the pathogenesis of HIT is the lack of
pure component heparin standards.
Therefore, this collaboration brings
together the following capabilities and
laboratories: (1) Synthesis of heparin
chains of the same length, sulfation
pattern and conformation (Dr. Liu at the
University of North Carolina and Dr.
Linhardt at Rensselaer Polytechnical
Institute), (2) synthesis and
physicochemical characterization of
heparin and heparin-PF4 complexes
PO 00000
Frm 00044
Fmt 4703
Sfmt 4703
(Keire FDA/DPA St Louis) and (3) a
HIT-immunogenicity animal model (Dr.
Arepally at Duke University). FDA
believes that this combination of skills
and expertise has the potential to make
pure standards, fully characterize the
standards, create and characterize PF4heparin standard aggregates and assess
their propensity to elicit an immune
response in an animal model. This
research is unique and not otherwise
available. The ability to make pure
heparin standards in gram quantities
and fully characterize their properties is
only available from the Liu and
Linhardt laboratories. Furthermore, Dr.
Arepally’s mouse model of HIT
immunogenicity is not available in any
other laboratory. When completed the
study will identify heparin components
that enhance HIT propensity and which
could potentially be minimized in
heparin manufacturing, leading to safer
heparin drugs with better patient
outcomes.
B. Research Objectives
The research objective is to identify
the components of the heparin mixture
that have the propensity to lead to HIT
pathogenesis.
C. Eligibility Information
This is a sole source RFA because the
investigators identified in this
document have unique skills and
expertise necessary to perform the
proposed work.
II. Award Information/Funds Available
A. Award Amount
Only one award will be available to
the University of North Carolina in the
amount of $250,000 (Total Cost) in the
first year.
B. Length of Support
Depending on research progress and
subject to the availability of funds
additional funds may be awarded under
this grant for up to a five year project
period reflecting $250,000 Total Cost
per year.
III. Paper Application, Registration,
and Submission Information
To submit a paper application in
response to this FOA, applicants should
first review the full announcement.
Persons interested in applying for a
grant may obtain an application at
https://grants.nih.gov/grants/forms.htm.
For all paper application submissions,
the following steps are required:
• Step 1: Obtain a Dun and Bradstreet
(DUNS) Number
• Step 2: Register With Central
Contractor Registration
E:\FR\FM\19JNN1.SGM
19JNN1
Federal Register / Vol. 78, No. 118 / Wednesday, June 19, 2013 / Notices
• Step 3: Register With Electronic
Research Administration (eRA)
Commons
Steps 1 and 2, in detail, can be found
at https://www07.grants.gov/applicants/
organization_registration.jsp. Step 3, in
detail, can be found at https://
commons.era.nih.gov/commons/
registration/registrationInstructions.jsp.
After you have followed these steps,
submit paper applications to: Gladys
Melendez; Grants Management, Food
and Drug Administration, 5630 Fishers
Lane, rm. 2032; HFA–500; Rockville,
MD 20857.
Dated: June 12, 2013.
Leslie Kux,
Assistant Commissioner for Policy.
[FR Doc. 2013–14579 Filed 6–18–13; 8:45 am]
BILLING CODE 4160–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA–2013–N–0001]
Cardiovascular and Renal Drugs
Advisory Committee; Notice of Meeting
AGENCY:
Food and Drug Administration,
HHS.
mstockstill on DSK4VPTVN1PROD with NOTICES
ACTION:
Notice.
This notice announces a forthcoming
meeting of a public advisory committee
of the Food and Drug Administration
(FDA). The meeting will be open to the
public.
Name of Committee: Cardiovascular
and Renal Drugs Advisory Committee.
General Function of the Committee:
To provide advice and
recommendations to the Agency on
FDA’s regulatory issues.
Date and Time: The meeting will be
held on August 5, 2013, from 8 a.m. to
5:30 p.m.
Location: FDA White Oak Campus,
Building 31, the Great Room, White Oak
Conference Center (Rm. 1503), 10903
New Hampshire Ave., Silver Spring, MD
20993–0002. Information regarding
special accommodations due to a
disability, visitor parking, and
transportation may be accessed at:
https://www.fda.gov/Advisory
Committees/default.htm; under the
heading ‘‘Resources for You,’’ click on
‘‘Public Meetings at the FDA White Oak
Campus.’’ Please note that visitors to the
White Oak Campus must enter through
Building 1.
Contact Person: Kristina Toliver,
Center for Drug Evaluation and
Research, Food and Drug
Administration, 10903 New Hampshire
VerDate Mar<15>2010
17:13 Jun 18, 2013
Jkt 229001
Ave., WO31–2417, Silver Spring, MD
20993–0002, 301–796–9001, FAX: 301–
847–8533, email: CRDAC@fda.hhs.gov,
or FDA Advisory Committee
Information Line, 1–800–741–8138
(301–443–0572 in the Washington, DC
area). A notice in the Federal Register
about last minute modifications that
impact a previously announced
advisory committee meeting cannot
always be published quickly enough to
provide timely notice. Therefore, you
should always check the Agency’s Web
site at https://www.fda.gov/
AdvisoryCommittees/default.htm and
scroll down to the appropriate advisory
committee meeting link, or call the
advisory committee information line to
learn about possible modifications
before coming to the meeting.
Agenda: On August 5, 2013, the
committee will discuss new drug
application (NDA) 204441, tolvaptan
tablets, submitted by Otsuka
Pharmaceutical Company, Ltd., for the
proposed indication of slowing kidney
disease in adults at risk of rapidly
progressing autosomal dominant
polycystic kidney disease (autosomal
dominant polycystic kidney disease is a
genetic disease that affects the kidney
and can lead to kidney failure).
FDA intends to make background
material available to the public no later
than 2 business days before the meeting.
If FDA is unable to post the background
material on its Web site prior to the
meeting, the background material will
be made publicly available at the
location of the advisory committee
meeting, and the background material
will be posted on FDA’s Web site after
the meeting. Background material is
available at https://www.fda.gov/
AdvisoryCommittees/Calendar/
default.htm. Scroll down to the
appropriate advisory committee meeting
link.
Procedure: Interested persons may
present data, information, or views,
orally or in writing, on issues pending
before the committee. Written
submissions may be made to the contact
person on or before July 22, 2013. Oral
presentations from the public will be
scheduled between approximately 1
p.m. to 2 p.m. Those individuals
interested in making formal oral
presentations should notify the contact
person and submit a brief statement of
the general nature of the evidence or
arguments they wish to present, the
names and addresses of proposed
participants, and an indication of the
approximate time requested to make
their presentation on or before July 12,
2013. Time allotted for each
presentation may be limited. If the
number of registrants requesting to
PO 00000
Frm 00045
Fmt 4703
Sfmt 4703
36787
speak is greater than can be reasonably
accommodated during the scheduled
open public hearing session, FDA may
conduct a lottery to determine the
speakers for the scheduled open public
hearing session. The contact person will
notify interested persons regarding their
request to speak by July 15, 2013.
Persons attending FDA’s advisory
committee meetings are advised that the
Agency is not responsible for providing
access to electrical outlets.
FDA welcomes the attendance of the
public at its advisory committee
meetings and will make every effort to
accommodate persons with physical
disabilities or special needs. If you
require special accommodations due to
a disability, please contact Kristina
Toliver at least 7 days in advance of the
meeting.
FDA is committed to the orderly
conduct of its advisory committee
meetings. Please visit our Web site at
https://www.fda.gov/
AdvisoryCommittees/
AboutAdvisoryCommittees/
ucm111462.htm for procedures on
public conduct during advisory
committee meetings.
Notice of this meeting is given under
the Federal Advisory Committee Act (5
U.S.C. app. 2).
Dated: June 14, 2013.
Jill Hartzler Warner,
Acting Associate Commissioner for Special
Medical Programs.
[FR Doc. 2013–14632 Filed 6–18–13; 8:45 am]
BILLING CODE 4160–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA–2013–N–0001]
Rechanneling the Current Cardiac Risk
Paradigm: Arrhythmia Risk
Assessment During Drug Development
Without the Thorough QT Study;
Public Workshop
AGENCY:
Food and Drug Administration,
HHS.
ACTION:
Notice of public workshop.
SUMMARY: The Food and Drug
Administration (FDA), the Cardiac
Safety Research Consortium, and the
International Life Sciences Institute’s
Health and Environmental Sciences
Institute (HESI) will cosponsor a public
workshop entitled ‘‘Rechanneling the
Current Cardiac Risk Paradigm:
Arrhythmia Risk Assessment During
Drug Development Without the
Thorough QT Study.’’ The workshop
will introduce for discussion a new
E:\FR\FM\19JNN1.SGM
19JNN1
Agencies
[Federal Register Volume 78, Number 118 (Wednesday, June 19, 2013)]
[Notices]
[Pages 36786-36787]
From the Federal Register Online via the Government Printing Office [www.gpo.gov]
[FR Doc No: 2013-14579]
-----------------------------------------------------------------------
DEPARTMENT OF HEALTH AND HUMAN SERVICES
Food and Drug Administration
[Docket No. FDA-2013-N-0012]
Linking Marketplace Heparin Product Attributes and Manufacturing
Processes to Bioactivity and Immunogenicity
AGENCY: Food and Drug Administration, HHS.
ACTION: Notice.
-----------------------------------------------------------------------
SUMMARY: The Food and Drug Administration (FDA) is announcing the
availability of grant funds for the support of a sole source award to
the University of North Carolina. The goal of the award is to identify
what component(s) of the complex heparin mixtures have the propensity
to cause heparin induced thrombocytopenia (HIT) to improve the safety
of heparin drug products. The FDA seeks to identify the components of
the heparin mixture that are associated with HIT so that actions may be
taken to reduce these events and improve patient outcomes with this
widely used drug.
DATES: Important dates are as follows:
1. The application due date is July 15, 2013.
2. The anticipated start date is August, 2013.
3. The opening date is the date this announcement is published in
the Federal Register.
4. The expiration date is July 16, 2013.
ADDRESSES: Submit the paper application to: Gladys Melendez at the Food
and Drug Administration, Grants Management (HFA-500), 5630 Fishers
Lane, Rockville, MD 20857. For more information, see section III of the
SUPPLEMENTARY INFORMATION section of this notice.
FOR FURTHER INFORMATION CONTACT: David Keire, Center for Drug
Evaluation and Research, Food and Drug Administration, 1114 Market St.,
rm. 1002, St Louis, MO, 63130, 314-539-3850; or Gladys Melendez, Office
of Acquisition Support and Grant Services, Food and Drug
Administration, 5630 Fishers Lane, Rockville, MD 20857, 301-827-7175,
email: Gladys.bohler@fda.hhs.gov.
For more information on this funding opportunity announcement (FOA)
and to obtain detailed requirements, please contact Gladys.bohler@fda.hhs.gov.
SUPPLEMENTARY INFORMATION:
I. Funding Opportunity Description
Request for Application: FDA RFA-13-007
[Catalog of Federal Domestic Assistance: 93.103]
A. Background
The goal of this Research Project is to identify which components
of heparin drug mixtures have the propensity to cause heparin induced
thrombocytopenia (HIT) in order to improve the safety profile of this
widely used anticoagulant. Heparin is a heterogeneous mixture of
polysaccharides of varying length, sulfation pattern, acylation and
conformation that has been in clinical use since the 1930s. HIT is a
drug-dependent immune disorder caused by antibodies to complexes formed
between platelet factor 4 (PF4) and heparin which can occur in patients
who undergo major trauma (e.g. broken bones and cardiovascular surgery)
and receive heparin. The condition leads to formation of abnormal blood
clots and concomitant complications associated with clots. PF4-heparin
antibodies are observed in all patients with HIT. In addition, low
molecular weight heparins or the synthetic pentasaccharide
(fondaparinux) have also been shown to cause HIT antibody formation
although these smaller chain length heparins are much less likely to
lead to clinical HIT symptoms.
The major limitation in the available reagents for studies aimed at
identifying the components of heparin that lead to the pathogenesis of
HIT is the lack of pure component heparin standards. Therefore, this
collaboration brings together the following capabilities and
laboratories: (1) Synthesis of heparin chains of the same length,
sulfation pattern and conformation (Dr. Liu at the University of North
Carolina and Dr. Linhardt at Rensselaer Polytechnical Institute), (2)
synthesis and physicochemical characterization of heparin and heparin-
PF4 complexes (Keire FDA/DPA St Louis) and (3) a HIT-immunogenicity
animal model (Dr. Arepally at Duke University). FDA believes that this
combination of skills and expertise has the potential to make pure
standards, fully characterize the standards, create and characterize
PF4-heparin standard aggregates and assess their propensity to elicit
an immune response in an animal model. This research is unique and not
otherwise available. The ability to make pure heparin standards in gram
quantities and fully characterize their properties is only available
from the Liu and Linhardt laboratories. Furthermore, Dr. Arepally's
mouse model of HIT immunogenicity is not available in any other
laboratory. When completed the study will identify heparin components
that enhance HIT propensity and which could potentially be minimized in
heparin manufacturing, leading to safer heparin drugs with better
patient outcomes.
B. Research Objectives
The research objective is to identify the components of the heparin
mixture that have the propensity to lead to HIT pathogenesis.
C. Eligibility Information
This is a sole source RFA because the investigators identified in
this document have unique skills and expertise necessary to perform the
proposed work.
II. Award Information/Funds Available
A. Award Amount
Only one award will be available to the University of North
Carolina in the amount of $250,000 (Total Cost) in the first year.
B. Length of Support
Depending on research progress and subject to the availability of
funds additional funds may be awarded under this grant for up to a five
year project period reflecting $250,000 Total Cost per year.
III. Paper Application, Registration, and Submission Information
To submit a paper application in response to this FOA, applicants
should first review the full announcement. Persons interested in
applying for a grant may obtain an application at https://grants.nih.gov/grants/forms.htm.
For all paper application submissions, the following steps are
required:
Step 1: Obtain a Dun and Bradstreet (DUNS) Number
Step 2: Register With Central Contractor Registration
[[Page 36787]]
Step 3: Register With Electronic Research Administration
(eRA) Commons
Steps 1 and 2, in detail, can be found at https://www07.grants.gov/applicants/organization_registration.jsp. Step 3, in detail, can be
found at https://commons.era.nih.gov/commons/registration/registrationInstructions.jsp. After you have followed these steps,
submit paper applications to: Gladys Melendez; Grants Management, Food
and Drug Administration, 5630 Fishers Lane, rm. 2032; HFA-500;
Rockville, MD 20857.
Dated: June 12, 2013.
Leslie Kux,
Assistant Commissioner for Policy.
[FR Doc. 2013-14579 Filed 6-18-13; 8:45 am]
BILLING CODE 4160-01-P