Benzocaine; Weight Control Drug Products for Over-the-Counter Human Use, 12916-12920 [2011-5145]
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Federal Register / Vol. 76, No. 46 / Wednesday, March 9, 2011 / Proposed Rules
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PART 274—FORMS PRESCRIBED
UNDER THE INVESTMENT COMPANY
ACT OF 1940
10. Form N–MFP (referenced in
§ 274.201) is amended by:
a. Revising Item 33;
b. Removing Item 34;
c. Revising Item 37.b;
d. Removing Item 37.c;
e. Removing Items 38.b and 38.c;
f. Removing Items 39.c and 39.d;
g. Redesignating Items 35 through 46
as Items 34 through 45; and
h. In redesignated Item 38, replacing
‘‘Items 37 and 38’’ with ‘‘Items 36 and
37’’.
The revisions read as follows:
Note: The text of Form N–MFP does not,
and this amendment will not, appear in the
Code of Federal Regulations.
Form N–MFP
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Item 33
Submit written or electronic
comments on the proposed rule by June
7, 2011. See section IX of this document
for information on the proposed
effective date of this proposed rule.
ADDRESSES: You may submit comments,
identified by Docket No. FDA–1981–N–
0012 (formerly Docket No. 1981N–0022
and RIN No. 0910–AF45 by any of the
following methods:
DATES:
Indicate whether the security is a First
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b. The period remaining until the
principal amount of the security may be
recovered through the Demand Feature.
Dated: March 3, 2011.
By the Commission.
Elizabeth M. Murphy,
Secretary.
Electronic Submissions
[FR Doc. 2011–5184 Filed 3–8–11; 8:45 am]
Submit electronic comments in the
following way:
• Federal eRulemaking Portal: https://
www.regulations.gov. Follow the
instructions for submitting comments.
BILLING CODE 8011–01–P
Written Submissions
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Food and Drug Administration
21 CFR Part 310
[Docket No. FDA–1981–N–0012] (Formerly
Docket No. 1981N–0022)
RIN 0910–AF45
Benzocaine; Weight Control Drug
Products for Over-the-Counter Human
Use
AGENCY:
Food and Drug Administration,
HHS.
ACTION:
Proposed rule.
The Food and Drug
Administration (FDA) is issuing a
proposed rule to reclassify benzocaine
from its previously proposed
monograph status (category I) for overthe-counter (OTC) weight control use to
nonmonograph status. Although, in the
Federal Register of February 26, 1982,
an advanced notice of proposed
rulemaking (ANPR) included the
recommendation of an Advisory Panel,
consisting of health care providers from
outside FDA, recommended that
benzocaine should be generally
recognized as safe and effective
(GRASE) for weight control, this
document includes our first evaluation
of benzocaine for this use. Based on our
evaluation of the available data and
information, we have tentatively
concluded that the data are not
sufficient to support the safety and
effectiveness of benzocaine for this use.
This proposed rule, if finalized, would
require an approved new drug
application (NDA) or abbreviated new
drug application (ANDA) for the
marketing of OTC weight control
products containing benzocaine.
SUMMARY:
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Submit written submissions in the
following ways:
• FAX: 301–827–6870.
• Mail/Hand delivery/Courier (for
paper, disk, or CD–ROM submissions):
Division of Dockets Management (HFA–
305), Food and Drug Administration,
5630 Fishers Lane, Rm. 1061, Rockville,
MD 20852.
Instructions: All submissions received
must include the Agency name and
Docket No. FDA–1981–N–0012
(formerly Docket No. 1981N–0022) and
RIN No. 0910–AF45 for this rulemaking.
All comments received may be posted
without change to https://
www.regulations.gov, including any
personal information provided.
Docket: For access to the docket to
read background documents or
comments received, go to https://
www.regulations.gov and insert the
docket number, found in brackets in the
heading of this document, into the
‘‘Search’’ box and follow the prompts
and/or go to the Division of Dockets
Management, 5630 Fishers Lane, Rm.
1061, Rockville, MD 20852.
FOR FURTHER INFORMATION CONTACT:
Michelle M. Jackson, Center for Drug
Evaluation and Research (HFD–560),
Food and Drug Administration, 10903
New Hampshire Ave., Bldg. 22, MS
5411, Silver Spring, MD 20993–0002,
301–796–2090.
SUPPLEMENTARY INFORMATION:
I. Purpose of This Document
In the Federal Register of February
26, 1982, we (FDA) published an ANPR
to establish a monograph for OTC
weight control drug products. The
ANPR included the recommendations of
an Advisory Review Panel on the OTC
Miscellaneous Internal Drug Products
(the Panel) that evaluated all OTC
weight control drug products on the
market at the time the OTC drug review
began in 1972. The Panel consisted of
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Federal Register / Vol. 76, No. 46 / Wednesday, March 9, 2011 / Proposed Rules
scientists and health care providers
from outside FDA. The Panel concluded
that ‘‘benzocaine is safe for oral use as
an OTC anorectic in a dose of 3 to 15
milligrams (mg) in gum, lozenges, or
candy’’ and that ‘‘benzocaine in the form
of gum, lozenges, or candy is an
effective OTC drug product for weight
control’’ (47 FR 8466 at 8474). The Panel
believed that benzocaine numbed the
oral cavity (including the taste buds),
thereby discouraging food consumption
and decreasing caloric intake.
We reviewed the information and data
available to the Panel as well as
information and data that has been
developed since the Panel met to help
us determine whether benzocaine is
GRASE when used in OTC weight
control drug products. Under the
Federal Food, Drug, and Cosmetic Act
(the FD&C Act), all ‘‘new drugs’’ are
required to obtain approval under
section 505 of the FD&C Act (21 U.S.C.
355) prior to marketing. Most drugs are
‘‘new drugs’’ under the FD&C Act;
however, a drug is excluded from being
a ‘‘new drug’’ (and therefore is not
required to obtain approval under
section 505) if it is ‘‘generally
recognized, among experts qualified by
scientific training and experience to
evaluate the safety and effectiveness of
drugs, as safe and effective for use under
the conditions prescribed,
recommended, or suggested in the
labeling thereof.’’ (21 U.S.C. 321(p)(1)).1
As explained in this document, we
tentatively conclude that the existing
evidence is inadequate to establish that
OTC weight control drug products
containing benzocaine are GRASE.
Accordingly, we are proposing to
classify benzocaine as nonmonograph
(i.e., not GRASE) for use in OTC weight
control drug products. If this proposed
rule becomes a final rule, OTC weight
control drug products containing
benzocaine will require an approved
NDA or ANDA. Studies that may help
demonstrate the safety and effectiveness
of weight loss drug products are
described in an FDA guidance entitled
‘‘Developing Products for Weight
Management’’ (Ref. 1).
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II. Rulemakings and Petitions for OTC
Weight Control Drug Products
The Panel responsible for evaluating
OTC weight control drug products
recommended that benzocainecontaining drug products be deemed
GRASE for use in OTC weight control
drug products. The Panel’s
1 Consistent with the principles explained
previously, the OTC drug review regulations in 21
CFR 330.10 specify the considerations and evidence
required to establish both safety and effectiveness.
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recommendations were published in the
Federal Register as an ANPR for OTC
weight control products in 1982 (47 FR
8466).
Following publication of the 1982
ANPR, Thompson Medical Co., a
manufacturer of OTC weight control
drug products, submitted two citizen
petitions, one in 1990 and another in
1992, to support the effectiveness of
benzocaine for use as an appetite
suppressant (Refs. 2 and 3). The 1990
petition (Ref. 2) included a clinical
study by Collipp (Refs. 4 and 5) and a
summary of a clinical study by Piscano
and Lichter (Ref. 6) as data supporting
the effectiveness of benzocaine as an
appetite suppressant. We responded to
the manufacturer’s 1990 petition (Ref. 7)
reviewing the data submitted in the
petition and explaining our finding that
the data did not provide substantial
evidence from adequate and wellcontrolled studies to support the
effectiveness of benzocaine for weight
control use.
The 1992 petition (Ref. 3) was
submitted in response to our 1991 letter.
The petition provided two unpublished
statistical reevaluations of the Collipp
study, arguing that this data supported
finding benzocaine GRASE for use in
OTC weight control drug products. We
responded to the petition in 1993 (Ref.
8), stating that the reevaluations of the
Collipp study did not substantiate the
claim of effectiveness of benzocaine for
use in weight control. The two
reanalyses of the Collipp data include:
(1) An analysis of covariance excluding
subjects that failed to meet either the
age or the degree of overweight
inclusion criteria, and (2) a hierarchical
regression model to determine the effect
of benzocaine after attempting to control
for any familial effects. Neither of these
analyses adequately addressed the three
main problems that were listed in the
1991 response: (1) Possible breaking of
the blind; (2) imbalance in the sample
for important variables (age by family
status); and (3) lack of randomization
within families, affecting the
independence of observations. These
problems potentially biased the data
affecting the interpretability of the study
results.
Subsequent to our letter, we received
draft protocols for effectiveness studies
(Ref. 9) from the same manufacturer,
which were intended to generate
support for a GRASE finding. We sent
recommendations on the draft protocols
in 1992 (Ref. 10), but have not yet
received any study results.
III. Efficacy Evaluation
We are proposing that benzocaine be
classified as nonmonograph at any
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concentration for use in OTC weight
control drug products. This conclusion
is based in part on our review of the
effectiveness data that was submitted to
the Panel (Refs. 11 through 17) and
additional data submitted to us after
publication of the 1982 ANPR,
including the two petitions and draft
protocols described previously (Refs. 2,
3, and 9). In our responses to the
petitions, we explained in detail why
we did not find the available data
adequate to support a determination
that benzocaine is generally recognized
as effective (GRAE) for this use (Refs. 7,
8, and 10). In this document, we
summarize the available data and
limitations that prevent us from finding
benzocaine GRAE for use in OTC weight
control drug products. We have not
received any additional data from any
company or citizen since our 1992
response letter (Ref. 10) discussed
previously; and we are not aware of any
safety or effectiveness studies for
benzocaine in OTC weight control drug
products conducted since 1992.
In the following sections, we will first
describe the studies reviewed by the
Panel. After reviewing the data and
findings from these studies, we will
explain why the Agency has concluded
that these studies do not support a
finding that benzocaine is GRAE for use
in OTC weight control drug products.
A. Non-Clinical Studies
1. Review of Studies
In the ANPR, we reported that the
Panel considered a few nonclinical
studies (Refs. 11, 12, and 13) on
benzocaine for weight control. One of
the factors involved in overeating and
resulting obesity is the need to satisfy
the sense of taste. Horowitze (Ref. 11)
and Rosner (Ref. 12) showed that there
appears to be a decreased ability to
detect degrees of sweetness by taste
perception after chewing gum
containing benzocaine. Coons (Ref. 13)
demonstrated the effects of a local
anesthetic on hunger reduction in rats.
The Panel considered this study to be an
objective demonstration of the
effectiveness of a local anesthetic on
hunger reduction.
2. Analysis of Studies
We do not believe these studies
support a GRAE determination because
they do not demonstrate that decreased
taste perception or decreased hunger
results in weight loss. To find
benzocaine GRAE based in part on these
types of studies, we would also need
data demonstrating what level of
decrease in taste perception or hunger
actually resulted in a ‘‘clinically
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significant benefit of the type claimed’’
(i.e., weight loss) as required under
§ 330.10(a)(4)(ii) (21 CFR
330.10(a)(4)(ii)).
B. Clinical Studies
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1. Review of Studies
The Panel also considered clinical
studies that included weight loss as an
endpoint. Gould (Refs. 14 and 15)
assessed various case reports citing 1.5
to 2.0 pounds (lbs) per week weight loss
using lozenges containing benzocaine
and essential oils in conjunction with
dietary restrictions. Plotz (Ref. 16)
conducted an uncontrolled, nonrandomized 10-week study of 50
overweight adults (12 to 102 lbs
overweight). The subjects were
instructed to chew one or two pieces of
gum for 5 or 10 minutes followed by a
glass of water, just before meals. If
subjects became hungry between meals,
they could chew gum every few hours.
The study results showed weight loss
(2 pounds per week) in 45 of 50 patients
using the benzocaine gum in
conjunction with dietary restrictions.
McClure and Brush (Ref. 17)
conducted a placebo-controlled,
randomized, double-blinded 21-week
study of 308 overweight adults (255
females and 53 males). The subjects
were divided into five paired treatment
groups:
• Group 1: Dextroamphetamine
sulfate (10 mg, daily)
• Group 2: OTC proprietary appetite
suppressant (AYDS)
• Group 3: Dietary restriction (800 to
1,200 calories daily)
• Group 4: Glucose hard candy
containing benzocaine, caffeine, and
vitamins (benzocaine group)
• Group 5: Glucose candy only
(control group)
Over the course of 4 weeks, 170
participants dropped out of the study
(37 participants from the
dextroamphetamine group, 43
participants from the AYDS group, 51
participants from the dietary restriction
group, 9 participants from the
benzocaine group, and 30 participants
from the control group). The
investigators reported an average weight
loss during the first 4 weeks of 4.6 lbs
for the glucose (control) group and 12.1
lbs for the benzocaine group. After 21
weeks, the control group lost a weekly
average of 0.60 lbs as compared to 2.20
lbs for the benzocaine group.
In addition to these studies reviewed
by the Panel, as described previously,
we also reviewed clinical studies
submitted by a manufacturer of OTC
weight control drug products in two
petitions. The studies provided in the
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petitions included weight loss as an
endpoint. Reports purporting to be two
studies by Collipp (one published and
one unpublished) were submitted.
These reports appear to be the same
study (Refs. 4 and 5). The Collipp study
was designed to be a 6-week, doubleblind, placebo-controlled, randomized
trial comparing benzocaine (5 mg)
lozenges with placebo lozenges that
were identical in appearance (Ref. 4).
Male or female subjects who weighed 15
to 30 percent more than the ideal weight
for their body frame as determined from
Metropolitan Life Insurance Co. weight
tables and were between 14 and 55
years of age were eligible for enrollment.
Subjects were recruited from the same
families. Subjects were instructed to
follow a 1,250 calorie diet and to take
1 to 2 lozenges 10 minutes before meals,
1 lozenge instead of dessert, and 1 or 2
lozenges between meals. Subjects were
also instructed to drink a glass of water,
tea, coffee, or other non-caloric beverage
with each lozenge ingestion. Body
weight was measured at week 0 and
biweekly for the next 6 weeks. Subjects
were also asked to rate the average
quality of between-meal appetite
suppression as mild, moderate, or
complete.
The study results showed that the
mean body weight decreased from week
0 in both the active treatment and
placebo groups. Subjects treated with
benzocaine had a mean weight loss that
was statistically significant (p ≤: 0.001)
at all time points. The mean weight loss
during the study was approximately
twice as great for subjects treated with
benzocaine (¥3.5, ¥4.9, and ¥6.0 at 2,
4, and 6 weeks, respectively) compared
to placebo (¥2.1, ¥2.9, and ¥2.7 at 2,
4, and 6 weeks, respectively). The
manufacturer also submitted a study by
Piscano and Lichter (Ref. 6) which
consisted of a 1-page summary
describing an 8-week uncontrolled trial
involving 26 children. The summary
listed the baseline weight, final weight,
and weight loss of each subject. The
summary results showed that the
subjects lost approximately 0.5 lbs/
week. There was no protocol
description and no statistical analysis.
among other limitations, the Gould
studies (Refs. 14 and 15) were not wellcontrolled, as these studies consisted of
case reports. Similarly, the Plotz study
(Ref. 16) was not well controlled, being
both uncontrolled and non-randomized.
Finally, as detailed in our 1993 response
(Ref. 8), the McClure and Brusch study
(Ref. 17) had significant methodological
flaws including potential issues with
subject recruitment, inconsistent follow
up of subjects and inadequate
assessment of baseline characteristics.
The materials submitted in the
petition were also insufficient to
establish the effectiveness of benzocaine
in OTC weight control products. For
example, the Pisano and Lichter (Ref. 6)
study was not adequate and wellcontrolled as it consisted of case reports,
did not include a protocol description
and did not provide a statistical
analysis. Similarly, the Collipp study
and the reevaluations of the study
submitted in the petitions do not
provide detail regarding study design
and outcomes sufficient to show
benzocaine is GRASE for use in weight
control. Specifically, the Collipp study
had a significant number of limitations
that prevent us from concluding that
benzocaine is GRAE for weight control:
• Non-random selection of subjects
• Possible breaking of blinding
• Analysis did not account for a lack
of independence among subjects within
the same family, potentially affecting
the study’s findings
It is important to note that after
providing the petitioning manufacturer
with a response describing these
limitations, we received a protocol for a
further study from the manufacturer
(Ref. 9). We provided feedback on the
protocol in 1992 (Ref. 10), but we have
not yet received the study results from
the manufacturer. In order to establish
effectiveness, additional data are still
needed to show that benzocaine causes
a clinically and statistically significant
weight loss when compared with
placebo. The industry is advised to
consult a recently published FDA
guidance on the development of
products for weight management about
the requirement of clinical data (Ref. 1).
2. Analysis of Studies
We found a lack of substantial
evidence consisting of adequate and
well-controlled studies, as required in
§ 330.10(a)(4)(ii), on which to base a
determination of the effectiveness of
benzocaine in OTC weight control drug
products. In general, the clinical studies
reviewed by the Panel (Refs. 14 through
17) are inadequately controlled, and
study results were not clinically and
statistically significant. For example,
IV. Safety Evaluation
We are not aware of adequate data to
demonstrate that OTC weight control
drug products containing benzocaine
are generally recognized as safe (GRAS)
as defined under § 330.10(a)(4)(ii).
Under this regulatory provision, support
for a GRAS showing ‘‘shall consist of
adequate tests by methods reasonably
applicable to show the drug is safe
under the prescribed, recommended, or
suggested conditions of use.’’ We believe
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that the safety of the Panel’s proposed
benzocaine dosing for OTC weight
control use (multiple 3 to 15 mg doses
for up to 3 months) has not been
adequately established. Additional
safety data is needed to establish dosage
limitations or other aspects of the
labeling. Our current recommendation
as to what would constitute adequate
testing for a weight control drug product
is described in our guidance on weight
control drug products (Ref. 1).
V. Analysis of Impacts
We have examined the impacts of this
proposed rule under Executive Order
12866 and the Regulatory Flexibility Act
(5 U.S.C. 601–612), and the Unfunded
Mandates Reform Act of 1995 (Public
Law 104–4). Executive Order 12866
directs agencies to assess all costs and
benefits of available regulatory
alternatives and, when regulation is
necessary, to select regulatory
approaches that maximize net benefits
(including potential economic,
environmental, public health and safety,
and other advantages; distributive
impacts; and equity). We believe that
this proposed rule is not a significant
regulatory action as defined by the
Executive order.
The Regulatory Flexibility Act
requires agencies to analyze regulatory
options that would minimize any
significant impact of a rule on small
entities. Because few products will
likely be affected and those effects
would probably be small, we do not
believe that this proposed rule would
have a significant economic impact on
a substantial number of small entities.
Section 202(a) of the Unfunded
Mandates Reform Act of 1995 requires
that agencies prepare a written
statement, which includes an
assessment of anticipated costs and
benefits, before proposing ‘‘any rule that
includes any Federal mandate that may
result in the expenditure by State, local,
and tribal governments, in the aggregate,
or by the private sector, of $100,000,000
or more (adjusted annually for inflation)
in any one year.’’ The current threshold
after adjustment for inflation is $135
million, using the most current (2009)
Implicit Price Deflator for the Gross
Domestic Product. We do not expect
this proposed rule to result in any
1-year expenditure that would meet or
exceed this amount.
If this proposed rule is finalized, OTC
marketing of weight control drug
products containing benzocaine for this
use will cease, unless a product is
approved under an NDA or ANDA. In
this proposed rule, we tentatively
conclude that OTC weight control drug
products containing benzocaine lack
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sufficient evidence to support a finding
that such products are GRASE, and that
finalization of the regulatory status of
this ingredient will benefit consumers
by removing from the marketplace
products that have not been shown to be
safe and effective. We do not expect this
rule to have a significant effect on
industry as a whole, as we have only
been able to identify one company that
manufactures a benzocaine-containing
OTC weight control drug product.
We have few alternatives available to
us when we determine there are no data
available to demonstrate that an active
ingredient is GRASE. Even without
evidence of harm caused by the use of
these products, they cannot remain on
the market because there is no evidence
that they are safe and effective.
Accordingly, we have proposed a
30-day period within which companies
may remove benzocaine-containing
weight control drug products from the
market. We believe the only alternative
to this approach is a longer
implementation period.2 We could
allow a longer implementation period so
manufacturers would have time to
submit additional effectiveness and
safety data, but if we took this approach,
consumers would be unnecessarily
exposed to products that have not been
shown to be effective or safe.
VI. Paperwork Reduction Act of 1995
This proposed rule contains no
collections of information. Therefore,
clearance by the Office of Management
and Budget under the Paperwork
Reduction Act of 1995 is not required.
VII. Environmental Impact
We have determined under 21 CFR
25.31(a) that this action is of a type that
does not individually or cumulatively
have a significant effect on the human
environment. Therefore, neither an
environmental assessment nor an
environmental impact statement is
required.
VIII. Federalism
We have analyzed this proposed rule
in accordance with the principles set
forth in Executive Order 13132. Section
4(a) of the Executive order requires
agencies to ‘‘construe * * * a Federal
statute to preempt State law only where
the statute contains an express
preemption provision or there is some
other clear evidence that the Congress
intended preemption of State law, or
where the exercise of State authority
conflicts with the exercise of Federal
authority under the Federal statute.’’
The sole statutory provision giving
2 See
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12919
preemptive effect to the proposed rule is
section 751 of the act (21 U.S.C. 379r).
We believe that the preemptive effect
of this proposed rule, if finalized, would
be consistent with Executive Order
13132. Through the publication of this
proposed rule, we are providing notice
and an opportunity for State and local
officials to comment on this rulemaking.
IX. Proposed Effective Date
Due to effectiveness concerns
discussed in this document, any final
rule based on this proposal would
become effective 30 days after the date
of its publication. Manufacturers are
urged to comply voluntarily with this
proposed rule and to cease OTC
marketing at the earliest possible date.
X. References
The following references have been
placed on display in the Division of
Dockets Management (see ADDRESSES)
under Docket No. FDA–1981–N–0012
(formerly 1981N–0022) and may be seen
by interested persons between 9 a.m.
and 4 p.m., Monday through Friday.
(FDA has verified the Web site address,
but we are not responsible for any
subsequent changes to the Web site after
this document publishes in the Federal
Register.)
1. FDA, ‘‘Draft Guidance for Industry—
Developing Products for Weight
Management,’’ February 2007, https://
www.fda.gov/downloads/Drugs/
GuidanceComplianceRegulatory
Information/Guidances/ucm071612.pdf,
accessed on August 27, 2010.
2. Comment No. CP12, Docket No. FDA–
1981–N–0012 (formerly 1981N–0022),
Division of Dockets Management System.
3. Comment No. CP15, Docket No. FDA–
1981–N–0012 (formerly 1981N–0022),
Division of Dockets Management System.
4. Collipp, P. J., ‘‘The Treatment of Exogenous
Obesity by Medicated Benzocaine
Candy: A Double-Blind PlaceboControlled Study,’’ in OTC Vol. 170010,
Docket No. FDA–1981–N–0012 (formerly
1981N–0022), Division of Dockets
Management.
5. Collipp, P. J., ‘‘The Treatment of Exogenous
Obesity by Medicated Benzocaine
Candy: A Double Blind Placebo Study,’’
Obesity/Bariatric Medicine, 10:123–125,
1981.
6. Piscano, J. and H. Lichter, ‘‘A Matter of
Taste,’’ Fredrick Fell Publishers, Inc.,
New York, New York, pp. 42–64, 1979.
7. Comment No. LET82, Docket No. FDA–
1981–N–0012 (formerly 1981N–0022),
Division of Dockets Management System.
8. Comment No. LET87, Docket No. FDA–
1981–N–0012 (formerly 1981N–0022),
Division of Dockets Management System.
9. Comment No. PR9, Docket No. FDA–1981–
N–0012 (formerly 1981N–0022), Division
of Dockets Management System.
10. Comment No. LET84, Docket No. FDA–
1981–N–0012 (formerly 1981N–0022),
Division of Dockets Management System.
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Federal Register / Vol. 76, No. 46 / Wednesday, March 9, 2011 / Proposed Rules
11. Horowitz, S. and R. P. Scalici, ‘‘Results of
Sensory Panel Tests on Slim-Mint
Chewing Gum,’’ in OTC Vol. 170010,
Docket No. FDA–1981–N–0012 (formerly
1981N–0022), Division of Dockets
Management.
12. Rosner, L., ‘‘To Determine the Effect of
Chewing Slim-Mint Gum Upon Taste
Perception, Particularly Toward
Sweetness,’’ in OTC Vol. 170010, Docket
No. FDA–1981–N–0012 (formerly
1981N–0022), Division of Dockets
Management.
13. Summary Minutes of the 11th meeting of
the Advisory Review Panel on OTC
Miscellaneous Internal Drug Products
held on May 9–10, 1976 in OTC Vol.
170010, Docket No. FDA–1981–N–0012
(formerly 1981N–0022), Division of
Dockets Management.
14. Gould, W. L., ‘‘On the Use of a
Medicament to Reduce the Appetite in
the Treatment of Obesity and Other
Conditions,’’ New York State Journal of
Medicine, 47:981–983, 1947.
15. Gould, W. L., ‘‘Obesity and Hypertension:
The Importance of a Safe Compound to
Control Appetite,’’ North Carolina
Medical Journal, 11:327–334, 1950.
16. Plotz, M., ‘‘Obesity,’’ Medical Times,
86:860–863, 1958.
17. McClure, C. W. and C. A. Brusch,
‘‘Treatment of Oral Syndrome Obesity
with Non traditional Appetite Control
Plan,’’ Journal of the American Women’s
Medical Association, 28:239–248, 1973.
List of Subjects in 21 CFR Part 310
PART 310—NEW DRUGS
1. The authority citation for 21 CFR
part 310 continues to read as follows:
Authority: 21 U.S.C. 321, 331, 351, 352,
353, 355, 360b–360f, 360j, 361(a), 371, 374,
375, 379e; 42 U.S.C. 216, 241, 242(a), 262,
263b–263n.
erowe on DSK5CLS3C1PROD with PROPOSALS-1
2. Section 310.545 is amended by
adding paragraphs (a)(20)(i), (a)(20)(ii),
and (a)(20)(iii); by revising paragraph (d)
introductory text; and by adding
paragraph (d)(40) to read as follows:
§ 310.545 Drug products containing
certain active ingredients offered over-thecounter (OTC) for certain uses.
(a) * * *
(20) * * *
(i) [Reserved]
(ii) [Reserved]
(iii) Approved as of [DATE 30 DAYS
AFTER DATE OF PUBLICATION OF
THE FINAL RULE IN THE FEDERAL
REGISTER].
15:03 Mar 08, 2011
Jkt 223001
Dated: March 2, 2011.
Leslie Kux,
Acting Assistant Commissioner for Policy.
[FR Doc. 2011–5145 Filed 3–8–11; 8:45 am]
BILLING CODE 4160–01–P
DEPARTMENT OF THE INTERIOR
Office of Surface Mining Reclamation
and Enforcement
30 CFR Part 938
[PA–157–FOR; OSM 2010–0011]
Pennsylvania Regulatory Program
Office of Surface Mining
Reclamation and Enforcement (OSM),
Interior.
ACTION: Proposed rule; public comment
period and opportunity for public
hearing on removal of required
amendment.
AGENCY:
Administrative practice and
procedure, Drugs, Labeling, Medical
devices, Reporting and recordkeeping
requirements.
Therefore, under the Federal Food,
Drug, and Cosmetic Act and under
authority delegated to the Commissioner
of Food and Drugs, it is proposed that
21 CFR part 310 be amended as follows:
VerDate Mar<15>2010
Benzocaine
*
*
*
*
(d) Any OTC drug product that is not
in compliance with this section is
subject to regulatory action if initially
introduced or initially delivered for
introduction into interstate commerce
after the dates specified in paragraphs
(d)(1) through (d)(40) of this section.
*
*
*
*
*
(40) [DATE 30 DAYS AFTER DATE
OF PUBLICATION OF THE FINAL
RULE IN THE FEDERAL REGISTER],
for products subject to paragraph
(a)(20)(iii) of this section.
*
We are announcing receipt of
a request to remove a required
amendment to the Pennsylvania
regulatory program (the ‘‘Pennsylvania
program’’) under the Surface Mining
Control and Reclamation Act of 1977
(SMCRA or the Act). In response to a
required program amendment codified
in the Federal regulations, Pennsylvania
has submitted rationale that it believes
supports its position that current
program provisions are sufficient to
render its program no less effective than
the Federal requirements and, therefore,
no amendment is necessary. The
required amendment pertains to
regulatory exemptions for coal
extraction incidental to the extraction of
other minerals.
This document gives the times and
locations that the Pennsylvania program
and this submittal are available for your
inspection, the comment period during
which you may submit written
comments, and the procedures that we
will follow for the public hearing, if one
is requested.
SUMMARY:
PO 00000
Frm 00034
Fmt 4702
Sfmt 4702
We will accept written
comments until 4 p.m., local time April
8, 2011. If requested, we will hold a
public hearing on April 4, 2011. We will
accept requests to speak until 4 p.m.,
local time on March 24, 2011.
ADDRESSES: You may submit comments,
identified by ‘‘PA–157–FOR; Docket ID:
OSM–2010–0011’’ by either of the
following two methods:
Federal eRulemaking Portal: https://
www.regulations.gov. The proposed rule
has been assigned Docket ID: OSM–
2010–0011. If you would like to submit
comments through the Federal
eRulemaking Portal, go to https://
www.regulations.gov and follow the
instructions.
Mail/Hand Delivery/Courier: Mr.
George Rieger, Chief, Pittsburgh Field
Division, Office of Surface Mining
Reclamation and Enforcement,
Harrisburg Transportation Center, 415
Market St., Suite 304, Harrisburg, PA
17101.
Instructions: For detailed instructions
on submitting comments and additional
information on the rulemaking process,
see the ‘‘Public Comment Procedures’’
heading of the SUPPLEMENTARY
INFORMATION section of this document.
Docket: In addition to obtaining
copies of documents at https://
www.regulations.gov, information may
also be obtained at the addresses listed
below during normal business hours,
Monday through Friday, excluding
holidays. You may receive one free copy
of the amendment by contacting OSM’s
Pittsburgh Field Division Office.
George Rieger, Chief, Pittsburgh Field
Division, Office of Surface Mining
Reclamation and Enforcement,
Harrisburg Transportation Center, 415
Market St., Suite 304, Harrisburg,
Pennsylvania 17101, Telephone: (717)
782–4036, E-mail: grieger@osmre.gov.
Thomas Callaghan, P.G., Director,
Bureau of Mining and Reclamation,
Pennsylvania Department of
Environmental Protection, Rachel
Carson State Office Building, P.O. Box
8461, Harrisburg, Pennsylvania
17105–8461, Telephone: (717) 787–
5103, E-mail: tcallaghan@state.pa.us.
FOR FURTHER INFORMATION CONTACT:
George Rieger, Telephone: (717) 782–
4036. E-mail: grieger@osmre.gov.
SUPPLEMENTARY INFORMATION:
DATES:
I. Background on the Pennsylvania Program
II. Description of the Request
III. Public Comment Procedures
IV. Procedural Determinations
I. Background on the Pennsylvania
Program
Section 503(a) of the Act permits a
State to assume primacy for the
E:\FR\FM\09MRP1.SGM
09MRP1
Agencies
[Federal Register Volume 76, Number 46 (Wednesday, March 9, 2011)]
[Proposed Rules]
[Pages 12916-12920]
From the Federal Register Online via the Government Printing Office [www.gpo.gov]
[FR Doc No: 2011-5145]
=======================================================================
-----------------------------------------------------------------------
DEPARTMENT OF HEALTH AND HUMAN SERVICES
Food and Drug Administration
21 CFR Part 310
[Docket No. FDA-1981-N-0012] (Formerly Docket No. 1981N-0022)
RIN 0910-AF45
Benzocaine; Weight Control Drug Products for Over-the-Counter
Human Use
AGENCY: Food and Drug Administration, HHS.
ACTION: Proposed rule.
-----------------------------------------------------------------------
SUMMARY: The Food and Drug Administration (FDA) is issuing a proposed
rule to reclassify benzocaine from its previously proposed monograph
status (category I) for over-the-counter (OTC) weight control use to
nonmonograph status. Although, in the Federal Register of February 26,
1982, an advanced notice of proposed rulemaking (ANPR) included the
recommendation of an Advisory Panel, consisting of health care
providers from outside FDA, recommended that benzocaine should be
generally recognized as safe and effective (GRASE) for weight control,
this document includes our first evaluation of benzocaine for this use.
Based on our evaluation of the available data and information, we have
tentatively concluded that the data are not sufficient to support the
safety and effectiveness of benzocaine for this use. This proposed
rule, if finalized, would require an approved new drug application
(NDA) or abbreviated new drug application (ANDA) for the marketing of
OTC weight control products containing benzocaine.
DATES: Submit written or electronic comments on the proposed rule by
June 7, 2011. See section IX of this document for information on the
proposed effective date of this proposed rule.
ADDRESSES: You may submit comments, identified by Docket No. FDA-1981-
N-0012 (formerly Docket No. 1981N-0022 and RIN No. 0910-AF45 by any of
the following methods:
Electronic Submissions
Submit electronic comments in the following way:
Federal eRulemaking Portal: https://www.regulations.gov.
Follow the instructions for submitting comments.
Written Submissions
Submit written submissions in the following ways:
FAX: 301-827-6870.
Mail/Hand delivery/Courier (for paper, disk, or CD-ROM
submissions): Division of Dockets Management (HFA-305), Food and Drug
Administration, 5630 Fishers Lane, Rm. 1061, Rockville, MD 20852.
Instructions: All submissions received must include the Agency name
and Docket No. FDA-1981-N-0012 (formerly Docket No. 1981N-0022) and RIN
No. 0910-AF45 for this rulemaking. All comments received may be posted
without change to https://www.regulations.gov, including any personal
information provided.
Docket: For access to the docket to read background documents or
comments received, go to https://www.regulations.gov and insert the
docket number, found in brackets in the heading of this document, into
the ``Search'' box and follow the prompts and/or go to the Division of
Dockets Management, 5630 Fishers Lane, Rm. 1061, Rockville, MD 20852.
FOR FURTHER INFORMATION CONTACT: Michelle M. Jackson, Center for Drug
Evaluation and Research (HFD-560), Food and Drug Administration, 10903
New Hampshire Ave., Bldg. 22, MS 5411, Silver Spring, MD 20993-0002,
301-796-2090.
SUPPLEMENTARY INFORMATION:
I. Purpose of This Document
In the Federal Register of February 26, 1982, we (FDA) published an
ANPR to establish a monograph for OTC weight control drug products. The
ANPR included the recommendations of an Advisory Review Panel on the
OTC Miscellaneous Internal Drug Products (the Panel) that evaluated all
OTC weight control drug products on the market at the time the OTC drug
review began in 1972. The Panel consisted of
[[Page 12917]]
scientists and health care providers from outside FDA. The Panel
concluded that ``benzocaine is safe for oral use as an OTC anorectic in
a dose of 3 to 15 milligrams (mg) in gum, lozenges, or candy'' and that
``benzocaine in the form of gum, lozenges, or candy is an effective OTC
drug product for weight control'' (47 FR 8466 at 8474). The Panel
believed that benzocaine numbed the oral cavity (including the taste
buds), thereby discouraging food consumption and decreasing caloric
intake.
We reviewed the information and data available to the Panel as well
as information and data that has been developed since the Panel met to
help us determine whether benzocaine is GRASE when used in OTC weight
control drug products. Under the Federal Food, Drug, and Cosmetic Act
(the FD&C Act), all ``new drugs'' are required to obtain approval under
section 505 of the FD&C Act (21 U.S.C. 355) prior to marketing. Most
drugs are ``new drugs'' under the FD&C Act; however, a drug is excluded
from being a ``new drug'' (and therefore is not required to obtain
approval under section 505) if it is ``generally recognized, among
experts qualified by scientific training and experience to evaluate the
safety and effectiveness of drugs, as safe and effective for use under
the conditions prescribed, recommended, or suggested in the labeling
thereof.'' (21 U.S.C. 321(p)(1)).\1\
---------------------------------------------------------------------------
\1\ Consistent with the principles explained previously, the OTC
drug review regulations in 21 CFR 330.10 specify the considerations
and evidence required to establish both safety and effectiveness.
---------------------------------------------------------------------------
As explained in this document, we tentatively conclude that the
existing evidence is inadequate to establish that OTC weight control
drug products containing benzocaine are GRASE. Accordingly, we are
proposing to classify benzocaine as nonmonograph (i.e., not GRASE) for
use in OTC weight control drug products. If this proposed rule becomes
a final rule, OTC weight control drug products containing benzocaine
will require an approved NDA or ANDA. Studies that may help demonstrate
the safety and effectiveness of weight loss drug products are described
in an FDA guidance entitled ``Developing Products for Weight
Management'' (Ref. 1).
II. Rulemakings and Petitions for OTC Weight Control Drug Products
The Panel responsible for evaluating OTC weight control drug
products recommended that benzocaine-containing drug products be deemed
GRASE for use in OTC weight control drug products. The Panel's
recommendations were published in the Federal Register as an ANPR for
OTC weight control products in 1982 (47 FR 8466).
Following publication of the 1982 ANPR, Thompson Medical Co., a
manufacturer of OTC weight control drug products, submitted two citizen
petitions, one in 1990 and another in 1992, to support the
effectiveness of benzocaine for use as an appetite suppressant (Refs. 2
and 3). The 1990 petition (Ref. 2) included a clinical study by Collipp
(Refs. 4 and 5) and a summary of a clinical study by Piscano and
Lichter (Ref. 6) as data supporting the effectiveness of benzocaine as
an appetite suppressant. We responded to the manufacturer's 1990
petition (Ref. 7) reviewing the data submitted in the petition and
explaining our finding that the data did not provide substantial
evidence from adequate and well-controlled studies to support the
effectiveness of benzocaine for weight control use.
The 1992 petition (Ref. 3) was submitted in response to our 1991
letter. The petition provided two unpublished statistical reevaluations
of the Collipp study, arguing that this data supported finding
benzocaine GRASE for use in OTC weight control drug products. We
responded to the petition in 1993 (Ref. 8), stating that the
reevaluations of the Collipp study did not substantiate the claim of
effectiveness of benzocaine for use in weight control. The two
reanalyses of the Collipp data include: (1) An analysis of covariance
excluding subjects that failed to meet either the age or the degree of
overweight inclusion criteria, and (2) a hierarchical regression model
to determine the effect of benzocaine after attempting to control for
any familial effects. Neither of these analyses adequately addressed
the three main problems that were listed in the 1991 response: (1)
Possible breaking of the blind; (2) imbalance in the sample for
important variables (age by family status); and (3) lack of
randomization within families, affecting the independence of
observations. These problems potentially biased the data affecting the
interpretability of the study results.
Subsequent to our letter, we received draft protocols for
effectiveness studies (Ref. 9) from the same manufacturer, which were
intended to generate support for a GRASE finding. We sent
recommendations on the draft protocols in 1992 (Ref. 10), but have not
yet received any study results.
III. Efficacy Evaluation
We are proposing that benzocaine be classified as nonmonograph at
any concentration for use in OTC weight control drug products. This
conclusion is based in part on our review of the effectiveness data
that was submitted to the Panel (Refs. 11 through 17) and additional
data submitted to us after publication of the 1982 ANPR, including the
two petitions and draft protocols described previously (Refs. 2, 3, and
9). In our responses to the petitions, we explained in detail why we
did not find the available data adequate to support a determination
that benzocaine is generally recognized as effective (GRAE) for this
use (Refs. 7, 8, and 10). In this document, we summarize the available
data and limitations that prevent us from finding benzocaine GRAE for
use in OTC weight control drug products. We have not received any
additional data from any company or citizen since our 1992 response
letter (Ref. 10) discussed previously; and we are not aware of any
safety or effectiveness studies for benzocaine in OTC weight control
drug products conducted since 1992.
In the following sections, we will first describe the studies
reviewed by the Panel. After reviewing the data and findings from these
studies, we will explain why the Agency has concluded that these
studies do not support a finding that benzocaine is GRAE for use in OTC
weight control drug products.
A. Non-Clinical Studies
1. Review of Studies
In the ANPR, we reported that the Panel considered a few
nonclinical studies (Refs. 11, 12, and 13) on benzocaine for weight
control. One of the factors involved in overeating and resulting
obesity is the need to satisfy the sense of taste. Horowitze (Ref. 11)
and Rosner (Ref. 12) showed that there appears to be a decreased
ability to detect degrees of sweetness by taste perception after
chewing gum containing benzocaine. Coons (Ref. 13) demonstrated the
effects of a local anesthetic on hunger reduction in rats. The Panel
considered this study to be an objective demonstration of the
effectiveness of a local anesthetic on hunger reduction.
2. Analysis of Studies
We do not believe these studies support a GRAE determination
because they do not demonstrate that decreased taste perception or
decreased hunger results in weight loss. To find benzocaine GRAE based
in part on these types of studies, we would also need data
demonstrating what level of decrease in taste perception or hunger
actually resulted in a ``clinically
[[Page 12918]]
significant benefit of the type claimed'' (i.e., weight loss) as
required under Sec. 330.10(a)(4)(ii) (21 CFR 330.10(a)(4)(ii)).
B. Clinical Studies
1. Review of Studies
The Panel also considered clinical studies that included weight
loss as an endpoint. Gould (Refs. 14 and 15) assessed various case
reports citing 1.5 to 2.0 pounds (lbs) per week weight loss using
lozenges containing benzocaine and essential oils in conjunction with
dietary restrictions. Plotz (Ref. 16) conducted an uncontrolled, non-
randomized 10-week study of 50 overweight adults (12 to 102 lbs
overweight). The subjects were instructed to chew one or two pieces of
gum for 5 or 10 minutes followed by a glass of water, just before
meals. If subjects became hungry between meals, they could chew gum
every few hours. The study results showed weight loss (2 pounds per
week) in 45 of 50 patients using the benzocaine gum in conjunction with
dietary restrictions.
McClure and Brush (Ref. 17) conducted a placebo-controlled,
randomized, double-blinded 21-week study of 308 overweight adults (255
females and 53 males). The subjects were divided into five paired
treatment groups:
Group 1: Dextroamphetamine sulfate (10 mg, daily)
Group 2: OTC proprietary appetite suppressant (AYDS)
Group 3: Dietary restriction (800 to 1,200 calories daily)
Group 4: Glucose hard candy containing benzocaine,
caffeine, and vitamins (benzocaine group)
Group 5: Glucose candy only (control group)
Over the course of 4 weeks, 170 participants dropped out of the
study (37 participants from the dextroamphetamine group, 43
participants from the AYDS group, 51 participants from the dietary
restriction group, 9 participants from the benzocaine group, and 30
participants from the control group). The investigators reported an
average weight loss during the first 4 weeks of 4.6 lbs for the glucose
(control) group and 12.1 lbs for the benzocaine group. After 21 weeks,
the control group lost a weekly average of 0.60 lbs as compared to 2.20
lbs for the benzocaine group.
In addition to these studies reviewed by the Panel, as described
previously, we also reviewed clinical studies submitted by a
manufacturer of OTC weight control drug products in two petitions. The
studies provided in the petitions included weight loss as an endpoint.
Reports purporting to be two studies by Collipp (one published and one
unpublished) were submitted. These reports appear to be the same study
(Refs. 4 and 5). The Collipp study was designed to be a 6-week, double-
blind, placebo-controlled, randomized trial comparing benzocaine (5 mg)
lozenges with placebo lozenges that were identical in appearance (Ref.
4). Male or female subjects who weighed 15 to 30 percent more than the
ideal weight for their body frame as determined from Metropolitan Life
Insurance Co. weight tables and were between 14 and 55 years of age
were eligible for enrollment. Subjects were recruited from the same
families. Subjects were instructed to follow a 1,250 calorie diet and
to take 1 to 2 lozenges 10 minutes before meals, 1 lozenge instead of
dessert, and 1 or 2 lozenges between meals. Subjects were also
instructed to drink a glass of water, tea, coffee, or other non-caloric
beverage with each lozenge ingestion. Body weight was measured at week
0 and biweekly for the next 6 weeks. Subjects were also asked to rate
the average quality of between-meal appetite suppression as mild,
moderate, or complete.
The study results showed that the mean body weight decreased from
week 0 in both the active treatment and placebo groups. Subjects
treated with benzocaine had a mean weight loss that was statistically
significant (p <=: 0.001) at all time points. The mean weight loss
during the study was approximately twice as great for subjects treated
with benzocaine (-3.5, -4.9, and -6.0 at 2, 4, and 6 weeks,
respectively) compared to placebo (-2.1, -2.9, and -2.7 at 2, 4, and 6
weeks, respectively). The manufacturer also submitted a study by
Piscano and Lichter (Ref. 6) which consisted of a 1-page summary
describing an 8-week uncontrolled trial involving 26 children. The
summary listed the baseline weight, final weight, and weight loss of
each subject. The summary results showed that the subjects lost
approximately 0.5 lbs/week. There was no protocol description and no
statistical analysis.
2. Analysis of Studies
We found a lack of substantial evidence consisting of adequate and
well-controlled studies, as required in Sec. 330.10(a)(4)(ii), on
which to base a determination of the effectiveness of benzocaine in OTC
weight control drug products. In general, the clinical studies reviewed
by the Panel (Refs. 14 through 17) are inadequately controlled, and
study results were not clinically and statistically significant. For
example, among other limitations, the Gould studies (Refs. 14 and 15)
were not well-controlled, as these studies consisted of case reports.
Similarly, the Plotz study (Ref. 16) was not well controlled, being
both uncontrolled and non-randomized. Finally, as detailed in our 1993
response (Ref. 8), the McClure and Brusch study (Ref. 17) had
significant methodological flaws including potential issues with
subject recruitment, inconsistent follow up of subjects and inadequate
assessment of baseline characteristics.
The materials submitted in the petition were also insufficient to
establish the effectiveness of benzocaine in OTC weight control
products. For example, the Pisano and Lichter (Ref. 6) study was not
adequate and well-controlled as it consisted of case reports, did not
include a protocol description and did not provide a statistical
analysis. Similarly, the Collipp study and the reevaluations of the
study submitted in the petitions do not provide detail regarding study
design and outcomes sufficient to show benzocaine is GRASE for use in
weight control. Specifically, the Collipp study had a significant
number of limitations that prevent us from concluding that benzocaine
is GRAE for weight control:
Non-random selection of subjects
Possible breaking of blinding
Analysis did not account for a lack of independence among
subjects within the same family, potentially affecting the study's
findings
It is important to note that after providing the petitioning
manufacturer with a response describing these limitations, we received
a protocol for a further study from the manufacturer (Ref. 9). We
provided feedback on the protocol in 1992 (Ref. 10), but we have not
yet received the study results from the manufacturer. In order to
establish effectiveness, additional data are still needed to show that
benzocaine causes a clinically and statistically significant weight
loss when compared with placebo. The industry is advised to consult a
recently published FDA guidance on the development of products for
weight management about the requirement of clinical data (Ref. 1).
IV. Safety Evaluation
We are not aware of adequate data to demonstrate that OTC weight
control drug products containing benzocaine are generally recognized as
safe (GRAS) as defined under Sec. 330.10(a)(4)(ii). Under this
regulatory provision, support for a GRAS showing ``shall consist of
adequate tests by methods reasonably applicable to show the drug is
safe under the prescribed, recommended, or suggested conditions of
use.'' We believe
[[Page 12919]]
that the safety of the Panel's proposed benzocaine dosing for OTC
weight control use (multiple 3 to 15 mg doses for up to 3 months) has
not been adequately established. Additional safety data is needed to
establish dosage limitations or other aspects of the labeling. Our
current recommendation as to what would constitute adequate testing for
a weight control drug product is described in our guidance on weight
control drug products (Ref. 1).
V. Analysis of Impacts
We have examined the impacts of this proposed rule under Executive
Order 12866 and the Regulatory Flexibility Act (5 U.S.C. 601-612), and
the Unfunded Mandates Reform Act of 1995 (Public Law 104-4). Executive
Order 12866 directs agencies to assess all costs and benefits of
available regulatory alternatives and, when regulation is necessary, to
select regulatory approaches that maximize net benefits (including
potential economic, environmental, public health and safety, and other
advantages; distributive impacts; and equity). We believe that this
proposed rule is not a significant regulatory action as defined by the
Executive order.
The Regulatory Flexibility Act requires agencies to analyze
regulatory options that would minimize any significant impact of a rule
on small entities. Because few products will likely be affected and
those effects would probably be small, we do not believe that this
proposed rule would have a significant economic impact on a substantial
number of small entities.
Section 202(a) of the Unfunded Mandates Reform Act of 1995 requires
that agencies prepare a written statement, which includes an assessment
of anticipated costs and benefits, before proposing ``any rule that
includes any Federal mandate that may result in the expenditure by
State, local, and tribal governments, in the aggregate, or by the
private sector, of $100,000,000 or more (adjusted annually for
inflation) in any one year.'' The current threshold after adjustment
for inflation is $135 million, using the most current (2009) Implicit
Price Deflator for the Gross Domestic Product. We do not expect this
proposed rule to result in any 1-year expenditure that would meet or
exceed this amount.
If this proposed rule is finalized, OTC marketing of weight control
drug products containing benzocaine for this use will cease, unless a
product is approved under an NDA or ANDA. In this proposed rule, we
tentatively conclude that OTC weight control drug products containing
benzocaine lack sufficient evidence to support a finding that such
products are GRASE, and that finalization of the regulatory status of
this ingredient will benefit consumers by removing from the marketplace
products that have not been shown to be safe and effective. We do not
expect this rule to have a significant effect on industry as a whole,
as we have only been able to identify one company that manufactures a
benzocaine-containing OTC weight control drug product.
We have few alternatives available to us when we determine there
are no data available to demonstrate that an active ingredient is
GRASE. Even without evidence of harm caused by the use of these
products, they cannot remain on the market because there is no evidence
that they are safe and effective. Accordingly, we have proposed a 30-
day period within which companies may remove benzocaine-containing
weight control drug products from the market. We believe the only
alternative to this approach is a longer implementation period.\2\ We
could allow a longer implementation period so manufacturers would have
time to submit additional effectiveness and safety data, but if we took
this approach, consumers would be unnecessarily exposed to products
that have not been shown to be effective or safe.
---------------------------------------------------------------------------
\2\ See 5 U.S.C. 553(d).
---------------------------------------------------------------------------
VI. Paperwork Reduction Act of 1995
This proposed rule contains no collections of information.
Therefore, clearance by the Office of Management and Budget under the
Paperwork Reduction Act of 1995 is not required.
VII. Environmental Impact
We have determined under 21 CFR 25.31(a) that this action is of a
type that does not individually or cumulatively have a significant
effect on the human environment. Therefore, neither an environmental
assessment nor an environmental impact statement is required.
VIII. Federalism
We have analyzed this proposed rule in accordance with the
principles set forth in Executive Order 13132. Section 4(a) of the
Executive order requires agencies to ``construe * * * a Federal statute
to preempt State law only where the statute contains an express
preemption provision or there is some other clear evidence that the
Congress intended preemption of State law, or where the exercise of
State authority conflicts with the exercise of Federal authority under
the Federal statute.'' The sole statutory provision giving preemptive
effect to the proposed rule is section 751 of the act (21 U.S.C. 379r).
We believe that the preemptive effect of this proposed rule, if
finalized, would be consistent with Executive Order 13132. Through the
publication of this proposed rule, we are providing notice and an
opportunity for State and local officials to comment on this
rulemaking.
IX. Proposed Effective Date
Due to effectiveness concerns discussed in this document, any final
rule based on this proposal would become effective 30 days after the
date of its publication. Manufacturers are urged to comply voluntarily
with this proposed rule and to cease OTC marketing at the earliest
possible date.
X. References
The following references have been placed on display in the
Division of Dockets Management (see ADDRESSES) under Docket No. FDA-
1981-N-0012 (formerly 1981N-0022) and may be seen by interested persons
between 9 a.m. and 4 p.m., Monday through Friday. (FDA has verified the
Web site address, but we are not responsible for any subsequent changes
to the Web site after this document publishes in the Federal Register.)
1. FDA, ``Draft Guidance for Industry--Developing Products for
Weight Management,'' February 2007, https://www.fda.gov/downloads/Drugs/GuidanceComplianceRegulatoryInformation/Guidances/ucm071612.pdf, accessed on August 27, 2010.
2. Comment No. CP12, Docket No. FDA-1981-N-0012 (formerly 1981N-
0022), Division of Dockets Management System.
3. Comment No. CP15, Docket No. FDA-1981-N-0012 (formerly 1981N-
0022), Division of Dockets Management System.
4. Collipp, P. J., ``The Treatment of Exogenous Obesity by Medicated
Benzocaine Candy: A Double-Blind Placebo-Controlled Study,'' in OTC
Vol. 170010, Docket No. FDA-1981-N-0012 (formerly 1981N-0022),
Division of Dockets Management.
5. Collipp, P. J., ``The Treatment of Exogenous Obesity by Medicated
Benzocaine Candy: A Double Blind Placebo Study,'' Obesity/Bariatric
Medicine, 10:123-125, 1981.
6. Piscano, J. and H. Lichter, ``A Matter of Taste,'' Fredrick Fell
Publishers, Inc., New York, New York, pp. 42-64, 1979.
7. Comment No. LET82, Docket No. FDA-1981-N-0012 (formerly 1981N-
0022), Division of Dockets Management System.
8. Comment No. LET87, Docket No. FDA-1981-N-0012 (formerly 1981N-
0022), Division of Dockets Management System.
9. Comment No. PR9, Docket No. FDA-1981-N-0012 (formerly 1981N-
0022), Division of Dockets Management System.
10. Comment No. LET84, Docket No. FDA-1981-N-0012 (formerly 1981N-
0022), Division of Dockets Management System.
[[Page 12920]]
11. Horowitz, S. and R. P. Scalici, ``Results of Sensory Panel Tests
on Slim-Mint Chewing Gum,'' in OTC Vol. 170010, Docket No. FDA-1981-
N-0012 (formerly 1981N-0022), Division of Dockets Management.
12. Rosner, L., ``To Determine the Effect of Chewing Slim-Mint Gum
Upon Taste Perception, Particularly Toward Sweetness,'' in OTC Vol.
170010, Docket No. FDA-1981-N-0012 (formerly 1981N-0022), Division
of Dockets Management.
13. Summary Minutes of the 11th meeting of the Advisory Review Panel
on OTC Miscellaneous Internal Drug Products held on May 9-10, 1976
in OTC Vol. 170010, Docket No. FDA-1981-N-0012 (formerly 1981N-
0022), Division of Dockets Management.
14. Gould, W. L., ``On the Use of a Medicament to Reduce the
Appetite in the Treatment of Obesity and Other Conditions,'' New
York State Journal of Medicine, 47:981-983, 1947.
15. Gould, W. L., ``Obesity and Hypertension: The Importance of a
Safe Compound to Control Appetite,'' North Carolina Medical Journal,
11:327-334, 1950.
16. Plotz, M., ``Obesity,'' Medical Times, 86:860-863, 1958.
17. McClure, C. W. and C. A. Brusch, ``Treatment of Oral Syndrome
Obesity with Non traditional Appetite Control Plan,'' Journal of the
American Women's Medical Association, 28:239-248, 1973.
List of Subjects in 21 CFR Part 310
Administrative practice and procedure, Drugs, Labeling, Medical
devices, Reporting and recordkeeping requirements.
Therefore, under the Federal Food, Drug, and Cosmetic Act and under
authority delegated to the Commissioner of Food and Drugs, it is
proposed that 21 CFR part 310 be amended as follows:
PART 310--NEW DRUGS
1. The authority citation for 21 CFR part 310 continues to read as
follows:
Authority: 21 U.S.C. 321, 331, 351, 352, 353, 355, 360b-360f,
360j, 361(a), 371, 374, 375, 379e; 42 U.S.C. 216, 241, 242(a), 262,
263b-263n.
2. Section 310.545 is amended by adding paragraphs (a)(20)(i),
(a)(20)(ii), and (a)(20)(iii); by revising paragraph (d) introductory
text; and by adding paragraph (d)(40) to read as follows:
Sec. 310.545 Drug products containing certain active ingredients
offered over-the-counter (OTC) for certain uses.
(a) * * *
(20) * * *
(i) [Reserved]
(ii) [Reserved]
(iii) Approved as of [DATE 30 DAYS AFTER DATE OF PUBLICATION OF THE
FINAL RULE IN THE FEDERAL REGISTER].
Benzocaine
* * * * *
(d) Any OTC drug product that is not in compliance with this
section is subject to regulatory action if initially introduced or
initially delivered for introduction into interstate commerce after the
dates specified in paragraphs (d)(1) through (d)(40) of this section.
* * * * *
(40) [DATE 30 DAYS AFTER DATE OF PUBLICATION OF THE FINAL RULE IN
THE FEDERAL REGISTER], for products subject to paragraph (a)(20)(iii)
of this section.
Dated: March 2, 2011.
Leslie Kux,
Acting Assistant Commissioner for Policy.
[FR Doc. 2011-5145 Filed 3-8-11; 8:45 am]
BILLING CODE 4160-01-P