National Institute on Deafness and Other Communication Disorders; Amended Notice of Meeting, 18582 [E9-9204]
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18582
Federal Register / Vol. 74, No. 77 / Thursday, April 23, 2009 / Notices
35 U.S.C. 207 to achieve expeditious
commercialization of results of
federally-funded research and
development. Foreign patent
applications are filed on selected
inventions to extend market coverage
for companies and may also be available
for licensing.
ADDRESSES: Licensing information and
copies of the U.S. patent applications
listed below may be obtained by writing
to the indicated licensing contact at the
Office of Technology Transfer, National
Institutes of Health, 6011 Executive
Boulevard, Suite 325, Rockville,
Maryland 20852–3804; telephone: 301/
496–7057; fax: 301/402–0220. A signed
Confidential Disclosure Agreement will
be required to receive copies of the
patent applications.
sroberts on PROD1PC70 with NOTICES
Identification of Subjects Likely To
Benefit From Copper Treatment
Description of Technology: Menkes
disease is an infantile onset X-linked
recessive neurodegenerative disorder
caused by deficiency or dysfunction of
a copper-transporting ATPase, ATP7A.
The clinical and pathologic features of
this condition reflect decreased
activities of enzymes that require copper
as a cofactor, including dopamine-bhydrolase, cytochrome c oxidase and
lysyl oxidase. Recent studies indicate
that ATP7A normally responds to Nmethyl-D-aspartate receptor activation
in the brain, and an impaired response
probably contributes to the
neuropathology of Menkes disease.
Affected infants appear healthy at birth
and develop normally for 6 to 8 weeks.
Subsequently, hypotonia, seizures and
failure to thrive occur and death by 3
years of age is typical. Occipital horn
syndrome (OHS) is also caused by
mutations in the copper transporting
ATPase ATP7A, although its symptoms
are milder than Menkes syndrome,
including occipital horns and lax skin
and joints.
Treatment with daily copper
injections may improve the outcome in
Menkes disease if commenced within
days after birth; however, newborn
screening for this disorder is not
available and early detection is difficult
because clinical abnormalities in
affected newborns are absent or subtle.
Moreover, the usual biochemical
markers (low serum copper and
ceruloplasmin) are unreliable predictors
in the neonatal period, since levels in
healthy newborns are low and overlap
with those in infants with Menkes
disease. Although molecular diagnosis
is available, its use is complicated by
the diversity of mutation types and the
large size of ATP7A (about 140kb).
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16:59 Apr 22, 2009
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Thus, there is a need for improved
methods for early detection of infants
with Menkes disease or OHS in order to
improve outcomes.
This technology relates to methods of
identifying individuals who may benefit
from treatment with copper, particularly
those having Menkes disease or
Occipital Horn Syndrome.
Inventor: Stephen G. Kaler (NICHD).
Publication: SG Kaler, CS Holmes, DS
Goldstein, JR Tang, SC Godwin, A
Donsante, CJ Liew, S Sato, N Patronas.
Neonatal diagnosis and treatment of
Menkes disease. N Engl J Med. 2008 Feb
7;358(6):605–614.
Patent Status: PCT Application No.
PCT/US2008/078966 filed 06 Oct 2008
(HHS Reference No. E–186–2008/0–
PCT–01).
Licensing Status: Available for
licensing.
Licensing Contact: Fatima Sayyid,
M.H.P.M.; 301–435–4521;
Fatima.Sayyid@hhs.nih.gov.
Collaborative Research Opportunity:
The National Institute of Child Health
and Human Development, Division of
Intramural Research, Molecular
Medicine Program, Unit on Pediatric
Genetics, is seeking statements of
capability or interest from parties
interested in collaborative research to
further develop, evaluate, or
commercialize population-based
newborn screening for Menkes disease
and related disorders of copper
transport in order to identify subjects
likely to benefit from copper injections
and other treatments. Please contact
Alan Hubbs, PhD at 301–594–4263 or
hubbsa@mail.nih.gov for more
information.
Polyclonal Antibody Against Bloom’s
Syndrome Protein (BLM) for Research
and Diagnostic Use
Description of Technology:
Investigators at the National Institutes of
Health have generated a polyclonal
antibody against Bloom’s syndrome
protein (BLM). The BLM protein is a
DNA helicase enzyme and a key
component of the DNA damage
response signaling pathway. Several
protein kinases including ATM, DNA–
PK, and ATR can mediate the
phosphorylation of BLM. The
polyclonal antibody is generated by
using a phosphorylated peptide
belonging to the N-terminus of BLM.
The antibody shows a rapid
phosphorylation of BLM on threonine
99 (T99p-BLM) following DNA damage
by anti-cancer agents and could serve as
a therapeutic marker of drug action on
DNA. The antibody is also useful for
microscopic and biochemical analysis of
DNA damage signaling.
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Applications:
• A therapeutic marker of drug action
on DNA
• A diagnostic indicator of inherent
genomic instability
Inventors: Yves Pommier and V.
Ashutosh Rao (NCI)
Patent Status: HHS Reference No. E–
053–2006/0—Research Tool. Patent
protection is not being sought for this
technology.
Licensing Status: Threonine 99
specific polyclonal antibody against the
BLM protein is available for licensing.
Licensing Contact: Betty Tong, PhD;
301–594–6565; tongb@mail.nih.gov.
Dated: April 16, 2009.
Richard U. Rodriguez,
Director, Division of Technology Development
and Transfer, Office of Technology Transfer,
National Institutes of Health.
[FR Doc. E9–9345 Filed 4–22–09; 8:45 am]
BILLING CODE 4140–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
National Institute on Deafness and
Other Communication Disorders;
Amended Notice of Meeting
Notice is hereby given of a change in
the meeting of the National Institute on
Deafness and Other Communication
Disorders Special Emphasis Panel, April
28, 2009, 1 p.m. to April 28, 2009, 4
p.m., National Institutes of Health,
Bethesda, MD which was published in
the Federal Register on April 6, 2009,
7415501.
The meeting will be held April 29,
2009. The meeting is closed to the
public.
Dated: April 15, 2009.
Jennifer Spaeth,
Director, Office of Federal Advisory
Committee Policy.
[FR Doc. E9–9204 Filed 4–22–09; 8:45 am]
BILLING CODE 4140–01–M
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
National Institute on Drug Abuse;
Notice of Closed Meetings
Pursuant to section 10(d) of the
Federal Advisory Committee Act, as
amended (5 U.S.C. App.), notice is
hereby given of the following meetings.
The meetings will be closed to the
public in accordance with the
provisions set forth in sections
552b(c)(4) and 552b(c)(6), Title 5 U.S.C.,
E:\FR\FM\23APN1.SGM
23APN1
Agencies
[Federal Register Volume 74, Number 77 (Thursday, April 23, 2009)]
[Notices]
[Page 18582]
From the Federal Register Online via the Government Printing Office [www.gpo.gov]
[FR Doc No: E9-9204]
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DEPARTMENT OF HEALTH AND HUMAN SERVICES
National Institutes of Health
National Institute on Deafness and Other Communication Disorders;
Amended Notice of Meeting
Notice is hereby given of a change in the meeting of the National
Institute on Deafness and Other Communication Disorders Special
Emphasis Panel, April 28, 2009, 1 p.m. to April 28, 2009, 4 p.m.,
National Institutes of Health, Bethesda, MD which was published in the
Federal Register on April 6, 2009, 7415501.
The meeting will be held April 29, 2009. The meeting is closed to
the public.
Dated: April 15, 2009.
Jennifer Spaeth,
Director, Office of Federal Advisory Committee Policy.
[FR Doc. E9-9204 Filed 4-22-09; 8:45 am]
BILLING CODE 4140-01-M