Licensing and/or Cooperative Research and Development Agreement (CRADA) Opportunities-Enhanced T-cell Activation by Costimulation: A Potentially Novel Approach for the Prevention and/or Therapy of Cancer (Excluding Prostate Diseases and Melanoma) and for Infectious Diseases, 49686-49688 [E8-19462]
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49686
Federal Register / Vol. 73, No. 164 / Friday, August 22, 2008 / Notices
TABLE A—ANNUALIZED BURDEN ESTIMATES FOR CHIS 2009—Continued
Frequency
of response
Adolescent Pilot ........................................
Adolescent Survey ...................................
8
2,000.00
1
1
2/60
2/60
.27
66.67
...................................................................
26,083
....................
....................
3,276.94
Form type
Adolescents ..............................................
Total ...................................................
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Dated: August 13, 2008.
Vivian Horovitch-Kelley,
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[FR Doc. E8–19453 Filed 8–21–08; 8:45 am]
jlentini on PROD1PC65 with NOTICES
BILLING CODE 4140–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
Licensing and/or Cooperative
Research and Development Agreement
(CRADA) Opportunities—Enhanced Tcell Activation by Costimulation: A
Potentially Novel Approach for the
Prevention and/or Therapy of Cancer
(Excluding Prostate Diseases and
Melanoma) and for Infectious Diseases
National Institutes of Health,
Public Health Service, HHS.
AGENCY:
ACTION:
Notice.
SUMMARY: The inventions listed below
are owned by an agency of the U.S.
Government and are available for
licensing in the U.S. in accordance with
35 U.S.C. 207 to achieve expeditious
commercialization of results of
federally-funded research and
development. Foreign patent
applications are filed on selected
inventions to extend market coverage
for companies and may also be available
for licensing. Cooperative Research and
Development Agreement (CRADA)
opportunities are also available.
FOR FURTHER INFORMATION CONTACT:
Licensing information and copies of the
U.S. patent applications listed below
may be obtained by contacting Mojdeh
Bahar, J.D., Office of Technology
Transfer, National Institutes of Health,
6011 Executive Boulevard, Suite 325,
Rockville MD 20852; telephone: 301/
435–2950; e-mail:
baharm@mail.nih.gov. A signed
Confidential Disclosure Agreement will
be required to receive copies of the
patent applications. If interested in a
Cooperative Research and Development
Agreement (CRADA) Opportunity,
please submit a statement of interest
and capability to Kevin Brand, J.D., in
the NCI Technology Transfer Center,
6120 Executive Boulevard, Suite 450,
Rockville MD 20852; telephone: 301/
451–4566; e-mail: kb229t@nih.gov.
SUPPLEMENTARY INFORMATION:
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time per
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Number of
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Type of respondent
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Description of Technology
Cancer immunotherapy is a recent
approach where tumor associated
antigens (TAAs), which are primarily
expressed in human tumor cells and not
expressed or minimally expressed in
normal tissues, are employed to
generate a tumor specific immune
response. Specifically, these antigens
serve as targets for the host immune
system and elicit responses that results
in tumor destruction. The initiation of
an effective T-cell immune response to
antigens requires two signals. The first
one is antigen specific via the peptide/
major histocompatibility complex and
the second or ‘‘costimulatory’’ signal is
required for cytokine production,
proliferation, and other aspects of T-cell
activation.
The present technology describes
recombinant poxvirus vectors encoding
at least three or more costimulatory
molecules and tumor associated
antigens (TAAs). The use of three
costimulatory molecules such as B7.1,
ICAM–1 and LFA–3 (TRICOM) has
been shown to act in synergy with
several tumor antigens and antigen
epitopes to activate T cells. The effects
with TRICOM were significantly
greater than with one or two
costimulatory molecules. Laboratory
results support the greater effect of
TRICOM to activate both CD4∂ and
CD8∂ T cells. The invention also
describes the use of at least one target
antigen or immunological epitope as an
immunogen or vaccine in conjunction
with TRICOM. The antigens include
but are not limited to carcinoembryonic
antigen (CEA) and MUC–1. The
combination of CEA, MUC–1, and
TRICOM is referred to as PANVAC.
Availability
The technology is available for
exclusive and non-exclusive license in
combinations and fields of use. Some
potential licensing opportunities
involving recombinant poxviral vectors
containing transgenes are as follows:
(1) TRICOM (alone or with a
transgene for a tumor antigen and/or an
immunostimulatory molecule);
E:\FR\FM\22AUN1.SGM
22AUN1
Federal Register / Vol. 73, No. 164 / Friday, August 22, 2008 / Notices
(2) The antigens only, including but
not limited to CEA and MUC–1;
PANVAC; and
(3) Recombinant fowlpox–GM–CSF.
Applications and Modality
Vector-based TRICOM (alone or with
a transgene(s) for a tumor antigen and/
or an immunostimulatory molecule(s)),
PANVAC and combinations thereof
can be a potential novel approach for
the prevention or treatment of cancer
(with the exclusion of prostate cancer,
prostatic diseases, and melanoma) and
infectious diseases.
Advantages
• The technology is beyond proof-ofconcept, supported by laboratory results
and publications.
• Phase I and Phase II clinical data
available (to qualified licensees).
• Fewer validation studies are
required compared to other
immunotherapy related technologies.
Development Status
Phase I and Phase II results available
(to qualified licensees) for poxvirus
recombinants containing transgenes for
TRICOM, CEA–TRICOM, and
PANVAC. Further clinical studies are
ongoing.
jlentini on PROD1PC65 with NOTICES
Inventors
Jeffrey Schlom (NCI) et al. (Inventor
Web page: https://ccr.cancer.gov/Staff/
staff.asp?profileid=5444).
Publications
1. Kudo-Saito C, Wansley EK, Gruys
ME, Wiltrout R, Schlom J and Hodge
JW. Combination therapy of an
orthotopic renal cell carcinoma model
employing intratumoral vector-mediated
costimulation and systemic IL–2. Clin
Cancer Res. 13:1936–1946, 2007.
2. Chakraborty M, Schlom J, and
Hodge JW. The combined activation of
positive costimulatory signals with
modulation of a negative costimulatory
signal for the enhancement of vaccine
mediated T-cell responses. Cancer
Immunol Immunother. 56:1471–1484,
2007.
3. Kudo-Saito C, Garnett CT, Wansley
EK, Schlom J, and Hodge JW.
Intratumoral delivery of vector mediated
IL–2 in combination with vaccine
results in enhanced T-cell avidity and
anti-tumor activity. Cancer Immunol
Immunother. 56:1897–1910, 2007.
4. Garnett CT, Schlom J, and Hodge
JW. Combination of docetaxel and
recombinant vaccine enhances T-cell
responses and antitumor activity: Effects
of docetaxel on immune enhancement.
Clin Cancer Res. (in press).
5. Chakraborty M, Gelbard A,
Carrasquillo JA, Yu S, Mamede M, Park
VerDate Aug<31>2005
17:12 Aug 21, 2008
Jkt 214001
CH, Camphuasen K, Schlom J, and
Hodge JW. Use of radiolabeled
monoclonal antibody to enhance
vaccine-mediated antitumor effects.
Cancer Immunol Immunother. 56:1471–
1484, 2007.
6. Litzinger MT, Fernando R, Curiel
TJ, Grosenbach DW, Schlom J, and
Palena C. The IL–2 immunotoxin
denileukin diftitox reduces regulatory
T-cells and enhances vaccine-mediated
T-cell immunity. Blood 110:3192–3201,
2007.
7. Gelbard A, Garnett CT, Abrams SI,
Patel V, Gutkind JS, Palena C, Tsang KY,
Schlom J, and Hodge JW. Combination
chemotherapy and radiation of human
squamous cell carcinoma of the head
and neck augments CTL-mediated lysis.
Clin Cancer Res. 12:1897–1905, 2006.
8. Kaufman HL, Cohen S, Cheung K,
DeRaffele, Mitcham J, Moroziewicz D,
Schlom J, and Hesdorffer C. Local
delivery of vaccinia virus expressing
multiple costimulatory molecules for
the treatment of established tumors.
Human Gene Ther. 17:239–244, 2006.
9. Marshall J, Gulley JL, Arlen PM,
Beetham PK, Tsang KY, Slack R, Hodge
JW, Doren S, Grosenbach DW, Hwang J,
Fox E, Odogwa L, Park S, Panicali D,
Schlom J. A phase I study of sequential
vaccinations with fowlpox-CEA(6D)TRICOM (B7–1/ICAM–1/LFA–3) alone
and sequentially with vacciniaCEA(6D)-TRICOM, with and without
GM-CSF, in patients with CEAexpressing carcinomas. J Clin Oncol.
23:720–731, 2005.
10. Palena C, Foon KA, Panicali D,
Yafal AG, Chinsangaram J, Hodge JW,
Schlom J, and Tsang KY. A potential
approach to immunotherapy of chronic
lymphocytic leukemia (CLL): enhanced
immunogenicity of CLL cells via
infection with vectors encoding for
multiple costimulatory molecules.
Blood 106:3515–3523, 2005.
11. Yang S, Hodge JW, Grosenbach
DW, and Schlom J. Vaccines with
enhanced costimulation maintain high
avidity memory CTL. J. Immunol.
175:3715–3723, 2005.
12. Yang S, Tsang KY, and Schlom J.
Induction of higher avidity human CTL
by vector-mediated enhanced
costimulation of antigen-presenting
cells. Clin Cancer Res. 11:5603–5615,
2005.
13. Hodge JW, Chakraborty M, KudoSaito C, Garnett CT, Schlom J. Multiple
costimulatory modalities enhance CTL
avidity. J Immunol 174:5994–6004,
2005.
14. Tsang K-Y, Palena C, Yokokawa J,
Arlen PM, Gulley JL, Mazzara GP, Gritz
´
L, Gomez Yafal A, Ogueta S, Greenhalgh
P, Manson K, Panicali D, and Schlom J.
Analyses of recombinant vaccinia and
PO 00000
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Fmt 4703
Sfmt 4703
49687
fowlpox vaccine vectors expressing
transgenes for two human tumor
antigens and three human costimulatory
molecules. Clin Cancer Res. 11:1597–
1607, 2005.
15. Chakraborty M, Abrams SI,
Coleman CN, Camphausen K, Schlom J,
Hodge JW. External beam radiation of
tumors alters phenotype of tumor cells
to render them susceptible to vaccinemediated T-cell killing. Cancer Res.
64:4328–4337, 2004.
16. Zeytin HE, Patel AC, Rogers CJ, et
al. Combination of a poxvirus-based
vaccine with a cyclooxygenase-2
inhibitor (celecoxib) elicits antitumor
immunity and long-term survival in
CEA.Tg/MIN mice. Cancer Res.
64:3668–3678, 2004.
17. Palena C, Zhu M-Z, Schlom J, and
Tsang K-Y. Human B cells that
hyperexpress a triad of costimulatory
molecules via avipoxvector infection:
An alternative source of efficient
antigen-presenting cells. Blood 104:192–
199, 2004.
18. Kudo-Saito C, Schlom J, and
Hodge JW. Intratumoral vaccination and
diversified subcutaneous/intratumoral
vaccination with recombinant
poxviruses encoding a tumor antigen
and multiple costimulatory molecules.
Clin Cancer Res. 10:1090–1099, 2004.
19. Hodge JW, Poole DJ, Aarts WM,
´
Gomez Yafal A, Gritz L, and Schlom J.
Modified vaccinia virus ankara
recombinants are as potent as vaccinia
recombinants in diversified prime and
boost vaccine regimens to elicit
therapeutic antitumor responses. Cancer
Res. 63:7942–7949, 2003.
20. Hodge JW, Grosenbach DW, Aarts
WM, Poole DJ, and Schlom J. Vaccine
therapy of established tumors in the
absence of autoimmunity. Clin Cancer
Res. 9:1837–1849, 2003.
21. Aarts WM, Schlom J, and Hodge
JW. Vector-based vaccine/cytokine
combination therapy to enhance
induction of immune responses to a
self-antigen and anti-tumor activity.
Cancer Res. 62:5770–5777, 2002.
22. Hodge JW, Sabzevari H, Yafal AG,
Gritz L, Lorenz MG, Schlom J. A triad
of costimulatory molecules synergize to
amplify T-cell activation. Cancer Res.
59: 5800–5807, 1999.
Patent Status
1. U.S. Patent No. 6,969,609 issued
November 29, 2005 as well as issued
and pending foreign counterparts [HHS
Ref. No. E–256–1998/0];
2. U.S. Patent Application No. 11/
321,868 filed December 30, 2005 [HHS
Ref. No. E–256–1998/1]; and
3. U.S. Patent No. 6,756,038 issued
June 29, 2004 as well as issued and
E:\FR\FM\22AUN1.SGM
22AUN1
49688
Federal Register / Vol. 73, No. 164 / Friday, August 22, 2008 / Notices
jlentini on PROD1PC65 with NOTICES
pending foreign counterparts [HHS Ref.
No. E–099–1996/0];
4. U.S. Patent No. 6,001,349 issued
December 14, 1999 as well as issued and
pending foreign counterparts [HHS Ref.
No E–200–1990/3–US–01];
5. U.S. Patent No.6,165,460 issued
December 26, 2000; as well as issued
and pending foreign counterparts [HHS
Ref. No E–200–1990/4–US–01];
6. U.S. Patent No. 7,118,738 issued
October 10, 2006 as well as issued and
pending foreign counterparts [HHS Ref.
No E–154–1998/0–US–07];
7. PCT Application No. PCT/US97/
12203 filed July 15, 1997 [HHS Ref. No
E–259–1994/3–PCT–02];
8. U.S. Patent Application Nos. 10/
197,127. and 08/686,280 filed July 17,
2002 and July 25, 1996 [HHS Ref. No E–
259–1994/3–US–08 and /4–US–01];
9. U.S. Patent No. 6,946,133 issued
September 20, 2005 as well as issued
and pending foreign counterparts [HHS
Ref. No E–062–1996/0–US–01];
10. U.S. Patent Application No. 11/
606,929 filed December 1, 2006 [E–062–
1996/0–US–11];
11. U.S. Patent Nos. 6,893,869,
6,548,068 and 6,045,802 issued May 17,
2005, April 15, 2003 and April 4, 2000
respectively, as well as issued and
pending foreign counterparts [HHS Ref.
Nos. E–260–1994/1–US–03, US–02, US–
01]; and
12. U.S. Patent. Application No. 11/
090,686 filed March 8, 2005 [HHS Ref.
No E–260–1994/1–US–04].
Cooperative Research and Development
Agreement (CRADA) Opportunities
A CRADA partner for the further codevelopment of this technology is
currently being sought by the Laboratory
of Tumor Immunology and Biology,
Center for Cancer Research, NCI. The
CRADA partner will (a) generate and
characterize recombinant poxviruses
expressing specific tumor-associated
antigens, cytokines, and/or T-cell
costimulatory factors, (b) analyze the
recombinant poxviruses containing
these genes with respect to appropriate
expression of the encoded gene
product(s), (c) supply adequate amounts
of recombinant virus stocks for
preclinical testing, (d) manufacture and
test selected recombinant viruses for use
in human clinical trials (with the
exception of trials for prostatic diseases
and melanoma), (e) submit Drug Master
Files detailing the development,
manufacture, and testing of live
recombinant vaccines to support the
NCI-sponsored IND and/or companysponsored IND, (f) supply adequate
amounts of clinical grade recombinant
poxvirus vaccines for clinical trials
conducted at the NCI Center for Cancer
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17:12 Aug 21, 2008
Jkt 214001
Research (CCR), and (g) provide
adequate amounts of vaccines for
extramural clinical trials, if agreed upon
by the parties, and conduct clinical
trials under company-sponsored or NCIsponsored INDs. NCI will (a) provide
genes of tumor-associated antigens,
cytokines and other immunostimulatory
molecules for incorporation into
poxvirus vectors, (b) evaluate
recombinant vectors in preclinical
models alone and in combination
therapies, and (c) conduct clinical trials
(with the exception of trials for prostatic
diseases and melanoma) of recombinant
vaccines alone and in combination
therapies.
Dated: August 14, 2008
Richard U. Rodriguez,
Director, Division of Technology Development
and Transfer, Office of Technology Transfer,
National Institutes of Health.
[FR Doc. E8–19462 Filed 8–21–08; 8:45 am]
BILLING CODE 4140–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
National Institute of Neurological
Disorders and Stroke; Notice of
Meeting
Pursuant to section 10(d) of the
Federal Advisory Committee Act, as
amended (5 U.S.C. Appendix 2), notice
is hereby given of a meeting of the
National Advisory Neurological
Disorders and Stroke Council.
The meeting will be open to the
public as indicated below, with
attendance limited to space available.
Individuals who plan to attend and
need special assistance, such as sign
language interpretation or other
reasonable accommodations, should
notify the Contact Person listed below
in advance of the meeting.
The meeting will be closed to the
public in accordance with the
provisions set forth in sections
552b(c)(4) and 552b(c)(6), Title 5 U.S.C.,
as amended. The grant applications and
the discussions could disclose
confidential trade secrets or commercial
property such as patentable material,
and personal information concerning
individuals associated with the grant
applications, the disclosure of which
would constitute a clearly unwarranted
invasion of personal privacy.
Name of Committee: National Advisory
Neurological Disorders and Stroke Council;
Clinical Trials Subcommittee.
Date: September 18, 2008.
Closed: 8 a.m. to 9 a.m.
Agenda: To review and evaluate grant
applications and/or proposals.
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Place: National Institutes of Health,
Building 31, 31 Center Drive, C Wing,
Conference Room 10, Bethesda, MD 20892.
Open: 9 a.m. to 10 a.m.
Agenda: To discuss clinical trials policy.
Place: National Institutes of Health,
Building 31, 31 Center Drive, C Wing,
Conference Room 10, Bethesda, MD 20892.
Contact Person: Deborah G Hirtz, MD,
Acting Director, Clinical Trials Cluster,
National Institute of Neurological, Disorders
and Stroke, National Institute of Health, 6001
Executive Blvd., Suite 2212, Bethesda, MD
20892, (301) 496–5821, hirtz@ninds.nih.gov.
In the interest of security, NIH has
instituted stringent procedures for entrance
onto the NIH campus. All visitor vehicles,
including taxicabs, hotel, and airport shuttles
will be inspected before being allowed on
campus. Visitors will be asked to show one
form of identification (for example, a
government-issued photo ID, driver’s license,
or passport) and to state the purpose of their
visit.
Information is also available on the
Institute’s/Center’s home page:
www.ninds.nih.gov, where an agenda and
any additional information for the meeting
will be posted when available.
(Catalogue of Federal Domestic Assistance
Program Nos. 93.853, Clinical Research
Related to NeurologicalDisorders; 93.854,
Biological Basis Research in the
Neurosciences, National Institutes of Health,
HHS)
Dated: August 15, 2008.
Jennifer Spaeth,
Director, Office of Federal Advisory
Committee Policy.
[FR Doc. E8–19442 Filed 8–21–08; 8:45 am]
BILLING CODE 4140–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
National Institute of Neurological
Disorders and Stroke; Notice of
Meetings
Pursuant to section 10(a) of the
Federal Advisory Committee Act, as
amended (5 U.S.C. Appendix 2), notice
is hereby given of meetings of the
National Advisory Neurological
Disorders and Stroke Council.
The meetings will be open to the
public, with attendance limited to space
available. Individuals who plan to
attend and need special assistance, such
as sign language interpretation or other
reasonable accommodations, should
notify the Contact Person listed below
in advance of the meeting.
Name of Committee: National Advisory
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Training, Career Development, and Special
Programs Subcommittees.
Date: September 17, 2008.
Time: 8 p.m. to 10 p.m.
E:\FR\FM\22AUN1.SGM
22AUN1
Agencies
[Federal Register Volume 73, Number 164 (Friday, August 22, 2008)]
[Notices]
[Pages 49686-49688]
From the Federal Register Online via the Government Printing Office [www.gpo.gov]
[FR Doc No: E8-19462]
-----------------------------------------------------------------------
DEPARTMENT OF HEALTH AND HUMAN SERVICES
National Institutes of Health
Licensing and/or Cooperative Research and Development Agreement
(CRADA) Opportunities--Enhanced T-cell Activation by Costimulation: A
Potentially Novel Approach for the Prevention and/or Therapy of Cancer
(Excluding Prostate Diseases and Melanoma) and for Infectious Diseases
AGENCY: National Institutes of Health, Public Health Service, HHS.
ACTION: Notice.
-----------------------------------------------------------------------
SUMMARY: The inventions listed below are owned by an agency of the U.S.
Government and are available for licensing in the U.S. in accordance
with 35 U.S.C. 207 to achieve expeditious commercialization of results
of federally-funded research and development. Foreign patent
applications are filed on selected inventions to extend market coverage
for companies and may also be available for licensing. Cooperative
Research and Development Agreement (CRADA) opportunities are also
available.
FOR FURTHER INFORMATION CONTACT: Licensing information and copies of
the U.S. patent applications listed below may be obtained by contacting
Mojdeh Bahar, J.D., Office of Technology Transfer, National Institutes
of Health, 6011 Executive Boulevard, Suite 325, Rockville MD 20852;
telephone: 301/435-2950; e-mail: baharm@mail.nih.gov. A signed
Confidential Disclosure Agreement will be required to receive copies of
the patent applications. If interested in a Cooperative Research and
Development Agreement (CRADA) Opportunity, please submit a statement of
interest and capability to Kevin Brand, J.D., in the NCI Technology
Transfer Center, 6120 Executive Boulevard, Suite 450, Rockville MD
20852; telephone: 301/451-4566; e-mail: kb229t@nih.gov.
SUPPLEMENTARY INFORMATION:
Description of Technology
Cancer immunotherapy is a recent approach where tumor associated
antigens (TAAs), which are primarily expressed in human tumor cells and
not expressed or minimally expressed in normal tissues, are employed to
generate a tumor specific immune response. Specifically, these antigens
serve as targets for the host immune system and elicit responses that
results in tumor destruction. The initiation of an effective T-cell
immune response to antigens requires two signals. The first one is
antigen specific via the peptide/major histocompatibility complex and
the second or ``costimulatory'' signal is required for cytokine
production, proliferation, and other aspects of T-cell activation.
The present technology describes recombinant poxvirus vectors
encoding at least three or more costimulatory molecules and tumor
associated antigens (TAAs). The use of three costimulatory molecules
such as B7.1, ICAM-1 and LFA-3 (TRICOM[reg]) has been shown
to act in synergy with several tumor antigens and antigen epitopes to
activate T cells. The effects with TRICOM[reg] were
significantly greater than with one or two costimulatory molecules.
Laboratory results support the greater effect of TRICOM[reg]
to activate both CD4+ and CD8+ T cells. The
invention also describes the use of at least one target antigen or
immunological epitope as an immunogen or vaccine in conjunction with
TRICOM[reg]. The antigens include but are not limited to
carcinoembryonic antigen (CEA) and MUC-1. The combination of CEA, MUC-
1, and TRICOM[reg] is referred to as PANVAC[reg].
Availability
The technology is available for exclusive and non-exclusive license
in combinations and fields of use. Some potential licensing
opportunities involving recombinant poxviral vectors containing
transgenes are as follows:
(1) TRICOM[reg] (alone or with a transgene for a tumor
antigen and/or an immunostimulatory molecule);
[[Page 49687]]
(2) The antigens only, including but not limited to CEA and MUC-1;
PANVAC[reg]; and
(3) Recombinant fowlpox-GM-CSF.
Applications and Modality
Vector-based TRICOM[reg] (alone or with a transgene(s)
for a tumor antigen and/or an immunostimulatory molecule(s)),
PANVAC[reg] and combinations thereof can be a potential
novel approach for the prevention or treatment of cancer (with the
exclusion of prostate cancer, prostatic diseases, and melanoma) and
infectious diseases.
Advantages
The technology is beyond proof-of-concept, supported by
laboratory results and publications.
Phase I and Phase II clinical data available (to qualified
licensees).
Fewer validation studies are required compared to other
immunotherapy related technologies.
Development Status
Phase I and Phase II results available (to qualified licensees) for
poxvirus recombinants containing transgenes for TRICOM[reg],
CEA-TRICOM[reg], and PANVAC[reg]. Further
clinical studies are ongoing.
Inventors
Jeffrey Schlom (NCI) et al. (Inventor Web page: https://
ccr.cancer.gov/Staff/staff.asp?profileid=5444).
Publications
1. Kudo-Saito C, Wansley EK, Gruys ME, Wiltrout R, Schlom J and
Hodge JW. Combination therapy of an orthotopic renal cell carcinoma
model employing intratumoral vector-mediated costimulation and systemic
IL-2. Clin Cancer Res. 13:1936-1946, 2007.
2. Chakraborty M, Schlom J, and Hodge JW. The combined activation
of positive costimulatory signals with modulation of a negative
costimulatory signal for the enhancement of vaccine mediated T-cell
responses. Cancer Immunol Immunother. 56:1471-1484, 2007.
3. Kudo-Saito C, Garnett CT, Wansley EK, Schlom J, and Hodge JW.
Intratumoral delivery of vector mediated IL-2 in combination with
vaccine results in enhanced T-cell avidity and anti-tumor activity.
Cancer Immunol Immunother. 56:1897-1910, 2007.
4. Garnett CT, Schlom J, and Hodge JW. Combination of docetaxel and
recombinant vaccine enhances T-cell responses and antitumor activity:
Effects of docetaxel on immune enhancement. Clin Cancer Res. (in
press).
5. Chakraborty M, Gelbard A, Carrasquillo JA, Yu S, Mamede M, Park
CH, Camphuasen K, Schlom J, and Hodge JW. Use of radiolabeled
monoclonal antibody to enhance vaccine-mediated antitumor effects.
Cancer Immunol Immunother. 56:1471-1484, 2007.
6. Litzinger MT, Fernando R, Curiel TJ, Grosenbach DW, Schlom J,
and Palena C. The IL-2 immunotoxin denileukin diftitox reduces
regulatory T-cells and enhances vaccine-mediated T-cell immunity. Blood
110:3192-3201, 2007.
7. Gelbard A, Garnett CT, Abrams SI, Patel V, Gutkind JS, Palena C,
Tsang KY, Schlom J, and Hodge JW. Combination chemotherapy and
radiation of human squamous cell carcinoma of the head and neck
augments CTL-mediated lysis. Clin Cancer Res. 12:1897-1905, 2006.
8. Kaufman HL, Cohen S, Cheung K, DeRaffele, Mitcham J, Moroziewicz
D, Schlom J, and Hesdorffer C. Local delivery of vaccinia virus
expressing multiple costimulatory molecules for the treatment of
established tumors. Human Gene Ther. 17:239-244, 2006.
9. Marshall J, Gulley JL, Arlen PM, Beetham PK, Tsang KY, Slack R,
Hodge JW, Doren S, Grosenbach DW, Hwang J, Fox E, Odogwa L, Park S,
Panicali D, Schlom J. A phase I study of sequential vaccinations with
fowlpox-CEA(6D)-TRICOM (B7-1/ICAM-1/LFA-3) alone and sequentially with
vaccinia-CEA(6D)-TRICOM, with and without GM-CSF, in patients with CEA-
expressing carcinomas. J Clin Oncol. 23:720-731, 2005.
10. Palena C, Foon KA, Panicali D, Yafal AG, Chinsangaram J, Hodge
JW, Schlom J, and Tsang KY. A potential approach to immunotherapy of
chronic lymphocytic leukemia (CLL): enhanced immunogenicity of CLL
cells via infection with vectors encoding for multiple costimulatory
molecules. Blood 106:3515-3523, 2005.
11. Yang S, Hodge JW, Grosenbach DW, and Schlom J. Vaccines with
enhanced costimulation maintain high avidity memory CTL. J. Immunol.
175:3715-3723, 2005.
12. Yang S, Tsang KY, and Schlom J. Induction of higher avidity
human CTL by vector-mediated enhanced costimulation of antigen-
presenting cells. Clin Cancer Res. 11:5603-5615, 2005.
13. Hodge JW, Chakraborty M, Kudo-Saito C, Garnett CT, Schlom J.
Multiple costimulatory modalities enhance CTL avidity. J Immunol
174:5994-6004, 2005.
14. Tsang K-Y, Palena C, Yokokawa J, Arlen PM, Gulley JL, Mazzara
GP, Gritz L, G[oacute]mez Yafal A, Ogueta S, Greenhalgh P, Manson K,
Panicali D, and Schlom J. Analyses of recombinant vaccinia and fowlpox
vaccine vectors expressing transgenes for two human tumor antigens and
three human costimulatory molecules. Clin Cancer Res. 11:1597-1607,
2005.
15. Chakraborty M, Abrams SI, Coleman CN, Camphausen K, Schlom J,
Hodge JW. External beam radiation of tumors alters phenotype of tumor
cells to render them susceptible to vaccine-mediated T-cell killing.
Cancer Res. 64:4328-4337, 2004.
16. Zeytin HE, Patel AC, Rogers CJ, et al. Combination of a
poxvirus-based vaccine with a cyclooxygenase-2 inhibitor (celecoxib)
elicits antitumor immunity and long-term survival in CEA.Tg/MIN mice.
Cancer Res. 64:3668-3678, 2004.
17. Palena C, Zhu M-Z, Schlom J, and Tsang K-Y. Human B cells that
hyperexpress a triad of costimulatory molecules via avipoxvector
infection: An alternative source of efficient antigen-presenting cells.
Blood 104:192-199, 2004.
18. Kudo-Saito C, Schlom J, and Hodge JW. Intratumoral vaccination
and diversified subcutaneous/intratumoral vaccination with recombinant
poxviruses encoding a tumor antigen and multiple costimulatory
molecules. Clin Cancer Res. 10:1090-1099, 2004.
19. Hodge JW, Poole DJ, Aarts WM, G[oacute]mez Yafal A, Gritz L,
and Schlom J. Modified vaccinia virus ankara recombinants are as potent
as vaccinia recombinants in diversified prime and boost vaccine
regimens to elicit therapeutic antitumor responses. Cancer Res.
63:7942-7949, 2003.
20. Hodge JW, Grosenbach DW, Aarts WM, Poole DJ, and Schlom J.
Vaccine therapy of established tumors in the absence of autoimmunity.
Clin Cancer Res. 9:1837-1849, 2003.
21. Aarts WM, Schlom J, and Hodge JW. Vector-based vaccine/cytokine
combination therapy to enhance induction of immune responses to a self-
antigen and anti-tumor activity. Cancer Res. 62:5770-5777, 2002.
22. Hodge JW, Sabzevari H, Yafal AG, Gritz L, Lorenz MG, Schlom J.
A triad of costimulatory molecules synergize to amplify T-cell
activation. Cancer Res. 59: 5800-5807, 1999.
Patent Status
1. U.S. Patent No. 6,969,609 issued November 29, 2005 as well as
issued and pending foreign counterparts [HHS Ref. No. E-256-1998/0];
2. U.S. Patent Application No. 11/321,868 filed December 30, 2005
[HHS Ref. No. E-256-1998/1]; and
3. U.S. Patent No. 6,756,038 issued June 29, 2004 as well as issued
and
[[Page 49688]]
pending foreign counterparts [HHS Ref. No. E-099-1996/0];
4. U.S. Patent No. 6,001,349 issued December 14, 1999 as well as
issued and pending foreign counterparts [HHS Ref. No E-200-1990/3-US-
01];
5. U.S. Patent No.6,165,460 issued December 26, 2000; as well as
issued and pending foreign counterparts [HHS Ref. No E-200-1990/4-US-
01];
6. U.S. Patent No. 7,118,738 issued October 10, 2006 as well as
issued and pending foreign counterparts [HHS Ref. No E-154-1998/0-US-
07];
7. PCT Application No. PCT/US97/12203 filed July 15, 1997 [HHS Ref.
No E-259-1994/3-PCT-02];
8. U.S. Patent Application Nos. 10/197,127. and 08/686,280 filed
July 17, 2002 and July 25, 1996 [HHS Ref. No E-259-1994/3-US-08 and /4-
US-01];
9. U.S. Patent No. 6,946,133 issued September 20, 2005 as well as
issued and pending foreign counterparts [HHS Ref. No E-062-1996/0-US-
01];
10. U.S. Patent Application No. 11/606,929 filed December 1, 2006
[E-062-1996/0-US-11];
11. U.S. Patent Nos. 6,893,869, 6,548,068 and 6,045,802 issued May
17, 2005, April 15, 2003 and April 4, 2000 respectively, as well as
issued and pending foreign counterparts [HHS Ref. Nos. E-260-1994/1-US-
03, US-02, US-01]; and
12. U.S. Patent. Application No. 11/090,686 filed March 8, 2005
[HHS Ref. No E-260-1994/1-US-04].
Cooperative Research and Development Agreement (CRADA) Opportunities
A CRADA partner for the further co-development of this technology
is currently being sought by the Laboratory of Tumor Immunology and
Biology, Center for Cancer Research, NCI. The CRADA partner will (a)
generate and characterize recombinant poxviruses expressing specific
tumor-associated antigens, cytokines, and/or T-cell costimulatory
factors, (b) analyze the recombinant poxviruses containing these genes
with respect to appropriate expression of the encoded gene product(s),
(c) supply adequate amounts of recombinant virus stocks for preclinical
testing, (d) manufacture and test selected recombinant viruses for use
in human clinical trials (with the exception of trials for prostatic
diseases and melanoma), (e) submit Drug Master Files detailing the
development, manufacture, and testing of live recombinant vaccines to
support the NCI-sponsored IND and/or company-sponsored IND, (f) supply
adequate amounts of clinical grade recombinant poxvirus vaccines for
clinical trials conducted at the NCI Center for Cancer Research (CCR),
and (g) provide adequate amounts of vaccines for extramural clinical
trials, if agreed upon by the parties, and conduct clinical trials
under company-sponsored or NCI-sponsored INDs. NCI will (a) provide
genes of tumor-associated antigens, cytokines and other
immunostimulatory molecules for incorporation into poxvirus vectors,
(b) evaluate recombinant vectors in preclinical models alone and in
combination therapies, and (c) conduct clinical trials (with the
exception of trials for prostatic diseases and melanoma) of recombinant
vaccines alone and in combination therapies.
Dated: August 14, 2008
Richard U. Rodriguez,
Director, Division of Technology Development and Transfer, Office of
Technology Transfer, National Institutes of Health.
[FR Doc. E8-19462 Filed 8-21-08; 8:45 am]
BILLING CODE 4140-01-P