Government-Owned Inventions; Availability for Licensing, 33183-33185 [05-11221]
Download as PDF
Federal Register / Vol. 70, No. 108 / Tuesday, June 7, 2005 / Notices
For products regulated by the Center for
Biologics Evaluation and Research:
Elizabeth Callaghan, Center for
Biologics Evaluation and Research
(HFM–370), Food and Drug
Administration, 1401 Rockville
Pike, Rockville, MD 20852–1448,
301–827–3424.
SUPPLEMENTARY INFORMATION:
Dated: May 27, 2005.
Jeffrey Shuren,
Assistant Commissioner for Policy.
[FR Doc. 05–11266 Filed 6–6–05; 8:45 am]
I. Background
FDA is announcing the availability of
a draft guidance for industry entitled
‘‘Bar Code Label Requirements—
Questions and Answers.’’ Under FDA
regulations, certain human drug and
biological product labels must have a
bar code containing the drug’s NDC
number (69 FR 9120, February 26,
2004). Bar codes will help reduce the
number of medication errors in
hospitals and other health care settings
by allowing health care professionals to
use bar code scanning equipment to
verify that the right drug (in the right
dose and right route of administration)
is being given to the right patient at the
right time. This draft guidance is
intended to explain certain bar code
labeling requirements and their
application to human drug and
biological products.
This draft guidance is being issued
consistent with FDA’s good guidance
practices regulation (21 CFR 10.115).
The draft guidance, when finalized, will
represent the agency’s current thinking
on certain questions and answers on bar
code labeling requirements. It does not
create or confer any rights for or on any
person and does not operate to bind
FDA or the public. An alternative
approach may be used if such approach
satisfies the requirements of the
applicable statutes and regulations.
National Institutes of Health
II. Comments
Interested persons may submit to the
Division of Dockets Management (see
ADDRESSES) written or electronic
comments regarding this document.
Submit a single copy of electronic
comments or two paper copies of any
mailed comments, except that
individuals may submit one paper copy.
Comments are to be identified with the
docket number found in brackets in the
heading of this document. Received
comments may be seen in the Division
of Dockets Management between 9 a.m.
and 4 p.m., Monday through Friday.
III. Electronic Access
Persons with access to the Internet
may obtain the document at either http:/
/www.fda.gov/cder/guidance/index.htm,
https://www.fda.gov/cber/
guidelines.htm, or https://www.fda.gov/
ohrms/dockets/default.htm.
VerDate jul<14>2003
20:54 Jun 06, 2005
Jkt 205001
BILLING CODE 4160–01–S
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
Government-Owned Inventions;
Availability for Licensing
National Institutes of Health,
Public Health Service, DHHS.
ACTION: Notice.
AGENCY:
SUMMARY: The inventions listed below
are owned by an agency of the U.S.
Government and are available for
licensing in the U.S. in accordance with
35 U.S.C. 207 to achieve expeditious
commercialization of results of
federally-funded research and
development. Foreign patent
applications are filed on selected
inventions to extend market coverage
for companies and may also be available
for licensing.
ADDRESSES: Licensing information and
copies of the U.S. patent applications
listed below may be obtained by writing
to the indicated licensing contact at the
Office of Technology Transfer, National
Institutes of Health, 6011 Executive
Boulevard, Suite 325, Rockville,
Maryland 20852–3804; telephone: 301/
496–7057; fax: 301/402–0220. A signed
Confidential Disclosure Agreement will
be required to receive copies of the
patent applications.
Farnesyltransferase Inhibitors for
Treatment of Laminopathies, Cellular
Aging and Atherosclerosis
Francis Collins (NHGRI) et al.
U.S. Provisional Application No. 60/
648,307 filed 28 Jan 2005 (DHHS
Reference No. E–055–2005/0–US–01).
Licensing Contact: Fatima Sayyid;
301/435–4521; sayyidf@mail.nih.gov.
Hutchinson-Gilford Progeria
Syndrome (HGPS) is a very rare
progressive childhood disorder
characterized by premature aging
(progeria). Recently, the gene
responsible for HGPS was identified
(Eriksson M, Brown WT, Gordon LB,
Glynn MW, Singer J, Scott L, et al.
Recurrent de novo point mutations in
lamin A cause Hutchinson-Gilford
progeria syndrome. Nature 2003;
423(6937): 293–8), and HGPS joined a
group of syndromes—the
laminopathies—all of which are caused
by various mutations in the lamin A/C
gene (LMNA). Lamin A is one of the
PO 00000
Frm 00129
Fmt 4703
Sfmt 4703
33183
family of proteins that is modified posttranslationally by the addition of a
farnesyl group. In progeria, the
abnormal protein (progerin) can still be
farnesylated, however, a subsequent
cleavage is blocked.
The present invention describes a
possible treatment of laminopathies,
cellular aging and aging-related
conditions such as HGPS through the
use of farnesyltransferase inhibitors
(FTIs) and other related compounds.
This treatment should lead to a decrease
in the accumulation of abnormal
proteins such as progerin in case of
HGPS patients and therefore reduce or
eliminate many of the devastating
clinical symptoms of the underlying
biological defect of nuclear membrane
instability (Goldman R, Shumaker DK,
Erdos MR, Eriksson M, Goldman AE,
Gordon LB, Gruenbaum Y, Khuon S,
Mendez M, Varga R, Collins FS.
Accumulation of mutant lamin A causes
progressive changes in nuclear
architecture in Hutchinson-Gilford
progeria syndrome. Proc Natl Acad Sci
U S A 2004; 8963–8968.).
In addition to licensing, the
technology is available for further
development through collaborative
research opportunities with the
inventors.
Cell Culture System for Efficient
Expression of Self-Replicating Norwalk
Virus
Kyeong-Ok Chang, Stanislav
Sosnovtsev, Gael M. Belliot, Kim Y.
Green (NIAID).
U.S. Provisional Application filed 08
Apr 2005 (DHHS Reference No. E–043–
2005/0–US–01).
Licensing Contact: Michael
Shmilovich; 301/435–5019;
shmilovm@mail.nih.gov.
Available for licensing and
commercial development is a cell
culture system for the efficient
expression of self-replicating Norwalk
virus (NV) RNA (NV replicons). This
invention provides compositions and
methods for preparing a cell-based
system for molecular studies of NV
replication and the development of
antiviral drugs. A method related to
effectively clearing NV replicons, by
subjecting cells infected with NV
replicon to IFN-alpha is included that
demonstrates the applicability of this
invention to drug development. A
method of effectively clearing NV
replicons, by subjecting cells expressing
the NV replicon to nucleotide analogues
is also provided. These methods provide
molecular tools for the identification
and development of treatments for NV
and may also extend to other members
E:\FR\FM\07JNN1.SGM
07JNN1
33184
Federal Register / Vol. 70, No. 108 / Tuesday, June 7, 2005 / Notices
of the Calicivirus(es) (e.g., Norovirus,
Sapovirus, Lagovirus and Vesivirus).
Therapeutic Delivery of Nitric Oxide
From Novel Diazeniumdiolated
Derivatives of Acrylonitrile-based
Polymers
Joseph Hrabie, Michael Citro, Frank
DeRosa, and Larry Keefer (NCI).
U.S. Provisional Application No. 60/
613,257 filed 27 Sep 2004 (DHHS
Reference No. E–188–2004/0–US–01).
Licensing Contact: Norbert Pontzer;
301/435–5502; pontzern@mail.nih.gov.
Nucleophile/nitric oxide adduct ions
(materials containing the X–N2O2–
functional group; known as
diazeniumdiolates or NONOates)
spontaneously dissociate at
physiological pH to release nitric oxide
(NO) with reproducible half-lives
ranging from 2 seconds to 20 hours. The
bulk of the known and patented NIH
compositions and methods using
diazeniumdiolates are derived from
amine nucleophiles (i.e., where X–is
R1R2N–). These inventors more recently
developed simple and efficient chemical
methods to produce diazeniumdiolates
by bonding the N2O2–functional group
directly to carbon atoms. Using these
methods, the NIH inventors have now
produced and tested polymers in which
the NO releasing group is attached
directly to the carbon backbone of
polyacrylonitrile containing polymers.
Available for licensing are
compounds, compositions, medical
devices, and methods of treatment using
acrylonitrile-based polymers that release
NO for a week or longer.
Polyacrylonitrile itself, co-polymers,
admixtures, and products such as cloth
and hollow fiber hemofilters have been
treated and shown to release NO over
time. These polyacrylonitrile-based
products could be useful in conjunction
with medical devices where the many
therapeutic actions of NO would be
beneficial. Treatments using stents,
extracorporeal blood tubing, shunts,
wound dressings and many other
devices could be greatly improved by
NO actions including but not limited to
prevention of clotting, promotion of
tissue vascularization, and reduction of
excessive tissue proliferation.
In addition to licensing, the
technology is available for further
development through collaborative
research opportunities with the
inventors.
A New Antiviral Pathway that is
Responsible for Viral Clearance:
Modulation of ADAR1 Activities
Enhance Antiviral Therapies and Virus
Infection of Tissue Culture Systems
Deborah R. Taylor et al. (FDA).
VerDate jul<14>2003
20:54 Jun 06, 2005
Jkt 205001
U.S. Provisional Application No. 60/
605,238 filed 27 Aug 2004 (DHHS
Reference No. E–121–2004/0–US–01).
Licensing Contact: Robert M. Joynes;
301/594–6565; joynesr@mail.nih.gov.
This technology relates to the finding
that the antiviral activity of interferon
(IFN) is mediated by the activation of an
enzyme RNA adenosine deaminase
(ADAR1). This enzyme acts by
deaminating adenosine residues in
dsRNA molecules of the virus into
inosine residues. This, in turn, may lead
to mutations, genomic instability and
ultimately to complete degradation and
elimination of the virus. The subject
patent application focuses on Hepatitis
C virus (HCV), but may be broadly
applied to the other viruses.
Based on the above-described finding,
the technology offers two important
utilities in the medical field:
1. Antiviral therapeutics: Because
ADAR is so potent as an inhibitor of the
growth of HCV, an agonist of this
pathway or specifically of ADAR should
enhance the clearance of the virus from
the cells. Methods to identify such
ADAR agonists are described in the
subject patent applications.
2. HCV cell line for drug and vaccine
research: The finding described in the
subject patent application may lead to
an efficient cell line for growing HCV.
Currently, there is not a good system to
grow this virus. The addition of ADAR
inhibitors (such as RNAi or chemicals
that target the catalytic domain of
ADAR) to the system will result in a
system that can efficiently grow the
virus. Such a cell line is important for
vaccine development against HCV as
well as the development of anti-viral
therapeutics.
In addition to licensing, the
technology is available for further
development through collaborative
research opportunities with the
inventors.
Compositions Comprising T Cell
Receptors and Methods of Use Thereof
Richard Morgan (NCI) and Steven
Rosenberg (NCI).
PCT Application No. PCT/US2004/
029608 filed 13 Sep 2004 (DHHS
Reference No. E–106–2004/0–PCT–01).
Licensing Contact: Michelle A.
Booden; 301/451–7337;
boodenm@mail.nih.gov.
Historically, adoptive immunotherapy
has shown promise in treating cancer.
Traditionally, these adoptive techniques
developed to date have relied on
isolating and expanding T-cells reactive
to a specific tumor associated antigen.
However, the approach has been limited
by number of isolatable T cells specific
to a tumor-associated antigen in a
PO 00000
Frm 00130
Fmt 4703
Sfmt 4703
cancer patient’s immune system and a
very time consuming procedure to
isolate and expand the appropriate Tcells.
This invention describes the
composition and use of nucleic acid
sequences that encode polypeptides
capable of forming a T cell receptor
(TCR) in a genetically engineered cell.
Specifically, these nucleic acid
sequences will encode TCR’s specific to
tumor associated antigens (TAA), gp100,
NY–ESO–1, and MART–1. T Cells
engineered with these tumor associated
antigen specific TCRs show specific
immune responses against TAA
expressing cancer cells. This
observation has a profound effect on the
potential efficiency of new adoptive
therapies targeted towards cancer.
An adoptive therapy method has been
developed using the TAA specific TCR
nucleic acids to engineer isolated, nonspecific T-cells. This method could
eliminate the need to isolate and expand
T-cells that may or may not be present
in a cancer patient. Clinical trials are
currently underway to prove the
efficacy of this new adoptive therapy in
malignant melanoma.
Details of this invention are published
in:
1. Morgan RA, Dudley ME, Yu YY,
Zheng Z, Robbins PF, Theoret MR,
Wunderlich JR, Hughes MS, Restifo NP,
Rosenberg SA. High efficiency TCR gene
transfer into primary human
lymphocytes affords avid recognition of
melanoma tumor antigen glycoprotein
100 and does not alter the recognition
of autologous melanoma antigens. J
Immunol. 2003 Sep 15;171(6):3287–95.
2. Zhao Y, Zheng Z, Robbins PF,
Khong HT, Rosenberg SA, Morgan RA.
Primary human lymphocytes
transduced with NY–ESO–1 antigenspecific TCR genes recognize and kill
diverse human tumor cell lines. J
Immunol. 2005 Apr 1;174(7):4415–23.
3. Hughes MS, Yu YY, Dudley ME,
Zheng Z, Robbins PF, Li Y, Wunderlich
J, Hawley RG, Moayeri M, Rosenberg
SA, Morgan RA. Transfer of a TCR Gene
Derived from a Patient with a Marked
Antitumor Response Conveys Highly
Active T-Cell Effector Functions. Hum
Gene Ther. 2005 Apr;16(4):457–72.
In addition to licensing, the
technology is available for further
development through collaborative
research opportunities with the
inventors.
Retrovirus-Like Particles and
Retroviral Vaccines
David E. Ott (NCI).
PCT Application filed 27 Oct 2003
(DHHS Reference No. E–236–2003/0–
PCT–01).
E:\FR\FM\07JNN1.SGM
07JNN1
Federal Register / Vol. 70, No. 108 / Tuesday, June 7, 2005 / Notices
Licensing Contact: Susan Ano; 301/
435–5515; anos@mail.nih.gov.
This technology describes retroviruslike particles and their production from
retroviral constructs in which the gene
encoding all but seven amino acids of
the nucleocapsid (NC) protein was
deleted. This deletion functionally
eliminates packaging of the genomic
RNA, thus resulting in non-infectious
retrovirus-like particles. These particles
can be used in vaccines or immunogenic
compositions. Specific examples using
HIV–1 constructs are given.
Furthermore, efficient formation of
these particles requires inhibition of the
protease enzymatic activity, either by
mutation to the protease gene in the
construct or by protease inhibitor
thereby ensuring the production of noninfectious retrovirus-like particles. This
technology is further described in Ott et
al., Journal of Virology, 2003, 77(5),
5547.
Dated: May 26, 2005.
Steven M. Ferguson,
Director, Division of Technology Development
and Transfer, Office of Technology
Transfer,National Institutes of Health.
[FR Doc. 05–11221 Filed 6–6–05; 8:45 am]
BILLING CODE 4140–01–P
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
National Heart, Lung, and Blood
Institute; Notice of Meeting
Pursuant to section 10(d) of the
Federal Advisory Committee Act, as
amended (5 U.S.C. Appendix 2), notice
is hereby given of a meeting of the
National Heart, Lung, and Blood
Advisory Council.
The meeting will be open to the
public as indicated below, with
attendance limited to space available.
Individuals who plan to attend and
need special assistance, such as sign
language interpretation or other
reasonable accommodations, should
notify the Contact Person listed below
in advance of the meeting.
The meeting will be closed to the
public in accordance with the
provisions set forth in secions 552b(c)(4)
and 552b(c)(6), title 5 U.S.C., as
amended. The grant applications and
the discussions could disclose
confidential trade secrets or commercial
property such as patentable material,
and personal information concerning
individuals associated with the grant
applications, the disclosure of which
would constitute a clearly unwarranted
invasion of personal privacy.
VerDate jul<14>2003
20:54 Jun 06, 2005
Jkt 205001
Name of Committee: National Heart, Lung,
and Blood Advisory Council.
Date: June 16, 2005.
Open: 8:30 a.m. to 1 p.m.
Agenda: Discussion of program policies
and issues.
Place: National Institutes of Health,
Building 31, 31 Center Drive, Bethesda, MD
20892.
Closed: 1 p.m. to 4 p.m.
Agenda: To review and evaluate grant
applications.
Place: National Institutes of Health,
Building 31, 31 Center Drive, Bethesda, MD
20892.
Contact Person: Deborah P. Beebe, PhD,
Director, Division of Extramural Affairs,
National Heart, Lung, and Blood Institute,
National Institutes of Health, Two Rockledge
Center, Room 7100, 6701 Rockledge Drive,
Bethesda, MD 20892. 301/435–0260.
This notice is being published less than 15
days prior to the meeting due to the timing
limitations imposed by the review and
funding cycle.
Any interested person may file written
comments with the committee by forwarding
the statement to the Contact Person listed on
this notice. The statement should include the
name, address, telephone number and when
applicable, the business or professional
affiliation of the interested person.
In the interest of security, NIH has
instituted stringent procedures for entrance
into the building by non-government
employees. Persons without a government
I.D. will need to show a photo I.D. and signin at the security desk upon entering the
building.
Information is also available on the
Institute’s/Center’s home page https://
www.nhlbi.nih.gov/meetings/index.htm,
where an agenda and any additional
information for the meeting will be posted
when available.
(Catalogue of Federal Domestic Assistance
Program Nos. 93.233, National Center for
Sleep Disorders Research; 93.837, Heart and
Vascular Diseases Research; 93.838, Lung
Diseases Research; 93.839, Blood Diseases
and Resources Research, National Institutes
of Health, HHS.)
Dated: May 31, 2005.
LaVerne Y. Stringfield,
Director, Office of Federal Advisory
Committee Policy.
[FR Doc. 05–11218 Filed 6–6–05; 8:45 am]
BILLING CODE 4410–01–M
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
National Institute of Neurological
Disorders and Stroke; Amended Notice
of Meeting
Notice is hereby given of a change in
the meeting of the Neurological
Sciences and Disorders C, June 14, 2005,
8 a.m. to June 15, 2005, 5 p.m.
Wyndham Washington, DC 1400 M
PO 00000
Frm 00131
Fmt 4703
Sfmt 4703
33185
Street, NW., Washington, DC 20005
which was published in the Federal
Register on April 27, 2005, 70 FR Doc:
05–8413.
The meeting will be held for one day
on June 14, 2005 from 8 a.m. to 5 p.m.
The meeting is closed to the public.
Dated: May 27, 2005.
LaVerne Y. Stringfield,
Director, Office of Federal Advisory
Committee Policy.
[FR Doc. 05–11222 Filed 6–6–05; 8:45 am]
BILLING CODE 4140–01–M
DEPARTMENT OF HEALTH AND
HUMAN SERVICES
National Institutes of Health
National Institute of Dental &
Craniofacial Research; Notice of
Closed Meetings
Pursuant to section 10(d) of the
Federal Advisory Committee Act, as
amended (5 U.S.C. Appendix 2), notice
is hereby given of the following
meetings.
The meetings will be closed to the
public in accordance with the
provisions set forth in sections
552b(c)(4) and 552b(c)(6), Title 5 U.S.C.,
as amended. The grant applications and
the discussions could disclose
confidential trade secrets or commercial
property such as patentable material,
and personal information concerning
individuals associated with the grant
applications, the disclosure of which
would constitute a clearly unwarranted
invasion of persoanl privacy.
Name of Committee: National Institute of
Dental and Craniofacial Research Special
Emphasis Panel, 05–84, Review K22.
Date: June 30, 2005.
Time: 2 p.m. to 3 p.m.
Agenda: To review and evaluate grant
applications.
Place: National Institutes of Health,
Natcher Building, 45 Center Drive, Bethesda,
MD 20892, (Telephone Conference Call).
Contact Person: Soheyla Saadi, PhD,
Scientific Review Administrator, Intern,
Scientific Review Branch, 45 Center Dr. Rm
4AN32A, National Inst of Dental &
Craniofacial Research, National Institutes of
Health, Bethesda, MD 20892, (301) 594–4805,
saadisoh@nidcr.nih.gov.
Name of Committee: National Institute of
Dental and Craniofacial Research Special
Emphasis Panel, 05–79, Review R13s.
Date: July 6, 2005.
Time: 2 p.m. to 4 p.m.
Agenda: To review and evaluate grant
applications.
Place: National Institutes of Health,
Natcher Building, 45 Center Drive, Bethesda,
MD 20892, (Telephone Conference Call).
Contact Person: Mary Kelly, Scientific
Review Specialist, National Institute of
E:\FR\FM\07JNN1.SGM
07JNN1
Agencies
[Federal Register Volume 70, Number 108 (Tuesday, June 7, 2005)]
[Notices]
[Pages 33183-33185]
From the Federal Register Online via the Government Printing Office [www.gpo.gov]
[FR Doc No: 05-11221]
-----------------------------------------------------------------------
DEPARTMENT OF HEALTH AND HUMAN SERVICES
National Institutes of Health
Government-Owned Inventions; Availability for Licensing
AGENCY: National Institutes of Health, Public Health Service, DHHS.
ACTION: Notice.
-----------------------------------------------------------------------
SUMMARY: The inventions listed below are owned by an agency of the U.S.
Government and are available for licensing in the U.S. in accordance
with 35 U.S.C. 207 to achieve expeditious commercialization of results
of federally-funded research and development. Foreign patent
applications are filed on selected inventions to extend market coverage
for companies and may also be available for licensing.
ADDRESSES: Licensing information and copies of the U.S. patent
applications listed below may be obtained by writing to the indicated
licensing contact at the Office of Technology Transfer, National
Institutes of Health, 6011 Executive Boulevard, Suite 325, Rockville,
Maryland 20852-3804; telephone: 301/496-7057; fax: 301/402-0220. A
signed Confidential Disclosure Agreement will be required to receive
copies of the patent applications.
Farnesyltransferase Inhibitors for Treatment of Laminopathies, Cellular
Aging and Atherosclerosis
Francis Collins (NHGRI) et al.
U.S. Provisional Application No. 60/648,307 filed 28 Jan 2005 (DHHS
Reference No. E-055-2005/0-US-01).
Licensing Contact: Fatima Sayyid; 301/435-4521;
sayyidf@mail.nih.gov.
Hutchinson-Gilford Progeria Syndrome (HGPS) is a very rare
progressive childhood disorder characterized by premature aging
(progeria). Recently, the gene responsible for HGPS was identified
(Eriksson M, Brown WT, Gordon LB, Glynn MW, Singer J, Scott L, et al.
Recurrent de novo point mutations in lamin A cause Hutchinson-Gilford
progeria syndrome. Nature 2003; 423(6937): 293-8), and HGPS joined a
group of syndromes--the laminopathies--all of which are caused by
various mutations in the lamin A/C gene (LMNA). Lamin A is one of the
family of proteins that is modified post-translationally by the
addition of a farnesyl group. In progeria, the abnormal protein
(progerin) can still be farnesylated, however, a subsequent cleavage is
blocked.
The present invention describes a possible treatment of
laminopathies, cellular aging and aging-related conditions such as HGPS
through the use of farnesyltransferase inhibitors (FTIs) and other
related compounds. This treatment should lead to a decrease in the
accumulation of abnormal proteins such as progerin in case of HGPS
patients and therefore reduce or eliminate many of the devastating
clinical symptoms of the underlying biological defect of nuclear
membrane instability (Goldman R, Shumaker DK, Erdos MR, Eriksson M,
Goldman AE, Gordon LB, Gruenbaum Y, Khuon S, Mendez M, Varga R, Collins
FS. Accumulation of mutant lamin A causes progressive changes in
nuclear architecture in Hutchinson-Gilford progeria syndrome. Proc Natl
Acad Sci U S A 2004; 8963-8968.).
In addition to licensing, the technology is available for further
development through collaborative research opportunities with the
inventors.
Cell Culture System for Efficient Expression of Self-Replicating
Norwalk Virus
Kyeong-Ok Chang, Stanislav Sosnovtsev, Gael M. Belliot, Kim Y.
Green (NIAID).
U.S. Provisional Application filed 08 Apr 2005 (DHHS Reference No.
E-043-2005/0-US-01).
Licensing Contact: Michael Shmilovich; 301/435-5019;
shmilovm@mail.nih.gov.
Available for licensing and commercial development is a cell
culture system for the efficient expression of self-replicating Norwalk
virus (NV) RNA (NV replicons). This invention provides compositions and
methods for preparing a cell-based system for molecular studies of NV
replication and the development of antiviral drugs. A method related to
effectively clearing NV replicons, by subjecting cells infected with NV
replicon to IFN-alpha is included that demonstrates the applicability
of this invention to drug development. A method of effectively clearing
NV replicons, by subjecting cells expressing the NV replicon to
nucleotide analogues is also provided. These methods provide molecular
tools for the identification and development of treatments for NV and
may also extend to other members
[[Page 33184]]
of the Calicivirus(es) (e.g., Norovirus, Sapovirus, Lagovirus and
Vesivirus).
Therapeutic Delivery of Nitric Oxide From Novel Diazeniumdiolated
Derivatives of Acrylonitrile-based Polymers
Joseph Hrabie, Michael Citro, Frank DeRosa, and Larry Keefer (NCI).
U.S. Provisional Application No. 60/613,257 filed 27 Sep 2004 (DHHS
Reference No. E-188-2004/0-US-01).
Licensing Contact: Norbert Pontzer; 301/435-5502;
pontzern@mail.nih.gov.
Nucleophile/nitric oxide adduct ions (materials containing the X-
N2O2-functional group; known as diazeniumdiolates
or NONOates) spontaneously dissociate at physiological pH to release
nitric oxide (NO) with reproducible half-lives ranging from 2 seconds
to 20 hours. The bulk of the known and patented NIH compositions and
methods using diazeniumdiolates are derived from amine nucleophiles
(i.e., where X-is R1R2N-). These inventors more
recently developed simple and efficient chemical methods to produce
diazeniumdiolates by bonding the N2O2-functional
group directly to carbon atoms. Using these methods, the NIH inventors
have now produced and tested polymers in which the NO releasing group
is attached directly to the carbon backbone of polyacrylonitrile
containing polymers.
Available for licensing are compounds, compositions, medical
devices, and methods of treatment using acrylonitrile-based polymers
that release NO for a week or longer. Polyacrylonitrile itself, co-
polymers, admixtures, and products such as cloth and hollow fiber
hemofilters have been treated and shown to release NO over time. These
polyacrylonitrile-based products could be useful in conjunction with
medical devices where the many therapeutic actions of NO would be
beneficial. Treatments using stents,
extracorporeal blood tubing, shunts, wound dressings and many other
devices could be greatly improved by NO actions including but not
limited to prevention of clotting, promotion of tissue vascularization,
and reduction of excessive tissue proliferation.
In addition to licensing, the technology is available for further
development through collaborative research opportunities with the
inventors.
A New Antiviral Pathway that is Responsible for Viral Clearance:
Modulation of ADAR1 Activities Enhance Antiviral Therapies and Virus
Infection of Tissue Culture Systems
Deborah R. Taylor et al. (FDA).
U.S. Provisional Application No. 60/605,238 filed 27 Aug 2004 (DHHS
Reference No. E-121-2004/0-US-01).
Licensing Contact: Robert M. Joynes; 301/594-6565;
joynesr@mail.nih.gov.
This technology relates to the finding that the antiviral activity
of interferon (IFN) is mediated by the activation of an enzyme RNA
adenosine deaminase (ADAR1). This enzyme acts by deaminating adenosine
residues in dsRNA molecules of the virus into inosine residues. This,
in turn, may lead to mutations, genomic instability and ultimately to
complete degradation and elimination of the virus. The subject patent
application focuses on Hepatitis C virus (HCV), but may be broadly
applied to the other viruses.
Based on the above-described finding, the technology offers two
important utilities in the medical field:
1. Antiviral therapeutics: Because ADAR is so potent as an
inhibitor of the growth of HCV, an agonist of this pathway or
specifically of ADAR should enhance the clearance of the virus from the
cells. Methods to identify such ADAR agonists are described in the
subject patent applications.
2. HCV cell line for drug and vaccine research: The finding
described in the subject patent application may lead to an efficient
cell line for growing HCV. Currently, there is not a good system to
grow this virus. The addition of ADAR inhibitors (such as RNAi or
chemicals that target the catalytic domain of ADAR) to the system will
result in a system that can efficiently grow the virus. Such a cell
line is important for vaccine development against HCV as well as the
development of anti-viral therapeutics.
In addition to licensing, the technology is available for further
development through collaborative research opportunities with the
inventors.
Compositions Comprising T Cell Receptors and Methods of Use Thereof
Richard Morgan (NCI) and Steven Rosenberg (NCI).
PCT Application No. PCT/US2004/029608 filed 13 Sep 2004 (DHHS
Reference No. E-106-2004/0-PCT-01).
Licensing Contact: Michelle A. Booden; 301/451-7337;
boodenm@mail.nih.gov.
Historically, adoptive immunotherapy has shown promise in treating
cancer. Traditionally, these adoptive techniques developed to date have
relied on isolating and expanding T-cells reactive to a specific tumor
associated antigen. However, the approach has been limited by number of
isolatable T cells specific to a tumor-associated antigen in a cancer
patient's immune system and a very time consuming procedure to isolate
and expand the appropriate T-cells.
This invention describes the composition and use of nucleic acid
sequences that encode polypeptides capable of forming a T cell receptor
(TCR) in a genetically engineered cell. Specifically, these nucleic
acid sequences will encode TCR's specific to tumor associated antigens
(TAA), gp100, NY-ESO-1, and MART-1. T Cells engineered with these tumor
associated antigen specific TCRs show specific immune responses against
TAA expressing cancer cells. This observation has a profound effect on
the potential efficiency of new adoptive therapies targeted towards
cancer.
An adoptive therapy method has been developed using the TAA
specific TCR nucleic acids to engineer isolated, non-specific T-cells.
This method could eliminate the need to isolate and expand T-cells that
may or may not be present in a cancer patient. Clinical trials are
currently underway to prove the efficacy of this new adoptive therapy
in malignant melanoma.
Details of this invention are published in:
1. Morgan RA, Dudley ME, Yu YY, Zheng Z, Robbins PF, Theoret MR,
Wunderlich JR, Hughes MS, Restifo NP, Rosenberg SA. High efficiency TCR
gene transfer into primary human lymphocytes affords avid recognition
of melanoma tumor antigen glycoprotein 100 and does not alter the
recognition of autologous melanoma antigens. J Immunol. 2003 Sep
15;171(6):3287-95.
2. Zhao Y, Zheng Z, Robbins PF, Khong HT, Rosenberg SA, Morgan RA.
Primary human lymphocytes transduced with NY-ESO-1 antigen-specific TCR
genes recognize and kill diverse human tumor cell lines. J Immunol.
2005 Apr 1;174(7):4415-23.
3. Hughes MS, Yu YY, Dudley ME, Zheng Z, Robbins PF, Li Y,
Wunderlich J, Hawley RG, Moayeri M, Rosenberg SA, Morgan RA. Transfer
of a TCR Gene Derived from a Patient with a Marked Antitumor Response
Conveys Highly Active T-Cell Effector Functions. Hum Gene Ther. 2005
Apr;16(4):457-72.
In addition to licensing, the technology is available for further
development through collaborative research opportunities with the
inventors.
Retrovirus-Like Particles and Retroviral Vaccines
David E. Ott (NCI).
PCT Application filed 27 Oct 2003 (DHHS Reference No. E-236-2003/0-
PCT-01).
[[Page 33185]]
Licensing Contact: Susan Ano; 301/435-5515; anos@mail.nih.gov.
This technology describes retrovirus-like particles and their
production from retroviral constructs in which the gene encoding all
but seven amino acids of the nucleocapsid (NC) protein was deleted.
This deletion functionally eliminates packaging of the genomic RNA,
thus resulting in non-infectious retrovirus-like particles. These
particles can be used in vaccines or immunogenic compositions. Specific
examples using HIV-1 constructs are given. Furthermore, efficient
formation of these particles requires inhibition of the protease
enzymatic activity, either by mutation to the protease gene in the
construct or by protease inhibitor thereby ensuring the production of
non-infectious retrovirus-like particles. This technology is further
described in Ott et al., Journal of Virology, 2003, 77(5), 5547.
Dated: May 26, 2005.
Steven M. Ferguson,
Director, Division of Technology Development and Transfer, Office of
Technology Transfer,National Institutes of Health.
[FR Doc. 05-11221 Filed 6-6-05; 8:45 am]
BILLING CODE 4140-01-P